Children's Oncology Group's 2023 blueprint for research: Central nervous system tumors.
CNS germ cell tumor
diffuse midline glioma
ependymoma
medulloblastoma
pediatric low-grade glioma
Journal
Pediatric blood & cancer
ISSN: 1545-5017
Titre abrégé: Pediatr Blood Cancer
Pays: United States
ID NLM: 101186624
Informations de publication
Date de publication:
09 2023
09 2023
Historique:
received:
13
07
2023
accepted:
14
07
2023
pmc-release:
01
09
2024
medline:
18
8
2023
pubmed:
3
8
2023
entrez:
3
8
2023
Statut:
ppublish
Résumé
Tumors of the central nervous system (CNS) are a leading cause of morbidity and mortality in the pediatric population. Molecular characterization in the last decade has redefined CNS tumor diagnoses and risk stratification; confirmed the unique biology of pediatric tumors as distinct entities from tumors that occur in adulthood; and led to the first novel targeted therapies receiving Food and Drug Administration (FDA) approval for children with CNS tumors. There remain significant challenges to overcome: children with unresectable low-grade glioma may require multiple prolonged courses of therapy affecting quality of life; children with high-grade glioma have a dismal long-term prognosis; children with medulloblastoma may suffer significant short- and long-term morbidity from multimodal cytotoxic therapy, and approaches to improve survival in ependymoma remain elusive. The Children's Oncology Group (COG) is uniquely positioned to conduct the next generation of practice-changing clinical trials through rapid prospective molecular characterization and therapy evaluation in well-defined clinical and molecular groups.
Identifiants
pubmed: 37534382
doi: 10.1002/pbc.30600
pmc: PMC10569820
mid: NIHMS1930175
doi:
Types de publication
Journal Article
Research Support, N.I.H., Extramural
Langues
eng
Sous-ensembles de citation
IM
Pagination
e30600Subventions
Organisme : NCI NIH HHS
ID : U24 CA196173
Pays : United States
Organisme : NIH HHS
ID : U10CA098543
Pays : United States
Organisme : NIH HHS
ID : U24CA114766
Pays : United States
Organisme : NCI NIH HHS
ID : U10 CA098543
Pays : United States
Organisme : NCI NIH HHS
ID : U10 CA180899
Pays : United States
Organisme : NCI NIH HHS
ID : U10 CA180886
Pays : United States
Organisme : NCI NIH HHS
ID : U10 CA098413
Pays : United States
Organisme : NIH HHS
ID : U10CA180886
Pays : United States
Organisme : NCI NIH HHS
ID : U24 CA114766
Pays : United States
Organisme : NIH HHS
ID : U24CA196173
Pays : United States
Organisme : NIH HHS
ID : U10CA098413
Pays : United States
Informations de copyright
© 2023 Wiley Periodicals LLC.
Références
Lancet Oncol. 2015 May;16(5):569-82
pubmed: 25882982
Neurooncol Adv. 2021 Jul 07;3(1):vdab097
pubmed: 34409296
J Clin Oncol. 2021 Aug 20;39(24):2685-2697
pubmed: 34110925
Childs Nerv Syst. 2009 Oct;25(10):1261-8
pubmed: 19373477
Cancer Cell. 2015 May 11;27(5):728-43
pubmed: 25965575
Clin Cancer Res. 2023 May 1;:
pubmed: 37126021
Neuro Oncol. 2021 Oct 1;23(10):1777-1788
pubmed: 33631016
J Clin Oncol. 2012 Jul 20;30(21):2648-53
pubmed: 22665539
Qual Life Res. 2018 Feb;27(2):529-537
pubmed: 29090422
Ann Oncol. 2015 Mar;26(3):589-97
pubmed: 25527416
Acta Neuropathol. 2018 Aug;136(2):227-237
pubmed: 30019219
J Pediatr Hematol Oncol. 2019 Aug;41(6):433-437
pubmed: 30629003
Neuro Oncol. 2012 Sep;14(9):1194-200
pubmed: 22869621
Lancet Oncol. 2018 May;19(5):705-714
