Recurrence of a BBS1 variant in Bardet-Biedl patients from Prince Edward Island.


Journal

Clinical genetics
ISSN: 1399-0004
Titre abrégé: Clin Genet
Pays: Denmark
ID NLM: 0253664

Informations de publication

Date de publication:
12 2023
Historique:
revised: 08 08 2023
received: 12 06 2023
accepted: 09 08 2023
medline: 8 11 2023
pubmed: 24 8 2023
entrez: 23 8 2023
Statut: ppublish

Résumé

This study reports variants in BBS1 and BBS7 in patients with Bardet-Biedl syndrome from the Canadian Maritime provinces. The BBS1 variant NM_024649.5:c.1169T>G was identified as a recurrent variant in Prince Edward Island.

Identifiants

pubmed: 37612261
doi: 10.1111/cge.14418
doi:

Substances chimiques

Microtubule-Associated Proteins 0
Bbs1 protein, human 0

Types de publication

Letter Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

713-715

Informations de copyright

© 2023 John Wiley & Sons A/S. Published by John Wiley & Sons Ltd.

Références

Deveault C, Billingsley G, Duncan JL, et al. BBS genotype-phenotype assessment of a multiethnic patient cohort calls for a revision of the disease definition. Hum Mutat. 2011;32(6):610-619.
Webb MP, Dicks EL, Green JS, et al. Autosomal recessive Bardet-Biedl syndrome: first-degree relatives have no predisposition to metabolic and renal disorders. Kidney Int. 2009;76(2):215-223.
Forsythe E, Kenny J, Bacchelli C, Beales PL. Managing Bardet-Biedl syndrome-now and in the future. Front Pediatr. 2018;6:23.
Mykytyn K, Nishimura DY, Searby CC, et al. Evaluation of complex inheritance involving the common Bardet-Biedl syndrome locus (BBS1). Am J Hum Genet. 2003;72(2):429-437.
Cring MR, Meyer KJ, Searby CC, et al. Ectopic expression of BBS1 rescues male infertility, but not retinal degeneration, in a BBS1 mouse model. Gene Ther. 2022;29(5):227-235.

Auteurs

Fahad A Alghaith (FA)

Department of Pathology, Dalhousie University, Halifax, Nova Scotia, Canada.

Sara MacKay (S)

Maritime Medical Genetics Service, IWK Health Centre, Halifax, Nova Scotia, Canada.

Karin Wallace (K)

Division of Ophthalmology, Department of Surgery, Dalhousie University, Halifax, Nova Scotia, Canada.

Jeff Locke (J)

Department of Ophthalmology and Visual Sciences, Dalhousie University, Halifax, Nova Scotia, Canada.

Johane M Robitaille (JM)

Department of Ophthalmology and Visual Sciences, Dalhousie University, Halifax, Nova Scotia, Canada.

Sarah Dyack (S)

Maritime Medical Genetics Service, IWK Health Centre, Halifax, Nova Scotia, Canada.
Department of Pediatrics and Medicine, Dalhousie University, Halifax, Nova Scotia, Canada.

Heleen H Arts (HH)

Department of Pathology, Dalhousie University, Halifax, Nova Scotia, Canada.

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Classifications MeSH