Progressive Brain Atrophy in Multiple System Atrophy: A Longitudinal, Multicenter, Magnetic Resonance Imaging Study.

MRI brain atrophy multiple system atrophy progression

Journal

Movement disorders : official journal of the Movement Disorder Society
ISSN: 1531-8257
Titre abrégé: Mov Disord
Pays: United States
ID NLM: 8610688

Informations de publication

Date de publication:
07 Nov 2023
Historique:
revised: 27 08 2023
received: 10 06 2023
accepted: 28 09 2023
medline: 7 11 2023
pubmed: 7 11 2023
entrez: 7 11 2023
Statut: aheadofprint

Résumé

To determine the rates of brain atrophy progression in vivo in patients with multiple system atrophy (MSA). Surrogate biomarkers of disease progression are a major unmet need in MSA. Small-scale longitudinal studies in patients with MSA using magnetic resonance imaging (MRI) to assess progression of brain atrophy have produced inconsistent results. In recent years, novel MRI post-processing methods have been developed enabling reliable quantification of brain atrophy in an automated fashion. Serial 3D-T1-weighted MRI assessments (baseline and after 1 year of follow-up) of 43 patients with MSA were analyzed and compared to a cohort of early-stage Parkinson's disease (PD) patients and healthy controls (HC). FreeSurfer's longitudinal analysis stream was used to determine the brain atrophy rates in an observer-independent fashion. Mean ages at baseline were 64.4 ± 8.3, 60.0 ± 7.5, and 59.8 ± 9.2 years in MSA, PD patients and HC, respectively. A mean disease duration at baseline of 4.1 ± 2.5 years in MSA patients and 2.3 ± 1.4 years in PD patients was observed. Brain regions chiefly affected by MSA pathology showed progressive atrophy with annual rates of atrophy for the cerebellar cortex, cerebellar white matter, pons, and putamen of -4.24 ± 6.8%, -8.22 ± 8.8%, -4.67 ± 4.9%, and - 4.25 ± 4.9%, respectively. Similar to HC, atrophy rates in PD patients were minimal with values of -0.41% ± 1.8%, -1.47% ± 4.1%, -0.04% ± 1.8%, and -1.54% ± 2.2% for cerebellar cortex, cerebellar white matter, pons, and putamen, respectively. Patients with MSA show significant brain volume loss over 12 months, and cerebellar, pontine, and putaminal volumes were the most sensitive to change in mid-stage disease. © 2023 The Authors. Movement Disorders published by Wiley Periodicals LLC on behalf of International Parkinson and Movement Disorder Society.

Sections du résumé

OBJECTIVE OBJECTIVE
To determine the rates of brain atrophy progression in vivo in patients with multiple system atrophy (MSA).
BACKGROUND BACKGROUND
Surrogate biomarkers of disease progression are a major unmet need in MSA. Small-scale longitudinal studies in patients with MSA using magnetic resonance imaging (MRI) to assess progression of brain atrophy have produced inconsistent results. In recent years, novel MRI post-processing methods have been developed enabling reliable quantification of brain atrophy in an automated fashion.
METHODS METHODS
Serial 3D-T1-weighted MRI assessments (baseline and after 1 year of follow-up) of 43 patients with MSA were analyzed and compared to a cohort of early-stage Parkinson's disease (PD) patients and healthy controls (HC). FreeSurfer's longitudinal analysis stream was used to determine the brain atrophy rates in an observer-independent fashion.
RESULTS RESULTS
Mean ages at baseline were 64.4 ± 8.3, 60.0 ± 7.5, and 59.8 ± 9.2 years in MSA, PD patients and HC, respectively. A mean disease duration at baseline of 4.1 ± 2.5 years in MSA patients and 2.3 ± 1.4 years in PD patients was observed. Brain regions chiefly affected by MSA pathology showed progressive atrophy with annual rates of atrophy for the cerebellar cortex, cerebellar white matter, pons, and putamen of -4.24 ± 6.8%, -8.22 ± 8.8%, -4.67 ± 4.9%, and - 4.25 ± 4.9%, respectively. Similar to HC, atrophy rates in PD patients were minimal with values of -0.41% ± 1.8%, -1.47% ± 4.1%, -0.04% ± 1.8%, and -1.54% ± 2.2% for cerebellar cortex, cerebellar white matter, pons, and putamen, respectively.
CONCLUSIONS CONCLUSIONS
Patients with MSA show significant brain volume loss over 12 months, and cerebellar, pontine, and putaminal volumes were the most sensitive to change in mid-stage disease. © 2023 The Authors. Movement Disorders published by Wiley Periodicals LLC on behalf of International Parkinson and Movement Disorder Society.

