The International SCN8A Patient Registry: A Scientific Resource to Advance the Understanding and Treatment of a Rare Pediatric Neurodevelopmental Syndrome.


Journal

Journal of registry management
ISSN: 1945-6123
Titre abrégé: J Registry Manag
Pays: United States
ID NLM: 9804163

Informations de publication

Date de publication:
2023
Historique:
medline: 15 8 2023
pubmed: 14 8 2023
entrez: 14 8 2023
Statut: ppublish

Résumé

Genetic variants in the

Identifiants

pubmed: 37577282
pii: jrm.2023.50.1.4
pmc: PMC10414210

Substances chimiques

NAV1.6 Voltage-Gated Sodium Channel 0
SCN8A protein, human 0

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

4-10

Informations de copyright

© 2023 National Cancer Registrars Association.

Références

J Biomed Inform. 2009 Apr;42(2):377-81
pubmed: 18929686
Seizure. 2022 Apr;97:50-57
pubmed: 35325842
Epilepsy Res. 2020 Jan;159:106261
pubmed: 31887642
Nat Rev Neurosci. 2021 Mar;22(3):152-166
pubmed: 33531663
Cell Rep Med. 2022 Feb 15;3(2):100530
pubmed: 35243424
Neurology. 2018 Sep 18;91(12):e1112-e1124
pubmed: 30171078
Epilepsia. 2019 May;60(5):830-844
pubmed: 30968951
Am J Hum Genet. 2012 Mar 9;90(3):502-10
pubmed: 22365152
Neurology. 2015 Feb 3;84(5):480-9
pubmed: 25568300
Epilepsia. 2019 Aug;60(8):1711-1720
pubmed: 31335965

Auteurs

Jennifer G Andrews (JG)

University of Arizona, Tucson, Arizona.

Maureen Kelly Galindo (MK)

University of Arizona, Tucson, Arizona.

Joshua B Hack (JB)

University of Arizona, Tucson, Arizona.
BIO5 Institute, University of Arizona, Tucson, Arizona.

Joseph C Watkins (JC)

University of Arizona, Tucson, Arizona.

Gabrielle A Conecker (GA)

International SCN8A Alliance.

Michael F Hammer (MF)

University of Arizona, Tucson, Arizona.
BIO5 Institute, University of Arizona, Tucson, Arizona.
International SCN8A Alliance.

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Classifications MeSH