Array CGH Autism Exome sequencing Intellectual disability Microcephaly TRAPPC9

Journal

Molecular syndromology
ISSN: 1661-8769
Titre abrégé: Mol Syndromol
Pays: Switzerland
ID NLM: 101525192

Informations de publication

Date de publication:
Dec 2023
Historique:
received: 18 03 2023
accepted: 05 06 2023
pmc-release: 01 06 2024
medline: 7 12 2023
pubmed: 7 12 2023
entrez: 7 12 2023
Statut: ppublish

Résumé

Hereditary forms of intellectual disability (ID), an estimated prevalence ranging between 1% and 3% in the general population, are among the most important problems in health care. Especially, autosomal-recessive ID has a very heterogeneous molecular basis and a lack of specific phenotypic features. Here, we report on two unrelated patients with autosomal-recessive ID, microcephaly, and autistic features and review the patients with TRAPPC9-related ID. Whole-exome sequencing and array CGH were performed for molecular diagnosis of the patients. The first case has a microdeletion on chromosome 8q24.23-q24.3 region which is 1.7 Mb in length and includes the last 5 exons of Our study showed that the most consistent clinical findings for TRAPPC9-related ID are ID, microcephaly, and some structural brain MRI abnormalities. The mutations in the

Identifiants

pubmed: 38058760
doi: 10.1159/000531439
pii: 531439
pmc: PMC10697769
doi:

Types de publication

Journal Article

Langues

eng

Pagination

485-492

Informations de copyright

© 2023 S. Karger AG, Basel.

Déclaration de conflit d'intérêts

The authors declare that there are no potential conflicts of interest with respect to the authorship and/or publication of this manuscript.

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Auteurs

Eyyup Uctepe (E)

Acibadem Ankara Tissue Typing Laboratory, Ankara, Turkey.

Ahmet Yesilyurt (A)

Acibadem Labgen Genetic Diagnosis Center, Istanbul, Turkey.
Acibadem Maslak Hospital, Istanbul, Turkey.

Fatma Nisa Esen (FN)

Acibadem Labgen Genetic Diagnosis Center, Istanbul, Turkey.

Sait Tumer (S)

Acibadem Labgen Genetic Diagnosis Center, Istanbul, Turkey.

Hanifenur Mancilar (H)

Acibadem Labgen Genetic Diagnosis Center, Istanbul, Turkey.

Fatma Mujgan Sonmez (FM)

Karadeniz Technical University Faculty of Medicine, Department of Child Neurology, Ankara, Turkey.
Private office, Child Neurology, Ankara, Turkey.

Classifications MeSH