Determinants of Kidney Failure in Primary Hyperoxaluria Type 1: Findings of the European Hyperoxaluria Consortium.

kidney failure nephrocalcinosis primary hyperoxaluria urinary glycolate urinary oxalate urolithiasis

Journal

Kidney international reports
ISSN: 2468-0249
Titre abrégé: Kidney Int Rep
Pays: United States
ID NLM: 101684752

Informations de publication

Date de publication:
Oct 2023
Historique:
received: 11 05 2023
revised: 10 07 2023
accepted: 24 07 2023
medline: 18 10 2023
pubmed: 18 10 2023
entrez: 18 10 2023
Statut: epublish

Résumé

Primary hyperoxaluria type 1 (PH1) has a highly heterogeneous disease course. Apart from the c.508G>A (p.Gly170Arg) In this retrospective study of 932 patients with PH1 included in the OxalEurope registry, we analyzed genotype-phenotype correlations as well as the impact of nephrocalcinosis, urolithiasis, and urinary oxalate and glycolate excretion on the development of kidney failure, using survival and mixed model analyses. The risk of developing kidney failure was the highest for 175 vitamin-B6 unresponsive ("null") homozygotes and lowest for 155 patients with c.508G>A and c.454T>A (p.Phe152Ile) variants, with a median age of onset of kidney failure of 7.8 and 31.8 years, respectively. Fifty patients with c.731T>C (p.Ile244Thr) homozygote variants had better kidney survival than null homozygotes ( In conclusion, homozygosity for

Identifiants

pubmed: 37849991
doi: 10.1016/j.ekir.2023.07.025
pii: S2468-0249(23)01404-3
pmc: PMC10577369
doi:

Types de publication

Journal Article

Langues

eng

Pagination

2029-2042

Commentaires et corrections

Type : CommentIn

Informations de copyright

© 2023 International Society of Nephrology. Published by Elsevier Inc.

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Auteurs

Elisabeth L Metry (EL)

Department of Pediatric Nephrology, Emma Children's Hospital, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.

Sander F Garrelfs (SF)

Department of Pediatric Nephrology, Emma Children's Hospital, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.

Lisa J Deesker (LJ)

Department of Pediatric Nephrology, Emma Children's Hospital, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.

Cecile Acquaviva (C)

Service de Biochimie et Biologie Moléculaire, UM Pathologies Héréditaires du Métabolisme et du Globule Rouge, Hospices Civils de Lyon, France.

Viola D'Ambrosio (V)

Department of Nephrology, Catholic University of the Sacred Heart, Rome, Italy.

Justine Bacchetta (J)

Centre de Référence des Maladies Rares Néphrogones, Hospices Civils de Lyon et Université Claude-Bernard Lyon 1, Lyon, France.

Bodo B Beck (BB)

Institute of Human Genetics, Center for Molecular Medicine Cologne, University Hospital of Cologne, Cologne, Germany.
Center for Rare and Hereditary Kidney Disease Cologne, University Hospital of Cologne, Cologne, Germany.

Pierre Cochat (P)

Centre de Référence des Maladies Rares Néphrogones, Hospices Civils de Lyon et Université Claude-Bernard Lyon 1, Lyon, France.

Laure Collard (L)

Department of Pediatric Nephrology, Center Hospitalier Universitaire Liège, Liège, Belgium.

Julien Hogan (J)

Department of Pediatric Nephrology, Assistance Publique-Hôpitaux de Paris Robert-Debré, University of Paris, Paris, France.

Pietro Manuel Ferraro (PM)

Department of Nephrology, Catholic University of the Sacred Heart, Rome, Italy.

Casper F M Franssen (CFM)

Department of Internal Medicine, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands.

Jérôme Harambat (J)

Department of Pediatrics, Pediatric Nephrology Unit, Bordeaux University Hospital, Bordeaux, France.

Sally-Anne Hulton (SA)

Department of Nephrology, Birmingham Women's and Children's Hospital NHS Foundation Trust, Birmingham, UK.

Graham W Lipkin (GW)

Department of Nephrology, University Hospitals Birmingham NHS Foundation Trust, Birmingham, UK.

Giorgia Mandrile (G)

Genetic Unit and Thalassemia Center, San Luigi University Hospital, Orbassano, Italy.

Cristina Martin-Higueras (C)

Institute of Biomedical Technology, CIBERER, University of Laguna, San Cristóbal de La Laguna, Spain.

Nilufar Mohebbi (N)

Division of Nephrology, University Hospital Zurich, Zurich, Switzerland.

Shabbir H Moochhala (SH)

UCL Department of Renal Medicine, Royal Free Hospital, London, UK.

Thomas J Neuhaus (TJ)

Department of Pediatrics, Children's Hospital Lucerne, Lucerne, Switzerland.

Larisa Prikhodina (L)

Department of Inherited and Acquired Kidney Diseases, Veltishev Research and Clinical Institute for Pediatrics and Pediatric Surgery of the Pirogov Russian National Research Medical University, Moscow, Russia.

Eduardo Salido (E)

Department of Pathology, Center for Biomedical Research on Rare Diseases, Hospital Universitario Canarias, Universidad La Laguna, Tenerife, Spain.

Rezan Topaloglu (R)

Division of Pediatric Nephrology, Department of Pediatrics, Hacettepe University Faculty of Medicine, Ankara, Turkey.

Michiel J S Oosterveld (MJS)

Department of Pediatric Nephrology, Emma Children's Hospital, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.

Jaap W Groothoff (JW)

Department of Pediatric Nephrology, Emma Children's Hospital, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.

Hessel Peters-Sengers (H)

Center for Experimental and Molecular Medicine, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.

Classifications MeSH