A Prognostic Model to Predict Ruxolitinib Discontinuation and Death in Patients with Myelofibrosis.

myelofibrosis prognostic model ruxolitinib

Journal

Cancers
ISSN: 2072-6694
Titre abrégé: Cancers (Basel)
Pays: Switzerland
ID NLM: 101526829

Informations de publication

Date de publication:
17 Oct 2023
Historique:
received: 11 09 2023
revised: 09 10 2023
accepted: 16 10 2023
medline: 28 10 2023
pubmed: 28 10 2023
entrez: 28 10 2023
Statut: epublish

Résumé

Most patients with myelofibrosis (MF) discontinue ruxolitinib (JAK1/JAK2 inhibitor) in the first 5 years of therapy due to therapy failure. As the therapeutic possibilities of MF are expanding, it is critical to identify patients predisposed to early ruxolitinib monotherapy failure and worse outcomes. We investigated predictors of early ruxolitinib discontinuation and death on therapy in 889 patients included in the "RUX-MF" retrospective study. Overall, 172 patients were alive on ruxolitinib after ≥5 years (long-term ruxolitinib, LTR), 115 patients were alive but off ruxolitinib after ≥5 yrs (short-term RUX, STR), and 123 patients died while on ruxolitinib after <5 yrs (early death on ruxolitinib, EDR). The cumulative incidence of the blast phase was similar in LTR and STR patients (

Identifiants

pubmed: 37894394
pii: cancers15205027
doi: 10.3390/cancers15205027
pmc: PMC10605705
pii:
doi:

Types de publication

Journal Article

Langues

eng

Subventions

Organisme : Ministero della Salute
ID : RC-2023-2778976

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Auteurs

Francesca Palandri (F)

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Istituto di Ematologia "Seràgnoli", 40138 Bologna, Italy.

Giuseppe A Palumbo (GA)

Department of Scienze Mediche, Chirurgiche e Tecnologie Avanzate "G.F. Ingrassia", University of Catania, 95124 Catania, Italy.

Massimiliano Bonifacio (M)

Department of Engineering for Innovation Medicine, Section of Innovation Biomedicine, Hematology Area, University of Verona, 37129 Verona, Italy.

Elena M Elli (EM)

Hematology Division, Fondazione IRCCS, San Gerardo dei Tintori, 20900 Monza, Italy.

Mario Tiribelli (M)

Division of Hematology and BMT, Azienda Sanitaria Universitaria Integrata di Udine, 33100 Udine, Italy.

Giuseppe Auteri (G)

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Istituto di Ematologia "Seràgnoli", 40138 Bologna, Italy.
Medicina Specialistica, Diagnostica e Sperimentale, Università di Bologna, 40126 Bologna, Italy.

Malgorzata M Trawinska (MM)

Division of Hematology, Sant'Eugenio Hospital, Tor Vergata University, 00133 Rome, Italy.

Nicola Polverelli (N)

Unit of Blood Diseases and Stem Cells Transplantation, Department of Clinical and Experimental Sciences, University of Brescia, ASST Spedali Civili of Brescia, 25121 Brescia, Italy.

Giulia Benevolo (G)

Città della Salute e della Scienza Hospital, University Hematology Division, 10126 Torino, Italy.

Alessia Tieghi (A)

Department of Hematology, Azienda USL-IRCCS di Reggio Emilia, 42122 Reggio Emilia, Italy.

Fabrizio Cavalca (F)

Hematology Division, Fondazione IRCCS, San Gerardo dei Tintori, 20900 Monza, Italy.

Giovanni Caocci (G)

Hematology Unit, Department of Medical Sciences, University of Cagliari, 09124 Cagliari, Italy.

Eloise Beggiato (E)

Città della Salute e della Scienza Hospital, University Hematology Division, 10126 Torino, Italy.

Gianni Binotto (G)

Unit of Hematology and Clinical Immunology, University of Padova, 35122 Padova, Italy.

Francesco Cavazzini (F)

Division of Hematology, University of Ferrara, 44121 Ferrara, Italy.

Maurizio Miglino (M)

Clinic of Hematology, Department of Internal Medicine (DiMI), University of Genoa, 16126 Genova, Italy.
IRCCS Policlinico San Martino, 16132 Genova, Italy.

Costanza Bosi (C)

Division of Haematology, AUSL di Piacenza, 29121 Piacenza, Italy.

Monica Crugnola (M)

Division of Hematology, Azienda Ospedaliero, Universitaria di Parma, 43126 Parma, Italy.

Monica Bocchia (M)

Hematology Unit, Azienda Ospedaliera Universitaria Senese, University of Siena, 53100 Siena, Italy.

Bruno Martino (B)

Division of Hematology, Azienda Ospedaliera 'Bianchi Melacrino Morelli', 89124 Reggio Calabria, Italy.

Novella Pugliese (N)

Department of Clinical Medicine and Surgery, Hematology Section, University of Naples "Federico II", 80138 Naples, Italy.

Marta Venturi (M)

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Istituto di Ematologia "Seràgnoli", 40138 Bologna, Italy.
Medicina Specialistica, Diagnostica e Sperimentale, Università di Bologna, 40126 Bologna, Italy.

Alessandro Isidori (A)

Haematology and Haematopoietic Stem Cell Transplant Center, AORMN Hospital, 61100 Pesaro, Italy.

Daniele Cattaneo (D)

Hematology Division, Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, 20122 Milan, Italy.

Mauro Krampera (M)

Department of Engineering for Innovation Medicine, Section of Innovation Biomedicine, Hematology Area, University of Verona, 37129 Verona, Italy.

Fabrizio Pane (F)

Department of Clinical Medicine and Surgery, Hematology Section, University of Naples "Federico II", 80138 Naples, Italy.

Daniela Cilloni (D)

Department of Clinical and Biological Sciences, University of Turin, 10124 Turin, Italy.

Gianpietro Semenzato (G)

Unit of Hematology and Clinical Immunology, University of Padova, 35122 Padova, Italy.

Roberto M Lemoli (RM)

Clinic of Hematology, Department of Internal Medicine (DiMI), University of Genoa, 16126 Genova, Italy.
IRCCS Policlinico San Martino, 16132 Genova, Italy.

Antonio Cuneo (A)

Division of Hematology, University of Ferrara, 44121 Ferrara, Italy.

Elisabetta Abruzzese (E)

Division of Hematology, Sant'Eugenio Hospital, Tor Vergata University, 00133 Rome, Italy.

Filippo Branzanti (F)

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Istituto di Ematologia "Seràgnoli", 40138 Bologna, Italy.

Nicola Vianelli (N)

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Istituto di Ematologia "Seràgnoli", 40138 Bologna, Italy.

Michele Cavo (M)

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Istituto di Ematologia "Seràgnoli", 40138 Bologna, Italy.
Medicina Specialistica, Diagnostica e Sperimentale, Università di Bologna, 40126 Bologna, Italy.

Florian Heidel (F)

Internal Medicine II, Hematology and Oncology, Friedrich-Schiller-University Medical Center, 07747 Jena, Germany.

Alessandra Iurlo (A)

Hematology Division, Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, 20122 Milan, Italy.

Massimo Breccia (M)

Department of Translational and Precision Medicine, Sapienza University, 00185 Rome, Italy.

Classifications MeSH