Identifiants

pubmed: 37933745
doi: 10.1002/mds.29633
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Teva Pharmaceutical Industries

Informations de copyright

© 2023 The Authors. Movement Disorders published by Wiley Periodicals LLC on behalf of International Parkinson and Movement Disorder Society.

Références

Krismer F, Wenning GK. Multiple system atrophy: insights into a rare and debilitating movement disorder. Nat Rev Neurol 2017;13(4):232-243.
Poewe W, Stankovic I, Halliday G, et al. Multiple system atrophy. Nat Rev Dis Primers 2022;8(1):56.
Wenning GK, Stankovic I, Vignatelli L, et al. The Movement Disorder Society criteria for the diagnosis of multiple system atrophy. Mov Disord 2022;37(6):1131-1148.
Koga S, Aoki N, Uitti RJ, et al. When DLB, PD, and PSP masquerade as MSA: an autopsy study of 134 patients. Neurology 2015;85(5):1-9.
Pirker W, Asenbaum S, Bencsits G, Prayer D, Gerschlager W, Deecke L, Brücke T. [123I]β-CIT SPECT in multiple system atrophy, progressive supranuclear palsy, and corticobasal degeneration. Mov Disord 2000;15(6):1158-1167.
Walsh RR, Krismer F, Galpern WR, et al. Recommendations of the Global Multiple System Atrophy Research Roadmap Meeting. Neurology 2017;90(2):74-82.
Poewe W, Seppi K, Fitzer-Attas CJ, et al. Efficacy of rasagiline in patients with the parkinsonian variant of multiple system atrophy: a randomised, placebo-controlled trial. Lancet Neurol 2015;14(2):145-152. Available from: http://linkinghub.elsevier.com/retrieve/pii/S1474442214702881
Levin J, Maaß S, Schuberth M, et al. Safety and efficacy of epigallocatechin gallate in multiple system atrophy (PROMESA): a randomised, double-blind, placebo-controlled trial. Lancet Neurol 2019;18(8):724-735.
Paviour DC, Price SL, Jahanshahi M, Lees AJ, Fox NC. Longitudinal MRI in progressive supranuclear palsy and multiple system atrophy: rates and regions of atrophy. Brain 2006;129(Pt 4):1040-1049. Available from: http://www.ncbi.nlm.nih.gov/pubmed/16455792
Reginold W, Lang AE, Marras C, Heyn C, Alharbi M, Mikulis DJ. Longitudinal quantitative MRI in multiple system atrophy and progressive supranuclear palsy. Parkinsonism Relat Disord 2014;20(2):222-225.
Burciu RG, Chung JW, Shukla P, et al. Functional MRI of disease progression in Parkinson disease and atypical parkinsonian syndromes. Neurology 2016;87(7):709-717.
Lee JH, Kim TH, Mun CW, Kim TH, Han YH. Progression of subcortical atrophy and iron deposition in multiple system atrophy: a comparison between clinical subtypes. J Neurol 2015;262(8):1876-1882.
Pellecchia MT, Picillo M, Filla A, et al. Progression of striatal and extrastriatal degeneration in multiple system atrophy: a longitudinal diffusion-weighted MR study. Movement Disord 2011;26(7):1303-1309. Available from: http://www.ncbi.nlm.nih.gov/pubmed/21469200
Brenneis C, Egger K, Scherfler C, Seppi K, Schocke M, Poewe W, Wenning GK. Progression of brain atrophy in multiple system atrophy: a longitudinal VBM study. J Neurol 2007;254(2):191-196.
Seppi K, Schocke MFH, Mair KJ, et al. Progression of putaminal degeneration in multiple system atrophy: a serial diffusion MR study. Neuroimage 2006;31(1):240-245. Available from: http://www.ncbi.nlm.nih.gov/pubmed/16443375
Reuter M, Schmansky NJ, Rosas HD, Fischl B. Within-subject template estimation for unbiased longitudinal image analysis. Neuroimage 2012;61(4):1402-1418.
Gilman S, Wenning GK, Low PA, et al. Second consensus statement on the diagnosis of multiple system atrophy. Neurology 2008;71(9): 670-676.
