Patients' Preferences for Adjunctive Parkinson's Disease Treatments: A Discrete-Choice Experiment.

Parkinson’s discrete choice stated preferences

Journal

Patient preference and adherence
ISSN: 1177-889X
Titre abrégé: Patient Prefer Adherence
Pays: New Zealand
ID NLM: 101475748

Informations de publication

Date de publication:
2023
Historique:
received: 23 05 2023
accepted: 12 08 2023
medline: 19 9 2023
pubmed: 19 9 2023
entrez: 19 9 2023
Statut: epublish

Résumé

Several adjunctive medications are available to reduce OFF time between levodopa/carbidopa (LD/CD) doses for people with Parkinson's disease (PD). To explore how individuals with PD balance benefits and burdens when considering adjunctive medications. US adults (30-83 years) with self-reported PD, currently treated with LD/CD, who experienced OFF episodes were recruited through the Fox Insight study to complete a discrete-choice experiment survey. Respondents selected among experimentally designed profiles for hypothetical adjunctive PD treatments that varied in efficacy (additional ON time), potential adverse effects (troublesome dyskinesia, risk of diarrhea, risk of change in bodily fluid color), and dosing frequency or the option "No additional medicine". Data were analyzed with random-parameters logit models. Respondents (N=480) would require ≥60 additional minutes of daily ON time to accept either a 40% risk of change in bodily fluid color or 10 additional minutes with troublesome dyskinesia daily. Respondents would require 40 additional minutes of daily ON time to accept a 10% risk of diarrhea and 22 additional minutes of daily ON time to switch from 1 additional pill each day to 1 pill with each LD/CD dose. On average, respondents preferred adjunctive PD medication over no additional medication. Results predicted that 59.1% of respondents would select a hypothetical treatment profile similar to opicapone, followed by no additional medication (27.5%) and a hypothetical treatment profile similar to entacapone (13.4%). The data collected were based on responses to hypothetical choice profiles in the survey questions. The attributes and levels selected for this study were intended to reflect the characteristics of opicapone and entacapone; attributes associated with other adjunctive therapies were not evaluated. Patients with PD expressed interest in adjunctive treatment to increase ON time and would accept reduced ON time to avoid adverse effects.

Sections du résumé

Background UNASSIGNED
Several adjunctive medications are available to reduce OFF time between levodopa/carbidopa (LD/CD) doses for people with Parkinson's disease (PD).
Objective UNASSIGNED
To explore how individuals with PD balance benefits and burdens when considering adjunctive medications.
Methods UNASSIGNED
US adults (30-83 years) with self-reported PD, currently treated with LD/CD, who experienced OFF episodes were recruited through the Fox Insight study to complete a discrete-choice experiment survey. Respondents selected among experimentally designed profiles for hypothetical adjunctive PD treatments that varied in efficacy (additional ON time), potential adverse effects (troublesome dyskinesia, risk of diarrhea, risk of change in bodily fluid color), and dosing frequency or the option "No additional medicine". Data were analyzed with random-parameters logit models.
Results UNASSIGNED
Respondents (N=480) would require ≥60 additional minutes of daily ON time to accept either a 40% risk of change in bodily fluid color or 10 additional minutes with troublesome dyskinesia daily. Respondents would require 40 additional minutes of daily ON time to accept a 10% risk of diarrhea and 22 additional minutes of daily ON time to switch from 1 additional pill each day to 1 pill with each LD/CD dose. On average, respondents preferred adjunctive PD medication over no additional medication. Results predicted that 59.1% of respondents would select a hypothetical treatment profile similar to opicapone, followed by no additional medication (27.5%) and a hypothetical treatment profile similar to entacapone (13.4%).
Limitations UNASSIGNED
The data collected were based on responses to hypothetical choice profiles in the survey questions. The attributes and levels selected for this study were intended to reflect the characteristics of opicapone and entacapone; attributes associated with other adjunctive therapies were not evaluated.
Conclusion UNASSIGNED
Patients with PD expressed interest in adjunctive treatment to increase ON time and would accept reduced ON time to avoid adverse effects.

Identifiants

pubmed: 37724313
doi: 10.2147/PPA.S420051
pii: 420051
pmc: PMC10505378
doi:

Types de publication

Journal Article

Langues

eng

Pagination

2263-2277

Informations de copyright

© 2023 Serbin et al.

Déclaration de conflit d'intérêts

Michael Serbin, Charles Yonan, and Olga Klepitskaya are employees of Neurocrine Biosciences. Carol Mansfield is an employee of RTI Health Solutions, and Colton Leach was an employee of RTI Health Solutions when this research was conducted. Connie Marras is on the steering committee for the Fox Insight study. Margaret Sheehan and Anne Donnelly have nothing to disclose for this work.

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Auteurs

Michael Serbin (M)

Neurocrine Biosciences, Inc., San Diego, CA, USA.

Connie Marras (C)

The Edmond J. Safra Program in Parkinson's Disease, University Health Network, University of Toronto, Toronto, ON, Canada.

Carol Mansfield (C)

RTI Health Solutions, Research Triangle Park, NC, USA.

Colton Leach (C)

RTI Health Solutions, Research Triangle Park, NC, USA.

Charles Yonan (C)

Neurocrine Biosciences, Inc., San Diego, CA, USA.

Margaret Sheehan (M)

Ashurst, Washington, DC, USA.

Anne Donnelly (A)

Kellogg School of Management, Northwestern University, Evanston, IL, USA.

Olga Klepitskaya (O)

Neurocrine Biosciences, Inc., San Diego, CA, USA.

Classifications MeSH