Pembrolizumab with or Without Lenvatinib as First-line Therapy for Patients with Advanced Urothelial Carcinoma (LEAP-011): A Phase 3, Randomized, Double-Blind Trial.

Bladder cancer Checkpoint inhibitor Cisplatin Ineligible Immunotherapy Lenvatinib Pembrolizumab Platinum ineligible Urothelial carcinoma

Journal

European urology
ISSN: 1873-7560
Titre abrégé: Eur Urol
Pays: Switzerland
ID NLM: 7512719

Informations de publication

Date de publication:
29 Sep 2023
Historique:
received: 03 02 2023
revised: 07 08 2023
accepted: 18 08 2023
medline: 2 10 2023
pubmed: 2 10 2023
entrez: 1 10 2023
Statut: aheadofprint

Résumé

Pembrolizumab plus lenvatinib has shown antitumor activity and acceptable safety in patients with platinum-refractory urothelial carcinoma (UC). To evaluate pembrolizumab plus either lenvatinib or placebo as first-line therapy for advanced UC in the phase 3 LEAP-011 study. Patients with advanced UC who were ineligible for cisplatin-based therapy or any platinum-based chemotherapy were enrolled. Patients were randomly assigned (1:1) to pembrolizumab 200 mg intravenously every 3 wk plus either lenvatinib 20 mg or placebo orally once daily. Dual primary endpoints were progression-free survival (PFS) and overall survival (OS). An external data monitoring committee (DMC) regularly reviewed safety and efficacy data every 3 mo. Between June 25, 2019 and July 21, 2021, 487 patients were allocated to receive lenvatinib plus pembrolizumab (n = 245) or placebo plus pembrolizumab (n = 242). The median time from randomization to the data cutoff date (July 26, 2021) was 12.8 mo (interquartile range, 6.9-19.3). The median PFS was 4.5 mo in the combination arm and 4.0 mo in the pembrolizumab arm (hazard ratio [HR] 0.90 [95% confidence interval {CI} 0.72-1.14]). The median OS was 11.8 mo for the combination arm and 12.9 mo for the pembrolizumab arm (HR 1.14 [95% CI 0.87-1.48]). Grade 3-5 adverse events attributed to trial treatment occurred in 123 of 241 patients (51%) treated with lenvatinib plus pembrolizumab and in 66 of 242 patients (27%) treated with placebo plus pembrolizumab. This trial was terminated earlier than initially planned based on recommendation from the DMC. The benefit-to-risk ratio for first-line lenvatinib plus pembrolizumab was not considered favorable versus pembrolizumab plus placebo as first-line therapy in patients with advanced UC. Lenvatinib plus pembrolizumab was not more effective than pembrolizumab plus placebo in patients with advanced urothelial carcinoma.

Sections du résumé

BACKGROUND BACKGROUND
Pembrolizumab plus lenvatinib has shown antitumor activity and acceptable safety in patients with platinum-refractory urothelial carcinoma (UC).
OBJECTIVE OBJECTIVE
To evaluate pembrolizumab plus either lenvatinib or placebo as first-line therapy for advanced UC in the phase 3 LEAP-011 study.
DESIGN, SETTING, AND PARTICIPANTS METHODS
Patients with advanced UC who were ineligible for cisplatin-based therapy or any platinum-based chemotherapy were enrolled.
INTERVENTION METHODS
Patients were randomly assigned (1:1) to pembrolizumab 200 mg intravenously every 3 wk plus either lenvatinib 20 mg or placebo orally once daily.
OUTCOME MEASUREMENTS AND STATISTICAL ANALYSIS METHODS
Dual primary endpoints were progression-free survival (PFS) and overall survival (OS). An external data monitoring committee (DMC) regularly reviewed safety and efficacy data every 3 mo.
RESULTS AND LIMITATIONS CONCLUSIONS
Between June 25, 2019 and July 21, 2021, 487 patients were allocated to receive lenvatinib plus pembrolizumab (n = 245) or placebo plus pembrolizumab (n = 242). The median time from randomization to the data cutoff date (July 26, 2021) was 12.8 mo (interquartile range, 6.9-19.3). The median PFS was 4.5 mo in the combination arm and 4.0 mo in the pembrolizumab arm (hazard ratio [HR] 0.90 [95% confidence interval {CI} 0.72-1.14]). The median OS was 11.8 mo for the combination arm and 12.9 mo for the pembrolizumab arm (HR 1.14 [95% CI 0.87-1.48]). Grade 3-5 adverse events attributed to trial treatment occurred in 123 of 241 patients (51%) treated with lenvatinib plus pembrolizumab and in 66 of 242 patients (27%) treated with placebo plus pembrolizumab. This trial was terminated earlier than initially planned based on recommendation from the DMC.
CONCLUSIONS CONCLUSIONS
The benefit-to-risk ratio for first-line lenvatinib plus pembrolizumab was not considered favorable versus pembrolizumab plus placebo as first-line therapy in patients with advanced UC.
PATIENT SUMMARY RESULTS
Lenvatinib plus pembrolizumab was not more effective than pembrolizumab plus placebo in patients with advanced urothelial carcinoma.

