Novel compound heterozygous variants (c.971delA/c.542C > T) in

amino acid transporter microcephaly seizure spastic tetraplegia spasticity

Journal

Frontiers in pediatrics
ISSN: 2296-2360
Titre abrégé: Front Pediatr
Pays: Switzerland
ID NLM: 101615492

Informations de publication

Date de publication:
2023
Historique:
received: 10 03 2023
accepted: 26 06 2023
medline: 28 7 2023
pubmed: 28 7 2023
entrez: 28 7 2023
Statut: epublish

Résumé

Spastic tetraplegia, thin corpus callosum, and progressive microcephaly (SPATCCM) are linked to

Identifiants

pubmed: 37502193
doi: 10.3389/fped.2023.1183574
pmc: PMC10369183
doi:

Types de publication

Journal Article

Langues

eng

Pagination

1183574

Informations de copyright

© 2023 Mohamed, Ghattas, Almansoori, Tabouni, Baydoun, Kizhakkedath, John, Alblooshi, Shaukat and Al-Jasmi.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

Références

Nat Protoc. 2016 Jan;11(1):1-9
pubmed: 26633127
J Neurosci. 2003 Jan 15;23(2):550-60
pubmed: 12533615
Genomics. 1994 Nov 1;24(1):20-6
pubmed: 7896285
J Mol Neurosci. 2022 Jun;72(6):1322-1333
pubmed: 35316504
PLoS One. 2016 Jun 07;11(6):e0156551
pubmed: 27272177
Child Neurol Open. 2019 Oct 08;6:2329048X19880647
pubmed: 31763347
BMC Bioinformatics. 2010 Nov 08;11:548
pubmed: 21059217
Genet Med. 2015 May;17(5):405-24
pubmed: 25741868
PLoS One. 2012;7(10):e46688
pubmed: 23056405
Comput Struct Biotechnol J. 2021 Sep 17;19:5246-5254
pubmed: 34630942
Nat Methods. 2010 Apr;7(4):248-9
pubmed: 20354512
Hum Mutat. 2003 Jun;21(6):577-81
pubmed: 12754702
J Mol Graph Model. 2017 Jun;74:54-60
pubmed: 28351017
Proc Natl Acad Sci U S A. 2018 Sep 18;115(38):9628-9633
pubmed: 30185558
J Hum Genet. 2016 Aug;61(8):761-4
pubmed: 27193218
Nature. 2020 May;581(7809):434-443
pubmed: 32461654
Nucleic Acids Res. 2017 Jan 4;45(D1):D840-D845
pubmed: 27899611
Nucleic Acids Res. 2002 Jan 1;30(1):52-5
pubmed: 11752252
SLAS Discov. 2021 Oct;26(9):1148-1163
pubmed: 34269129
J Med Genet. 2015 Aug;52(8):541-7
pubmed: 26041762
J Chem Theory Comput. 2007 Nov;3(6):2312-34
pubmed: 26636222
Nat Methods. 2014 Apr;11(4):361-2
pubmed: 24681721
Nature. 2015 Oct 1;526(7571):68-74
pubmed: 26432245

Auteurs

Feda E Mohamed (FE)

Department of Genetics and Genomics, College of Medicine and Health Sciences, United Arab Emirates University, Al Ain, United Arab Emirates.

Mohammad A Ghattas (MA)

College of Pharmacy, Al Ain University, Al Ain, United Arab Emirates.
AAU Health and Biomedical Research Center, Al Ain University, Abu Dhabi, United Arab Emirates.

Taleb M Almansoori (TM)

Department of Radiology, College of Medicine and Health Sciences, United Arab Emirates University, Al Ain, United Arab Emirates.

Mohammed Tabouni (M)

Department of Genetics and Genomics, College of Medicine and Health Sciences, United Arab Emirates University, Al Ain, United Arab Emirates.

Ibrahim Baydoun (I)

Department of Genetics and Genomics, College of Medicine and Health Sciences, United Arab Emirates University, Al Ain, United Arab Emirates.

Praseetha Kizhakkedath (P)

Department of Genetics and Genomics, College of Medicine and Health Sciences, United Arab Emirates University, Al Ain, United Arab Emirates.

Anne John (A)

Department of Genetics and Genomics, College of Medicine and Health Sciences, United Arab Emirates University, Al Ain, United Arab Emirates.

Hiba Alblooshi (H)

Department of Genetics and Genomics, College of Medicine and Health Sciences, United Arab Emirates University, Al Ain, United Arab Emirates.

Qudsia Shaukat (Q)

Department of Pediatrics, Tawam Hospital, Al Ain, United Arab Emirates.

Fatma Al-Jasmi (F)

Department of Genetics and Genomics, College of Medicine and Health Sciences, United Arab Emirates University, Al Ain, United Arab Emirates.
Department of Pediatrics, Tawam Hospital, Al Ain, United Arab Emirates.

Classifications MeSH