pubmed: 29606586
Lancet Oncol. 2019 Jul;20(7):1011-1022
pubmed: 31151904
Neoplasia. 2023 Feb;36:100860
pubmed: 36521378
Acta Neuropathol. 2016 Jun;131(6):821-31
pubmed: 27040285
J Clin Oncol. 2020 Apr 10;38(11):1175-1185
pubmed: 32105509
Pediatr Blood Cancer. 2013 Jun;60(6):1022-6
pubmed: 23255213
Eur J Cancer. 2012 Jan;48(2):263-9
pubmed: 22206862
Neuro Oncol. 2022 Jun 1;24(6):974-983
pubmed: 34850169
Acta Neuropathol. 2022 Jun;143(6):697-711
pubmed: 35501487
Neuro Oncol. 2018 Jan 22;20(2):160-173
pubmed: 29016845
Lancet Oncol. 2018 Dec;19(12):1602-1616
pubmed: 30392813
Acta Neuropathol. 2017 Jan;133(1):5-12
pubmed: 27858204
Neuro Oncol. 2020 Oct 14;22(10):1536-1544
pubmed: 32215549
Acta Neuropathol. 2014 Jul;128(1):137-49
pubmed: 24791927
Brain Pathol. 2021 Sep;31(5):e12967
pubmed: 33938067
Semin Oncol. 2020 Feb;47(1):8-22
pubmed: 32139101
Oncologist. 2008 Jun;13(6):690-9
pubmed: 18586924
J Clin Oncol. 2021 Mar 1;39(7):822-835
pubmed: 33405951
J Clin Oncol. 2014 Mar 20;32(9):886-96
pubmed: 24493713
JAMA Oncol. 2021 Sep 01;7(9):1313-1321
pubmed: 34292305
Nat Med. 2023 May;29(5):1103-1112
pubmed: 37059834
Neurotherapeutics. 2022 Oct;19(6):1733-1751
pubmed: 35859223
Int J Radiat Oncol Biol Phys. 2022 May 1;113(1):143-151
pubmed: 34990779
J Clin Oncol. 2020 Jan 20;38(3):223-231
pubmed: 31774708
J Clin Oncol. 2015 Aug 1;33(22):2464-71
pubmed: 26101244
Neuro Oncol. 2016 Oct;18(10):1442-50
pubmed: 27006176
Acta Neuropathol. 2017 Nov;134(5):705-714
pubmed: 28733933
J Clin Oncol. 2019 Dec 10;37(35):3335-3339
pubmed: 31498029
Clin Cancer Res. 2021 May 15;27(10):2879-2889
pubmed: 33737307
Neuro Oncol. 2017 Jun 1;19(6):750-761
pubmed: 27683733
Nature. 2014 Feb 27;506(7489):451-5
pubmed: 24553141
Cancer Radiother. 2019 Sep;23(5):370-377
pubmed: 31331843
J Clin Oncol. 2019 Dec 1;37(34):3283-3290
pubmed: 31545689
Neuro Oncol. 2022 Apr 1;24(4):655-664
pubmed: 34347089
Neuro Oncol. 2022 Jul 1;24(7):1178-1190
pubmed: 34935967
Neuro Oncol. 2011 Apr;13(4):410-6
pubmed: 21345842
Pediatr Blood Cancer. 2017 Sep;64(9):
pubmed: 28296130
Neuro Oncol. 2018 Jan 10;20(1):13-23
pubmed: 28449033
Neuro Oncol. 2021 Aug 2;23(8):1231-1251
pubmed: 34185076
N Engl J Med. 2017 Oct 12;377(15):1409-1412
pubmed: 29020592
Pediatr Blood Cancer. 2023 Jun;70 Suppl 4:e30147
pubmed: 36519599
BMC Cancer. 2019 Jun 11;19(1):571
pubmed: 31185958
Curr Opin Pediatr. 2019 Feb;31(1):21-27
pubmed: 30531227
Cancer. 2016 Jun 15;122(12):1928-36
pubmed: 27061921
J Clin Oncol. 2015 Aug 20;33(24):2646-54
pubmed: 26169613
J Clin Oncol. 2018 Oct 17;:JCO2017764720
pubmed: 30332335
J Clin Oncol. 2012 Jul 20;30(21):2641-7
pubmed: 22665535
J Neurooncol. 2020 Oct;150(1):47-56
pubmed: 33021733
Acta Neuropathol. 2019 Dec;138(6):1075-1089
pubmed: 31414211
Nat Commun. 2019 Sep 25;10(1):4343
pubmed: 31554817
Acta Neuropathol. 2016 Jun;131(6):803-20
pubmed: 27157931
Cancer Cell. 2016 Mar 14;29(3):379-393
pubmed: 26923874
Neuro Oncol. 2022 Sep 6;24(Suppl 3):iii1-iii38
pubmed: 36066969
J Clin Oncol. 2019 Apr 20;37(12):974-983
pubmed: 30811284
J Clin Oncol. 2006 Sep 1;24(25):4202-8
pubmed: 16943538
Neuro Oncol. 2011 Mar;13(3):317-23
pubmed: 21339192
Pediatr Blood Cancer. 2011 Dec 1;57(6):978-85
pubmed: 21796761
J Clin Oncol. 2016 Oct 10;34(29):3537-3543
pubmed: 27573663
Neoplasia. 2023 May;39:100898
pubmed: 37011459
Cancer Cell. 2016 Dec 12;30(6):891-908
pubmed: 27960086
Neuro Oncol. 2020 Jul 7;22(7):1006-1017
pubmed: 31883020