Brain-penetrant cyanoindane and cyanotetralin inhibitors of G2019S-LRRK2 kinase activity.

G2019S Kinase inhibitor LRRK2 Parkinson’s disease

Journal

Bioorganic & medicinal chemistry letters
ISSN: 1464-3405
Titre abrégé: Bioorg Med Chem Lett
Pays: England
ID NLM: 9107377

Informations de publication

Date de publication:
15 Oct 2023
Historique:
received: 05 11 2022
revised: 10 08 2023
accepted: 19 09 2023
pubmed: 22 9 2023
medline: 22 9 2023
entrez: 21 9 2023
Statut: ppublish

Résumé

The G2019S variant of LRRK2, which causes an increase in kinase activity, is associated with the occurrence of Parkinson's disease (PD). Potent, mutation-selective, and brain penetrant inhibitors of LRRK2 can suppress the biological effects specific to G2019S-LRRK2 that cause pathogenicity. We report the discovery of a series of cyanoindane and cyanotetralin kinase inhibitors culminating in compound 34 that demonstrated selective inhibition of phosphorylation of LRRK2 in the mouse brain. These novel inhibitors may further enable the precision medicine path for future PD therapeutics.

Identifiants

pubmed: 37734423
pii: S0960-894X(23)00365-7
doi: 10.1016/j.bmcl.2023.129487
pii:
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

129487

Informations de copyright

Copyright © 2023 Elsevier Ltd. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of Competing Interest The authors declare that they have no known competing financial interests or personal relationships that could have appeared to influence the work reported in this paper.

Auteurs

Albert W Garofalo (AW)

ESCAPE Bio, South San Francisco, CA 94080, United States. Electronic address: albert6@stanford.edu.

Jacob Schwarz (J)

ESCAPE Bio, South San Francisco, CA 94080, United States.

Kerry Zobel (K)

ESCAPE Bio, South San Francisco, CA 94080, United States.

Claudia Beato (C)

Aptuit, an Evotec Company, 37135 Verona, Italy.

Silvia Bernardi (S)

Aptuit, an Evotec Company, 37135 Verona, Italy.

Federica Budassi (F)

Aptuit, an Evotec Company, 37135 Verona, Italy.

Laura Caberlotto (L)

Aptuit, an Evotec Company, 37135 Verona, Italy.

Peng Gao (P)

WuXi AppTec, Tianjin 300456, PR China.

Cristiana Griffante (C)

Aptuit, an Evotec Company, 37135 Verona, Italy.

Xinying Liu (X)

WuXi AppTec, Tianjin 300456, PR China.

Marco Migliore (M)

Aptuit, an Evotec Company, 37135 Verona, Italy.

Feifei Qiao (F)

WuXi AppTec, Tianjin 300456, PR China.

Fabio Maria Sabbatini (FM)

Aptuit, an Evotec Company, 37135 Verona, Italy.

Anna Sava (A)

Aptuit, an Evotec Company, 37135 Verona, Italy.

Mingliang Zhang (M)

WuXi AppTec, Tianjin 300456, PR China.

Holly J Carlisle (HJ)

ESCAPE Bio, South San Francisco, CA 94080, United States.

Classifications MeSH