Three-month life expectancy as inclusion criterion for clinical trials in advanced pancreatic cancer: is it really a valid tool for patient selection?

Clinical trial Inclusion criterion Pancreatic cancer Prognosis

Journal

Clinical & translational oncology : official publication of the Federation of Spanish Oncology Societies and of the National Cancer Institute of Mexico
ISSN: 1699-3055
Titre abrégé: Clin Transl Oncol
Pays: Italy
ID NLM: 101247119

Informations de publication

Date de publication:
May 2024
Historique:
received: 05 07 2023
accepted: 05 09 2023
pubmed: 5 10 2023
medline: 5 10 2023
entrez: 4 10 2023
Statut: ppublish

Résumé

To analyze the 3-month life expectancy rate in pancreatic cancer (PC) patients treated within prospective trials from the German AIO study group. A pooled analysis was conducted for patients with advanced PC that were treated within five phase II/III studies conducted between 1997 and 2017 (Gem/Cis, Ro96, RC57, ACCEPT, RASH). The primary goal for the current report was to identify the actual 3-month survival rate, a standard inclusion criterion in oncology trials. Overall, 912 patients were included, 83% had metastatic and 17% locally advanced PC; the estimated median overall survival (OS) was 7.1 months. Twenty-one percent of the participants survived < 3 months, with a range from 26% in RC57 to 15% in RASH. Significant predictors for not reaching 3-month OS were > 1 previous treatment line (p < 0.001) and performance status (p < 0.001). Despite the definition of a life expectancy of > 3 months as a standard inclusion criterion in clinical trials for advanced PC, a significant proportion of study patients does not survive > 3 months. NCT00440167 (AIO-PK0104), NCT01729481 (RASH), NCT01728818 (ACCEPT).

Identifiants

pubmed: 37794220
doi: 10.1007/s12094-023-03323-1
pii: 10.1007/s12094-023-03323-1
doi:

Banques de données

ClinicalTrials.gov
['NCT01729481', 'NCT00440167', 'NCT01728818']

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1268-1272

Informations de copyright

© 2023. The Author(s).

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Auteurs

Lena Weiss (L)

Department of Medicine III, University Hospital, LMU Munich, Munich, Germany.
Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany.

Volker Heinemann (V)

Department of Medicine III, University Hospital, LMU Munich, Munich, Germany.
Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany.
German Cancer Consortium (DKTK), Partner Site Munich, Munich, Germany.

Laura E Fischer (LE)

Department of Medicine III, University Hospital, LMU Munich, Munich, Germany.
Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany.

Frank Gieseler (F)

Department of Hematology and Oncology, University Hospital Schleswig-Holstein-Campus Lübeck, Lübeck, Germany.

Thomas Hoehler (T)

Department of Medicine I, Prosper Hospital, Recklinghausen, Germany.

Julia Mayerle (J)

Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany.
Department of Medicine II, University Hospital, LMU Munich, Munich, Germany.

Detlef Quietzsch (D)

Department of Medical Oncology, Klinikum Chemnitz, Chemnitz, Germany.

Anke Reinacher-Schick (A)

Department of Hematology and Oncology, St. Josef Hospital, Ruhr University, Bochum, Germany.

Michael Schenk (M)

Department of Hematology and Oncology, Klinikum Barmherzige Brüder, Regensburg, Germany.

Gernot Seipelt (G)

Onkologie Main-Taunus, Bad Soden, Germany.

Jens T Siveke (JT)

West German Cancer Center, Bridge Institute of Experimental Tumor Therapy, University Hospital Essen, University of Duisburg-Essen, Essen, Germany.
Division of Solid Tumor Translational Oncology, German Cancer Consortium (DKTK Partner Site Essen) and German Cancer Research Center, DKFZ, Heidelberg, Germany.

Michael Stahl (M)

Department of Medical Oncology, Evang. Kliniken Essen-Mitte, Essen, Germany.

Ursula Vehling-Kaiser (U)

MVZ Dr. Vehling-Kaiser GmbH, Landshut, Germany.

Dirk T Waldschmidt (DT)

Department of Gastroenterology and Hepatology, University of Cologne, Cologne, Germany.

Klara Dorman (K)

Department of Medicine III, University Hospital, LMU Munich, Munich, Germany.
Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany.
German Cancer Consortium (DKTK), Partner Site Munich, Munich, Germany.

Danmei Zhang (D)

Department of Medicine III, University Hospital, LMU Munich, Munich, Germany.
Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany.
German Cancer Consortium (DKTK), Partner Site Munich, Munich, Germany.

C Benedikt Westphalen (CB)

Department of Medicine III, University Hospital, LMU Munich, Munich, Germany.
Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany.

Michael von Bergwelt-Baildon (M)

Department of Medicine III, University Hospital, LMU Munich, Munich, Germany.
Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany.
German Cancer Consortium (DKTK), Partner Site Munich, Munich, Germany.

Stefan Boeck (S)

Department of Medicine III, University Hospital, LMU Munich, Munich, Germany.
Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany.
German Cancer Consortium (DKTK), Partner Site Munich, Munich, Germany.

Michael Haas (M)

Department of Medicine III, University Hospital, LMU Munich, Munich, Germany. michael.haas@med.uni-muenchen.de.
Comprehensive Cancer Center, University Hospital, LMU Munich, Munich, Germany. michael.haas@med.uni-muenchen.de.

Classifications MeSH