Identifiants

pubmed: 37778952
pii: S0302-2838(23)03064-6
doi: 10.1016/j.eururo.2023.08.012
pii:
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

Copyright © 2023 Merck Sharp & Dohme LLC., a subsidiary of Merck & Co., Inc., Rahway, NJ, USA, The Authors. Published by Elsevier B.V. All rights reserved.

Auteurs

Nobuaki Matsubara (N)

National Cancer Center Hospital East, Chiba, Japan.

Ronald de Wit (R)

Erasmus MC Cancer Institute, Rotterdam, The Netherlands.

Arjun Vasant Balar (AV)

Perlmutter Cancer Center, NYU Langone Health, New York, NY, USA.

Arlene O Siefker-Radtke (AO)

The University of Texas MD Anderson Cancer Center, Houston, TX, USA.

Jakub Zolnierek (J)

LUX MED Onkologia Hospital, Warsaw, Poland.

Tibor Csoszi (T)

Jász-Nagykun-Szolnok County Hospital, Szolnok, Hungary.

Sang Joon Shin (SJ)

Yosnei University College of Medicine, Seoul, South Korea.

Se Hoon Park (SH)

Samsung Medical Center, Sungkyunkwan University School of Medicine, Seoul, South Korea.

Vagif Atduev (V)

Volga District Medical Center, Federal Medical-Biological Agency, Nizhny Novgorod, Russia.

Mahmut Gumus (M)

Istanbul Medeniyet University, Istanbul, Turkey.

Yu-Li Su (YL)

Kaohsiung Chang Gung Memorial Hospital and Chang Gung University College of Medicine, Kaohsiung, Taiwan.

Saziye Burcak Karaca (SB)

Tülay Aktaş Onkoloji Hastanesi, İzmir Bornova, Turkey.

Hernán Javier Cutuli (HJ)

Institute for Diagnosis and Metabolic Research (IDIM), Buenos Aires, Argentina.

Mehmet A N Sendur (MAN)

Ankara Yildirim Beyazıt University Faculty of Medicine and Ankara City Hospital, Ankara, Turkey.

Liji Shen (L)

Merck & Co., Inc., Rahway, NJ, USA.

Karen O'Hara (K)

Eisai LTD, Hatfield, UK.

Chinyere E Okpara (CE)

Eisai LTD, Hatfield, UK.

Sonia Franco (S)

Merck & Co., Inc., Rahway, NJ, USA.

Blanca Homet Moreno (BH)

Merck & Co., Inc., Rahway, NJ, USA.

Petros Grivas (P)

University of Washington, Fred Hutchinson Cancer Center, Seattle, WA, USA. Electronic address: pgrivas@uw.edu.

Yohann Loriot (Y)

Gustave Roussy, Cancer Campus, Villejuif, France; Université Paris-Saclay, Villejuif, France. Electronic address: Yohann.loriot@gustaveroussy.fr.

Classifications MeSH