Genetic model of UBA5 deficiency highlights the involvement of both peripheral and central nervous systems and identifies widespread mitochondrial abnormalities.

UBA5 encephalopathy mitochondria ufmylation zebrafish

Journal

Brain communications
ISSN: 2632-1297
Titre abrégé: Brain Commun
Pays: England
ID NLM: 101755125

Informations de publication

Date de publication:
2023
Historique:
received: 07 12 2022
revised: 10 10 2023
accepted: 19 11 2023
medline: 4 12 2023
pubmed: 4 12 2023
entrez: 4 12 2023
Statut: epublish

Résumé

Variants in

Identifiants

pubmed: 38046095
doi: 10.1093/braincomms/fcad317
pii: fcad317
pmc: PMC10691876
doi:

Types de publication

Journal Article

Langues

eng

Pagination

fcad317

Informations de copyright

© The Author(s) 2023. Published by Oxford University Press on behalf of the Guarantors of Brain.

Déclaration de conflit d'intérêts

The authors report no competing interests.

Références

Acta Neuropathol. 2015 Sep;130(3):389-406
pubmed: 25931053
EMBO J. 2004 May 5;23(9):1977-86
pubmed: 15071506
Transl Psychiatry. 2020 Nov 6;10(1):385
pubmed: 33159045
PLoS One. 2011 Jan 14;6(1):e16156
pubmed: 21264253
Neuropediatrics. 2021 Dec;52(6):489-494
pubmed: 33853163
Acta Neuropathol Commun. 2020 Nov 9;8(1):189
pubmed: 33168089
Clin Genet. 2018 May;93(5):1057-1062
pubmed: 29286531
Hum Mutat. 2018 Jul;39(7):934-938
pubmed: 29663568
Nucleic Acids Res. 2014 Jul;42(Web Server issue):W401-7
pubmed: 24861617
J Cell Biochem. 2008 Aug 15;104(6):2324-34
pubmed: 18442052
J Med Genet. 2018 Dec;55(12):803-813
pubmed: 30287594
J Mol Biol. 2019 Feb 1;431(3):463-478
pubmed: 30412706
Expert Opin Drug Discov. 2009 Jul 1;4(7):715-726
pubmed: 19774094
Nat Commun. 2011 Feb 08;2:181
pubmed: 21304510
PLoS One. 2016 Feb 12;11(2):e0149039
pubmed: 26872069
Methods. 2018 Nov 1;150:49-62
pubmed: 29936090
Mol Microbiol. 2012 Oct;86(1):187-98
pubmed: 22897198
J Med Genet. 2020 Dec;57(12):835-842
pubmed: 32179706
Am J Hum Genet. 2016 Sep 1;99(3):695-703
pubmed: 27545681
BMC Med Genet. 2017 Oct 2;18(1):103
pubmed: 28965491
Am J Hum Genet. 2016 Sep 1;99(3):683-694
pubmed: 27545674
PLoS One. 2013 Aug 09;8(8):e70172
pubmed: 23950910
Eur J Med Genet. 2019 Feb;62(2):97-102
pubmed: 29902590
J Vis Exp. 2016 Oct 31;(116):
pubmed: 27842370
Hum Mol Genet. 2012 Sep 15;21(18):4073-83
pubmed: 22706277
J Neurosci. 2019 Oct 16;39(42):8200-8208
pubmed: 31619488
Epileptic Disord. 2018 Aug 1;20(4):313-318
pubmed: 30078785
Cold Spring Harb Mol Case Stud. 2021 Jun 11;7(3):
pubmed: 33811063
Brain. 2018 Jul 1;141(7):1934-1945
pubmed: 29868776
Exp Cell Res. 2014 Jun 10;324(2):192-9
pubmed: 24726913
Dev Biol. 2000 Nov 15;227(2):279-93
pubmed: 11071755
Neurology. 2017 Oct 24;89(17):1821-1828
pubmed: 28931644

Auteurs

Rita J Serrano (RJ)

School of Biological Sciences, Monash University, Melbourne 3800, Australia.

Viola Oorschot (V)

Monash Ramaciotti Centre for Cryo-Electron Microscopy, Monash University, Melbourne 3800, Australia.

Dashika Palipana (D)

School of Biological Sciences, Monash University, Melbourne 3800, Australia.

Vanessa Calcinotto (V)

School of Biological Sciences, Monash University, Melbourne 3800, Australia.

Carmen Sonntag (C)

School of Biological Sciences, Monash University, Melbourne 3800, Australia.

Georg Ramm (G)

Monash Ramaciotti Centre for Cryo-Electron Microscopy, Monash University, Melbourne 3800, Australia.
Department of Biochemistry and Molecular Biology, Biomedicine Discovery Institute, Monash University, Melbourne 3800, Australia.

Robert J Bryson-Richardson (RJ)

School of Biological Sciences, Monash University, Melbourne 3800, Australia.

Classifications MeSH