Pharmacologic and Genetic Downregulation of Proprotein Convertase Subtilisin/Kexin Type 9 and Survival From Sepsis.

endotoxins lipid regulating agents proprotein convertase subtilisin/kexin type 9 sepsis septic shock

Journal

Critical care explorations
ISSN: 2639-8028
Titre abrégé: Crit Care Explor
Pays: United States
ID NLM: 101746347

Informations de publication

Date de publication:
Nov 2023
Historique:
medline: 13 11 2023
pubmed: 13 11 2023
entrez: 13 11 2023
Statut: epublish

Résumé

Treatments that prevent sepsis complications are needed. Circulating lipid and protein assemblies-lipoproteins play critical roles in clearing pathogens from the bloodstream. We investigated whether early inhibition of proprotein convertase subtilisin/kexin type 9 (PCSK9) may accelerate bloodstream clearance of immunogenic bacterial lipids and improve sepsis outcomes. Genetic and clinical epidemiology, and experimental models. Human genetics cohorts, secondary analysis of a phase 3 randomized clinical trial enrolling patients with cardiovascular disease (Evaluation of Cardiovascular Outcomes After an Acute Coronary Syndrome During Treatment With Alirocumab [ODYSSEY OUTCOMES]; NCT01663402), and experimental murine models of sepsis. Nine human cohorts with sepsis (total Observational human cohort studies used genetic Across human cohort studies, the effect estimate for 28-day mortality after sepsis diagnosis associated with genetic PCSK9 inhibition may improve clinical outcomes in sepsis in preventive, pretreatment settings.

Identifiants

pubmed: 37954898
doi: 10.1097/CCE.0000000000000997
pmc: PMC10635596
doi:

Banques de données

ClinicalTrials.gov
['NCT01663402']

Types de publication

Journal Article

Langues

eng

Pagination

e0997

Informations de copyright

Copyright © 2023 The Authors. Published by Wolters Kluwer Health, Inc. on behalf of the Society of Critical Care Medicine.

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Auteurs

Patrick R Lawler (PR)

Department of Medicine, McGill University Health Centre, McGill University, Montreal, QC, Canada.
Department of Medicine, Peter Munk Cardiac Centre at University Health Network, University of Toronto, Toronto, ON, Canada.
Division of Cardiology, Department of Medicine, University of Toronto, Toronto, ON, Canada.

Garen Manvelian (G)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY.

Alida Coppi (A)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY.

Amy Damask (A)

Regeneron Genetics Center, Tarrytown, NY.

Michael N Cantor (MN)

Regeneron Genetics Center, Tarrytown, NY.

Manuel A R Ferreira (MAR)

Regeneron Genetics Center, Tarrytown, NY.

Charles Paulding (C)

Regeneron Genetics Center, Tarrytown, NY.

Nilanjana Banerjee (N)

Regeneron Genetics Center, Tarrytown, NY.

Dadong Li (D)

Regeneron Genetics Center, Tarrytown, NY.

Susan Jorgensen (S)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY.

Richa Attre (R)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY.

David J Carey (DJ)

Department of Molecular and Functional Genomics, Geisinger Medical Center, Danville, PA.

Kristi Krebs (K)

Estonian Genome Centre, Institute of Genomics, University of Tartu, Tartu, Estonia.

Lili Milani (L)

Estonian Genome Centre, Institute of Genomics, University of Tartu, Tartu, Estonia.

Kristian Hveem (K)

K.G. Jebsen Center for Genetic Epidemiology, Department of Public Health and Nursing, NTNU, Norwegian University of Science and Technology, Trondheim, Norway.
HUNT Research Center, Department of Public Health and Nursing, NTNU, Norwegian University of Science and Technology, Levanger, Norway.

Jan K Damås (JK)

Gemini Center for Sepsis Research, Department of Circulation and Medical Imaging, NTNU, Norwegian University of Science and Technology, Trondheim, Norway.
Department of Infectious Diseases, St Olav's Hospital, Trondheim University Hospital, Trondheim, Norway.
Department of Clinical and Molecular Medicine, Norwegian University of Science and Technology, Trondheim, Norway.

Erik Solligård (E)

Gemini Center for Sepsis Research, Department of Circulation and Medical Imaging, NTNU, Norwegian University of Science and Technology, Trondheim, Norway.
Department of Medical Quality, Møre and Romsdal Hospital Trust, Ålesund, Norway.

