Rare within Rare: A Girl with Severe Haemophilia A and Turner Syndrome.

Isochromosome Xq Turner syndrome severe haemophilia A in female

Journal

Journal of clinical medicine
ISSN: 2077-0383
Titre abrégé: J Clin Med
Pays: Switzerland
ID NLM: 101606588

Informations de publication

Date de publication:
30 Nov 2023
Historique:
received: 30 10 2023
revised: 25 11 2023
accepted: 27 11 2023
medline: 9 12 2023
pubmed: 9 12 2023
entrez: 9 12 2023
Statut: epublish

Résumé

A coincidental occurrence of severe haemophilia A and Turner syndrome in a female person is extremely rare (less than 10 cases published). In such challenging cases, a multidisciplinary approach based on medicine of precision with full access to genetic and bio-molecular exploration is indispensable. The article presents an eight-year-old girl, with a family history of haemophilia, without significant disease signs (only post-dental extraction bleeding and a shorter stature). Discordantly, however, the investigations revealed a challenging condition: a genotype of 46,X,i(Xq), with an Isochromosome Xq responsible for the Turner syndrome and simultaneously, for the detrimental transformation, interfering with X chromosome inactivation, of an obligate hemophilia carrier into a severe hemophilia case-two distinct and provocative diseases.

Identifiants

pubmed: 38068488
pii: jcm12237437
doi: 10.3390/jcm12237437
pmc: PMC10707082
pii:
doi:

Types de publication

Journal Article

Langues

eng

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Auteurs

Cristina Blag (C)

Pediatric Discipline, Department of Mother and Child, Iuliu Hațieganu University of Medicine and Pharmacy, 400177 Cluj-Napoca, Romania.

Margit Serban (M)

Onco-Hematology Research Unit, Romanian Academy of Medical Sciences, Children Emergency Hospital "Louis Turcanu" Timisoara, European Hemophilia Treatment Centre, 300011 Timisoara, Romania.

Cristina Emilia Ursu (CE)

Onco-Hematology Research Unit, Romanian Academy of Medical Sciences, Children Emergency Hospital "Louis Turcanu" Timisoara, European Hemophilia Treatment Centre, 300011 Timisoara, Romania.

Cristina Popa (C)

Onco-Hematology Research Unit, Romanian Academy of Medical Sciences, Children Emergency Hospital "Louis Turcanu" Timisoara, European Hemophilia Treatment Centre, 300011 Timisoara, Romania.
Discipline of Genetics, "Victor Babes" University of Medicine and Pharmacy Timisoara, 300041 Timisoara, Romania.

Adina Traila (A)

Medical Centre for Evaluation Therapy, Medical Education and Rehabilitation of Children and Young Adults, European Hemophilia Treatment Centre, 305100 Buzias, Romania.

Cristian Jinca (C)

Department of Pediatrics, Division of Onco-Hematology, "Victor Babes" University of Medicine and Pharmacy Timisoara, 300041 Timisoara, Romania.

Ciprian Tomuleasa (C)

Department of Hematology, Research Center for Functional Genomics and Translational Medicine, Iuliu Hatieganu University of Medicine and Pharmacy, 400012 Cluj Napoca, Romania.

Madalina Bota (M)

Pediatric Discipline, Department of Mother and Child, Iuliu Hațieganu University of Medicine and Pharmacy, 400177 Cluj-Napoca, Romania.

Ioana Ionita (I)

Department of Hematology, "Victor Babes" University of Medicine and Pharmacy Timisoara, 300041 Timisoara, Romania.

Teodora Smaranda Arghirescu (TS)

Department of Pediatrics, Division of Onco-Hematology, "Victor Babes" University of Medicine and Pharmacy Timisoara, 300041 Timisoara, Romania.

Classifications MeSH