Characteristics and long-term outcome in a large series of chronic myelomonocytic leukaemia patients including 104 formerly referred to as oligomonocytic.

CMML chronic myelomonocytic leukaemia oligomonocytic

Journal

British journal of haematology
ISSN: 1365-2141
Titre abrégé: Br J Haematol
Pays: England
ID NLM: 0372544

Informations de publication

Date de publication:
27 Nov 2023
Historique:
revised: 24 10 2023
received: 10 08 2023
accepted: 10 11 2023
medline: 28 11 2023
pubmed: 28 11 2023
entrez: 28 11 2023
Statut: aheadofprint

Résumé

Recently modified diagnostic criteria for chronic myelomonocytic leukaemia (CMML) have lowered the cut-off for absolute monocytosis. In the largest series to date, we have analysed 313 CMML patients, including 104 with oligomonocytic (OM)-CMML. Five-year survival was longer for OM-CMML than for other patients (p < 0.001). Multivariate analysis identified OM-CMML as a favourable prognostic factor (HR 0.58; p = 0.002). The 5-year cumulative incidence of progression to classical CMML was 47%. Older age and transfusion dependence were adverse prognostic factors for OM-CMML. Our results support the inclusion of OM-CMML in the CMML category as a subtype with superior outcomes.

Identifiants

pubmed: 38013238
doi: 10.1111/bjh.19217
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Contractes Clínic de Recerca Emili Letang-Josep Font 2021, granted by Hospital Clínic de Barcelona
Organisme : Convocatòria d'Intensificació Interna per als professionals de l'HCB 2023
Organisme : Fundació la Marató TV3 sobre Càncer
ID : 201 201930-31
Organisme : Instituto de Salud Carlos III (ISCIII), co-funded by the European Union
ID : FIS PI19/01476
Organisme : Instituto de Salud Carlos III (ISCIII), co-funded by the European Union
ID : FIS PI22/01660

Informations de copyright

© 2023 British Society for Haematology and John Wiley & Sons Ltd.

Références

Arber DA, Orazi A, Hasserjian RP, Borowitz MJ, Calvo KR, Kvasnicka HM, et al. International consensus classification of myeloid neoplasms and acute leukemia: integrating morphological, clinical, and genomic data. Blood. 2022;140:1200-1228.
Khoury JD, Solary E, Abla O, Akkari Y, Alaggio R, Apperley JF, et al. The 5th edition of the World Health Organization classification of haematolymphoid tumours: myeloid and histiocytic/dendritic neoplasms. Leukemia. 2022;36(7):1703-1719.
Geyer JT, Tam W, Liu YC, Chen Z, Wang SA, Bueso-Ramos C, et al. Oligomonocytic chronic myelomonocytic leukemia (chronic myelomonocytic leukemia without absolute monocytosis) displays a similar clinicopathologic and mutational profile to classical chronic myelomonocytic leukemia. Mod Pathol. 2017;30(9):1213-1222.
Schuler E, Frank F, Hildebrandt B, Betz B, Strupp C, Rudelius M, et al. Myelodysplastic syndromes without peripheral monocytosis but with evidence of marrow monocytosis share clinical and molecular characteristics with CMML. Leuk Res. 2018;65:1-4.
Valent P, Orazi A, Savona MR, Patnaik MM, Onida F, van de Loosdrecht AA, et al. Proposed diagnostic criteria for classical chronic myelomonocytic leukemia (CMML), CMML variants and pre-CMML conditions. Haematologica. 2019;104(10):1935-1949.
Calvo X, Garcia-Gisbert N, Parraga I, Gibert J, Florensa L, Andrade-Campos M, et al. Oligomonocytic and overt chronic myelomonocytic leukemia show similar clinical, genomic, and immunophenotypic features. Blood Adv. 2020;4(20):5285-5296.
Valent P. Oligo-monocytic CMML and other pre-CMML states: clinical impact, prognostication and management. Best Pract Res Clin Haematol. 2020;33(2):101137.
Calvo X, Roman-Bravo D, Garcia-Gisbert N, Rodriguez-Sevilla JJ, Garcia-Avila S, Florensa L, et al. Outcomes and molecular profile of oligomonocytic CMML support its consideration as the first stage in the CMML continuum. Blood Adv. 2022;6(13):3921-3931.
Montalban-Bravo G, Kanagal-Shamanna R, Guerra V, Ramos-Perez J, Hammond D, Shilpa P, et al. Clinical outcomes and influence of mutation clonal dominance in oligomonocytic and classical chronic myelomonocytic leukemia. Am J Hematol. 2021;96(2):E50-E53.
Swerdlow SH, Campo E, Harris NL, Jaffe ES, Pileri SA, Stein H, et al. WHO classification of tumors of haematopoietic and lymphoid tissues. International Agency for Research on Cancer. Revised 4th. ed. Lyon, France: International Agency for Research on Cancer (IARC); 2017. p. 82-86.
Castaño-Díez S, López-Guerra M, Bosch-Castañeda C, Bataller A, Charry P, Esteban D, et al. Real-world data on chronic myelomonocytic leukemia: clinical and molecular characteristics, treatment, emerging drugs, and patient outcomes. Cancer. 2022;14(17):4107.
Carr RM, Vorobyev D, Lasho T, Marks DL, Tolosa EJ, Vedder A, et al. RAS mutations drive proliferative chronic myelomonocytic leukemia via a KMT2A-PLK1 axis. Nat Commun. 2021;12(1):2901.
Patel BJ, Przychodzen B, Thota S, Radivoyevitch T, Visconte V, Kuzmanovic T, et al. Genomic determinants of chronic myelomonocytic leukemia. Leukemia. 2017;31(12):2815-2823.