Péran P, Barbagallo G, Nemmi F, et al. MRI supervised and unsupervised classification of Parkinson's disease and multiple system atrophy. Movement Disord 2018;33(4):600-608.
Foubert-Samier A, Traon APL, Guillet F, et al. Disease progression and prognostic factors in multiple system atrophy: a prospective cohort study. Neurobiol Dis 2020;139:104813.
Wenning GK, Tison F, Seppi K, et al. Development and validation of the Unified Multiple System Atrophy Rating Scale (UMSARS). Movement Disord 2004;19(12):1391-1402. Available from: http://www.ncbi.nlm.nih.gov/pubmed/15452868
Krismer F, Seppi K, Wenning GK, et al. Abnormalities on structural MRI associate with faster disease progression in multiple system atrophy. Parkinsonism Relat Disord 2019;58:23-27. https://doi.org/10.1016/j.parkreldis.2018.08.004
Postuma RB, Berg D, Stern M, et al. MDS clinical diagnostic criteria for Parkinson's disease. Mov Disord 2015;30(12):1591-1601.
Goetz CG, Tilley BC, Shaftman SR, et al. Movement Disorder Society-sponsored revision of the Unified Parkinson's Disease Rating Scale (MDS-UPDRS): scale presentation and clinimetric testing results. Movement Disord 2008;23(15):2129-2170.
Nasreddine ZS, Phillips NA, Bédirian V, et al. The Montreal Cognitive Assessment, MoCA: a brief screening tool for mild cognitive impairment. J Am Geriatr Soc 2005;53(4):695-699.
Heim B, Krismer F, Poewe W, Seppi K. Imaging markers of disease progression in multiple system atrophy. Future Neurol 2019;14(3):FNL24.
Koga S, Dickson DW. Recent advances in neuropathology, biomarkers and therapeutic approach of multiple system atrophy. J Neurology Neurosurg Psychiatry 2018;89(2):175.
Fischl B. FreeSurfer. NeuroImage 2012;62(2):774-781.
Fischl B, Salat DH, Busa E, et al. Whole brain segmentation automated labeling of neuroanatomical structures in the human brain. Neuron 2002;33(3):341-355.
Fischl B, Dale AM. Measuring the thickness of the human cerebral cortex from magnetic resonance images. Proc Natl Acad Sci U S A 2000;97(20):11050-11055.
Fischl B, Van Der Kouwe A, Destrieux C, et al. Automatically parcellating the human cerebral cortex. Cereb Cortex 2004;14(1):11-22.
Reuter M, Rosas HD, Fischl B. Highly accurate inverse consistent registration: a robust approach. Neuroimage 2010;53(4):1181-1196.
Reuter M, Fischl B. Avoiding asymmetry-induced bias in longitudinal image processing. Neuroimage 2011;57(1):19-21.
Iglesias JE, Leemput KV, Bhatt P, et al. Bayesian segmentation of brainstem structures in MRI. Neuroimage 2015;113:1-12.
Ségonne F, Dale AM, Busa E, Glessner M, Salat D, Hahn HK, Fischl B. A hybrid approach to the skull stripping problem in MRI. Neuroimage 2004;22(3):1060-1075.
van Eimeren T, Antonini A, Berg D, et al. Neuroimaging biomarkers for clinical trials in atypical parkinsonian disorders: proposal for a Neuroimaging Biomarker Utility System. Alzheimers Dement (Amst) 2019;11(1):301-309.
Lewis MM, Du G, Lee EY, et al. The pattern of gray matter atrophy in Parkinson's disease differs in cortical and subcortical regions. J Neurol 2016;263(1):68-75.
Fjell AM, Walhovd KB, Fennema-Notestine C, et al. One-year brain atrophy evident in healthy aging. J Neurosci 2009;29(48):15223-15231.
Fjell AM, McEvoy L, Holland D, Dale AM, Walhovd KB, Alzheimer's Disease Neuroimaging Initiative. Brain changes in older adults at very low risk for Alzheimer's disease. J Neurosci 2013;33(19):8237-8242.
Wenning GK, Shlomo YB, Magalhães M, Danie SE, Quinn NP. Clinical features and natural history of multiple system atrophy: an analysis of 100 cases. Brain 1994;117(4):835-845.

