Role of circulating biomarkers in spinal muscular atrophy: insights from a new treatment era.
SMA
circulating biomarkers
gene therapy
individualized medicine
innovative treatments
miRNA
neurofilaments
Journal
Frontiers in neurology
ISSN: 1664-2295
Titre abrégé: Front Neurol
Pays: Switzerland
ID NLM: 101546899
Informations de publication
Date de publication:
2023
2023
Historique:
received:
23
05
2023
accepted:
25
10
2023
medline:
29
11
2023
pubmed:
29
11
2023
entrez:
29
11
2023
Statut:
epublish
Résumé
Spinal muscular atrophy (SMA) is a lower motor neuron disease due to biallelic mutations in the
Identifiants
pubmed: 38020652
doi: 10.3389/fneur.2023.1226969
pmc: PMC10679720
doi:
Types de publication
Journal Article
Review
Langues
eng
Pagination
1226969Informations de copyright
Copyright © 2023 Giorgia, Gomez Garcia de la Banda and Smeriglio.
Déclaration de conflit d'intérêts
The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.
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