Aromatic l-amino acid decarboxylase deficiency in Taiwan.

AADC Chinese DDC Taiwan aromatic l‐amino acid decarboxylase incidence

Journal

JIMD reports
ISSN: 2192-8304
Titre abrégé: JIMD Rep
Pays: United States
ID NLM: 101568557

Informations de publication

Date de publication:
Sep 2023
Historique:
received: 17 05 2023
revised: 13 07 2023
accepted: 21 07 2023
medline: 13 9 2023
pubmed: 13 9 2023
entrez: 13 9 2023
Statut: epublish

Résumé

Aromatic l-amino acid decarboxylase (AADC) deficiency is a rare inherited disorder that affects neurotransmitter biosynthesis. A

Identifiants

pubmed: 37701332
doi: 10.1002/jmd2.12387
pii: JMD212387
pmc: PMC10494508
doi:

Types de publication

Journal Article

Langues

eng

Pagination

387-392

Informations de copyright

© 2023 The Authors. JIMD Reports published by John Wiley & Sons Ltd on behalf of SSIEM.

Déclaration de conflit d'intérêts

Wuh‐Liang Hwu participated as an advisory board member, received consulting fees, and was a speaker for PTC Therapeutics. In addition, he was a grant recipient for PTC Therapeutics and a research investigator for PTC Therapeutics. Rai‐Hseng Hsu, Mei‐Hsin Li, Hui‐Min Lee, Hui‐An Chen, Ni‐Chung Lee, and Yin‐Hsiu Chien declare no conflict of interest.

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Auteurs

Wuh-Liang Hwu (WL)

Department of Pediatrics National Taiwan University Hospital Taipei Taiwan.
Department of Medical Genetics National Taiwan University Hospital Taipei Taiwan.
Graduate Institute of Integrated Medicine China Medical University Taichung City Taiwan.

Rai-Hseng Hsu (RH)

Department of Medical Genetics National Taiwan University Hospital Taipei Taiwan.

Mei-Hsin Li (MH)

Department of Medical Genetics National Taiwan University Hospital Taipei Taiwan.

Hui-Min Lee (HM)

Department of Medical Genetics National Taiwan University Hospital Taipei Taiwan.

Hui-An Chen (HA)

Department of Pediatrics National Taiwan University Hospital Taipei Taiwan.

Ni-Chung Lee (NC)

Department of Pediatrics National Taiwan University Hospital Taipei Taiwan.
Department of Medical Genetics National Taiwan University Hospital Taipei Taiwan.

Yin-Hsiu Chien (YH)

Department of Pediatrics National Taiwan University Hospital Taipei Taiwan.
Department of Medical Genetics National Taiwan University Hospital Taipei Taiwan.

Classifications MeSH