Auteurs

Sandra Castaño-Díez (S)

Hematology Department, Hospital Clínic Barcelona, Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.

Helena Pomares (H)

Hematology Department, Institut Català d'Oncologia (ICO), Hospital Duran i Reynals, Hospitalet de Llobregat, Institut d'Investigació Biomèdica de Bellvitge (IDIBELL), Universitat de Barcelona, Barcelona, Spain.

Daniel Esteban (D)

Hematology Department, Hospital Clínic Barcelona, Barcelona, Spain.

Francesca Guijarro (F)

Institut d'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Hematopathology Section, Servei d'Anatomia Patològica, CDB, Hospital Clínic Barcelona, Barcelona, Spain.

Carlos Jiménez-Vicente (C)

Hematology Department, Hospital Clínic Barcelona, Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.

Inés Zugasti (I)

Hematology Department, Hospital Clínic Barcelona, Barcelona, Spain.

José Ramón Álamo (JR)

Hematopathology Section, Servei d'Anatomia Patològica, CDB, Hospital Clínic Barcelona, Barcelona, Spain.

Víctor Torrecillas Mayayo (VT)

Universitat de Barcelona, Barcelona, Spain.

Mònica López-Guerra (M)

Institut d'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Hematopathology Section, Servei d'Anatomia Patològica, CDB, Hospital Clínic Barcelona, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Cáncer (CIBERONC), Madrid, Spain.

Cristina de la Fuente (C)

Hematology Department, Institut Català d'Oncologia (ICO), Hospital Germans Trias i Pujol, Badalona, Universitat Autònoma de Barcelona, Barcelona, Spain.

Paola Charry (P)

Apheresis Department, Hospital Clínic Barcelona, Barcelona, Spain.

Albert Cortés-Bullich (A)

Hematology Department, Hospital Clínic Barcelona, Barcelona, Spain.

Álex Bataller (Á)

Hematology Department, Hospital Clínic Barcelona, Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Josep Carreras Leukaemia Research Institute, Badalona, Spain.

Clara Maluquer (C)

Hematology Department, Institut Català d'Oncologia (ICO), Hospital Duran i Reynals, Hospitalet de Llobregat, Institut d'Investigació Biomèdica de Bellvitge (IDIBELL), Universitat de Barcelona, Barcelona, Spain.

Dolors Colomer (D)

Institut d'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Hematopathology Section, Servei d'Anatomia Patològica, CDB, Hospital Clínic Barcelona, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Cáncer (CIBERONC), Madrid, Spain.

María Rozman (M)

Institut d'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Hematopathology Section, Servei d'Anatomia Patològica, CDB, Hospital Clínic Barcelona, Barcelona, Spain.

Montserrat Arnan (M)

Hematology Department, Institut Català d'Oncologia (ICO), Hospital Duran i Reynals, Hospitalet de Llobregat, Institut d'Investigació Biomèdica de Bellvitge (IDIBELL), Universitat de Barcelona, Barcelona, Spain.

Blanca Xicoy (B)

Hematology Department, Institut Català d'Oncologia (ICO), Hospital Germans Trias i Pujol, Badalona, Universitat Autònoma de Barcelona, Barcelona, Spain.
Josep Carreras Leukaemia Research Institute, Badalona, Spain.

Jordi Esteve (J)

Hematology Department, Hospital Clínic Barcelona, Barcelona, Spain.
Universitat de Barcelona, Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Josep Carreras Leukaemia Research Institute, Badalona, Spain.

Marina Díaz-Beyá (M)

Hematology Department, Hospital Clínic Barcelona, Barcelona, Spain.
Institut d'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Barcelona, Spain.
Josep Carreras Leukaemia Research Institute, Badalona, Spain.

Classifications MeSH