CATSHL syndrome, a new family and phenotypic expansion.

CATSHL syndrome FGFR3 LADD syndrome camptodactyly deafness overgrowth scoliosis

Journal

Clinical genetics
ISSN: 1399-0004
Titre abrégé: Clin Genet
Pays: Denmark
ID NLM: 0253664

Informations de publication

Date de publication:
22 Nov 2023
Historique:
revised: 06 11 2023
received: 14 09 2023
accepted: 08 11 2023
medline: 22 11 2023
pubmed: 22 11 2023
entrez: 22 11 2023
Statut: aheadofprint

Résumé

We report the case of a 12-year-old girl and her father who both had marked postnatal tall stature, camptodactyly and clinodactyly, scoliosis and juvenile-onset hearing loss. The CATSHL (CAmptodactyly - Tall stature - Scoliosis - Hearing Loss syndrome) syndrome was suspected, and molecular analysis revealed a hitherto unreported, monoallelic variant c.1861C>T (p.Arg621Cys) in FGFR3. This variant affects the same residue, but is different than, the variant p.Arg621His reported in the two families with dominant CATSHL described so far. Interestingly, peg-shaped incisors were observed in the proband, a feature never reported in CATSHL but typical of another FGFR3-related condition, LADD (Lacrimo - Auricolo - Dento - Digital) syndrome. The FGFR3 p.Arg621Cys variant seems to be a newly identified cause of CATSHL syndrome with some phenotypic overlap with the LADD syndrome.

Identifiants

pubmed: 37990933
doi: 10.1111/cge.14455
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2023 The Authors. Clinical Genetics published by John Wiley & Sons Ltd.

Références

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Auteurs

Silvia Cannova (S)

Università degli Studi di Milano, Milano, Italy.

Camilla Meossi (C)

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milano, Italy.

Federico Grilli (F)

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milano, Italy.

Donatella Milani (D)

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milano, Italy.

Federica Alberti (F)

Università degli Studi di Milano, Milano, Italy.

Claudia Cesaretti (C)

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milano, Italy.

Paola Giovanna Marchisio (PG)

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milano, Italy.
Dipartimento di Fisiopatologia Medico-Chirurgica e dei Trapianti, Università degli Studi di Milano, Milano, Italy.

Francesca Crosti (F)

UO Genetica Medica, IRCCS San Gerardo, Monza, Italy.

Lidia Pezzani (L)

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milano, Italy.
UO Pediatria, ASST Papa Giovanni XXIII, Bergamo, Italy.

Classifications MeSH