Auteurs

Florian Krismer (F)

Department of Neurology, Medical University Innsbruck, Innsbruck, Austria.
Neuroimaging Research Core Facility, Medical University Innsbruck, Innsbruck, Austria.

Patrice Péran (P)

ToNIC, Toulouse NeuroImaging Center, Université de Toulouse, INSERM, UPS, Toulouse, France.

Vincent Beliveau (V)

Department of Neurology, Medical University Innsbruck, Innsbruck, Austria.
Neuroimaging Research Core Facility, Medical University Innsbruck, Innsbruck, Austria.

Klaus Seppi (K)

Department of Neurology, Medical University Innsbruck, Innsbruck, Austria.
Neuroimaging Research Core Facility, Medical University Innsbruck, Innsbruck, Austria.

Germain Arribarat (G)

ToNIC, Toulouse NeuroImaging Center, Université de Toulouse, INSERM, UPS, Toulouse, France.

Anne Pavy-Le Traon (A)

French Reference Center for MSA, Neurology Department, University Hospital of Toulouse and INSERM-Institute of Cardiovascular and Metabolic Diseases (I2MC) UMR1297, Toulouse, France.

Wassilios G Meissner (WG)

CHU Bordeaux, Service de Neurologie des Maladies Neurodégénératives, IMNc, CRMR AMS, Bordeaux, France.
University of Bordeaux, CNRS, IMN, UMR 5293, Bordeaux, France.
Department of Medicine, University of Otago, Christchurch, and New Zealand Brain Research Institute, Christchurch, New Zealand.

Alexandra Foubert-Samier (A)

CHU Bordeaux, Service de Neurologie des Maladies Neurodégénératives, IMNc, CRMR AMS, Bordeaux, France.
University of Bordeaux, CNRS, IMN, UMR 5293, Bordeaux, France.
INSERM, UMR1219, Bordeaux Population Health Research Center, University of Bordeaux, ISPED, Bordeaux, France.

Margherita Fabbri (M)

French Reference Center for MSA, Clinical Investigation Center CIC1436, Departments of Clinical Pharmacology and Neurosciences, NS-Park/FCRIN Network and NeuroToul Center of Excellence for Neurodegeneration, INSERM, University Hospital of Toulouse and University of Toulouse, Toulouse, France.

Michael M Schocke (MM)

Neuroimaging Research Core Facility, Medical University Innsbruck, Innsbruck, Austria.

Mark Forrest Gordon (MF)

Teva Pharmaceuticals, West Chester, Pennsylvania, USA.

Gregor K Wenning (GK)

Department of Neurology, Medical University Innsbruck, Innsbruck, Austria.

Werner Poewe (W)

Department of Neurology, Medical University Innsbruck, Innsbruck, Austria.
Neuroimaging Research Core Facility, Medical University Innsbruck, Innsbruck, Austria.

Olivier Rascol (O)

French Reference Center for MSA, Clinical Investigation Center CIC1436, Departments of Clinical Pharmacology and Neurosciences, NS-Park/FCRIN Network and NeuroToul Center of Excellence for Neurodegeneration, INSERM, University Hospital of Toulouse and University of Toulouse, Toulouse, France.

Christoph Scherfler (C)

Department of Neurology, Medical University Innsbruck, Innsbruck, Austria.
Neuroimaging Research Core Facility, Medical University Innsbruck, Innsbruck, Austria.

Classifications MeSH