Germline genetic variants in pheochromocytoma/paraganglioma: single-center experience.

MAX NF1 RET SDHB SDHD TMEM127 VHL

Journal

Endocrine oncology (Bristol, England)
ISSN: 2634-4793
Titre abrégé: Endocr Oncol
Pays: England
ID NLM: 9918540584106676

Informations de publication

Date de publication:
01 Jan 2023
Historique:
received: 25 04 2023
accepted: 10 05 2023
medline: 2 8 2023
pubmed: 2 8 2023
entrez: 2 8 2023
Statut: epublish

Résumé

Pheochromocytoma and paragangliomas (PPGLs) are rare neuroendocrine tumors carrying 25-40% pathogenic germline gene variants (PGVs). We evaluated clinical, laboratory, and germline molecular profile of 115 patients with pathologic (14 patients were relatives from 8 different families recruited for genetic survey) confirmed PPGL followed in our institution. Patients with classic MEN2A/MEN2B phenotypes and at-risk relatives underwent direct analysis of

Identifiants

pubmed: 37529773
doi: 10.1530/EO-22-0091
pii: EO-22-0091
pmc: PMC10388674
doi:

Types de publication

Journal Article

Langues

eng

Pagination

e220091

Informations de copyright

© the author(s).

Déclaration de conflit d'intérêts

There is no conflict of interest that could be perceived as prejudicing the impartiality of this research.

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Auteurs

José V Lima (JV)

Department of Medicine, Division of Endocrinology and Metabolism, Universidade Federal de São Paulo (UNIFESP), São Paulo, SP, Brazil.
Santa Casa de São Paulo School of Medical Sciences, São Paulo, SP, Brazil.
Fleury Group, São Paulo, SP, Brazil.

Nilza M Scalissi (NM)

Santa Casa de São Paulo School of Medical Sciences, São Paulo, SP, Brazil.

Kelly C de Oliveira (KC)

Department of Medicine, Division of Endocrinology and Metabolism, Universidade Federal de São Paulo (UNIFESP), São Paulo, SP, Brazil.

Susan C Lindsey (SC)

Department of Medicine, Division of Endocrinology and Metabolism, Universidade Federal de São Paulo (UNIFESP), São Paulo, SP, Brazil.

Caroline Olivati (C)

Fleury Group, São Paulo, SP, Brazil.

Elisa Napolitano Ferreira (EN)

Fleury Group, São Paulo, SP, Brazil.

Claudio E Kater (CE)

Department of Medicine, Division of Endocrinology and Metabolism, Universidade Federal de São Paulo (UNIFESP), São Paulo, SP, Brazil.

Classifications MeSH