Stefan Stender (S)

Department of Clinical Biochemistry, Copenhagen University Hospital - Rigshospitalet, Copenhagen, Denmark.

Anne Tybjærg-Hansen (A)

Department of Clinical Biochemistry, Copenhagen University Hospital - Rigshospitalet, Copenhagen, Denmark.

Børge G Nordestgaard (BG)

Department of Clinical Biochemistry, Copenhagen University Hospital - Herlev Gentofte, University of Copenhagen, Copenhagen, Denmark.

Tamara Hernandez-Beeftink (T)

Research Unit, Hospital Universitario N.S. de Candelaria, Universidad de La Laguna, Santa Cruz de Tenerife, Spain.
Research Unit, Hospital Universitario de Gran Canaria Dr. Negrin, Las Palmas de Gran Canaria, Spain.

Tormod Rogne (T)

Gemini Center for Sepsis Research, Department of Circulation and Medical Imaging, NTNU, Norwegian University of Science and Technology, Trondheim, Norway.
Department of Chronic Disease Epidemiology and Center for Perinatal, Pediatric and Environmental Epidemiology, Yale School of Public Health, New Haven, CT.
Centre for Fertility and Health, Norwegian Institute of Public Health, Oslo, Norway.

Carlos Flores (C)

Research Unit, Hospital Universitario N.S. de Candelaria, Universidad de La Laguna, Santa Cruz de Tenerife, Spain.
CIBER de Enfermedades Respiratorias (CIBERES), Instituto de Salud Carlos III, Madrid, Spain.
Genomics Division, Instituto Tecnológico y de Energías Renovables (ITER), Santa Cruz de Tenerife, Spain.
Faculty of Health Sciences, University Fernando Pessoa Canarias, Las Palmas de Gran Canaria, Canary Islands, Spain.

Jesús Villar (J)

Research Unit, Hospital Universitario de Gran Canaria Dr. Negrin, Las Palmas de Gran Canaria, Spain.
CIBER de Enfermedades Respiratorias (CIBERES), Instituto de Salud Carlos III, Madrid, Spain.
Li Ka Shing Knowledge Institute, St. Michael's Hospital, Toronto, ON, Canada.

Keith R Walley (KR)

Centre for Heart Lung Innovation, University of British Columbia, Vancouver, BC, Canada.

Vincent X Liu (VX)

Kaiser Permanente Northern California, Division of Research, Oakland, CA.

Alison E Fohner (AE)

Kaiser Permanente Northern California, Division of Research, Oakland, CA.
Department of Epidemiology, School of Public Health, University of Washington, Seattle, WA.

Luca A Lotta (LA)

Regeneron Genetics Center, Tarrytown, NY.

Christos A Kyratsous (CA)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY.

Mark W Sleeman (MW)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY.

Michel Scemama (M)

Sanofi, Chilly-Mazarin, France.

Richard DelGizzi (R)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY.

Robert Pordy (R)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY.

Julie E Horowitz (JE)

Regeneron Genetics Center, Tarrytown, NY.

Aris Baras (A)

Regeneron Pharmaceuticals, Inc., Tarrytown, NY.
Regeneron Genetics Center, Tarrytown, NY.

Greg S Martin (GS)

Pulmonary, Allergy, Critical Care and Sleep Medicine, Emory University, Atlanta, GA.
Grady Memorial Hospital, Atlanta, GA.

Philippe Gabriel Steg (PG)

Université de Paris, INSERM U-1148 F75018 Paris, France and Assistance Publique-Hôpitaux de Paris, Paris, France.

Gregory G Schwartz (GG)

Division of Cardiology, University of Colorado School of Medicine, Aurora, CA.

Michael Szarek (M)

Division of Cardiology, University of Colorado School of Medicine, Aurora, CA.
CPC Clinical Research, Aurora, CA.
School of Public Health, Downstate Health Sciences University, Brooklyn, NY.

Shaun G Goodman (SG)

Division of Cardiology, Department of Medicine, University of Toronto, Toronto, ON, Canada.
Li Ka Shing Knowledge Institute, St. Michael's Hospital, Toronto, ON, Canada.
Division of Cardiology, Department of Medicine, St Michael's Hospital, Toronto, ON, Canada.
Canadian VIGOUR Centre, Department of Medicine, University of Alberta, Edmonton, AB, Canada.

Classifications MeSH