Evaluation of Optical Genome Mapping in Clinical Genetic Testing of Facioscapulohumeral Muscular Dystrophy.

FSHD1 FSHD2 OGM facioscapulohumeral muscular dystrophy optical genome mapping

Journal

Genes
ISSN: 2073-4425
Titre abrégé: Genes (Basel)
Pays: Switzerland
ID NLM: 101551097

Informations de publication

Date de publication:
30 Nov 2023
Historique:
received: 18 10 2023
revised: 24 11 2023
accepted: 27 11 2023
medline: 23 12 2023
pubmed: 23 12 2023
entrez: 23 12 2023
Statut: epublish

Résumé

Facioscapulohumeral muscular dystrophy (FSHD) is the third most common hereditary muscular dystrophy, caused by the contraction of the D4Z4 repeats on the permissive 4qA haplotype on chromosome 4, resulting in the faulty expression of the

Identifiants

pubmed: 38136988
pii: genes14122166
doi: 10.3390/genes14122166
pii:
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Slovenian Research Agency
ID : P3-0326
Organisme : University Medical Centre Ljubljana (UMCL)
ID : 20210031

Auteurs

Anja Kovanda (A)

Clinical Institute of Genomic Medicine, University Medical Center, 1000 Ljubljana, Slovenia.
Faculty of Medicine, University of Ljubljana, 1000 Ljubljana, Slovenia.

Luca Lovrečić (L)

Clinical Institute of Genomic Medicine, University Medical Center, 1000 Ljubljana, Slovenia.
Faculty of Medicine, University of Ljubljana, 1000 Ljubljana, Slovenia.

Gorazd Rudolf (G)

Clinical Institute of Genomic Medicine, University Medical Center, 1000 Ljubljana, Slovenia.
Faculty of Medicine, University of Ljubljana, 1000 Ljubljana, Slovenia.

Ivana Babic Bozovic (I)

Clinical Institute of Genomic Medicine, University Medical Center, 1000 Ljubljana, Slovenia.

Helena Jaklič (H)

Clinical Institute of Genomic Medicine, University Medical Center, 1000 Ljubljana, Slovenia.

Lea Leonardis (L)

Faculty of Medicine, University of Ljubljana, 1000 Ljubljana, Slovenia.
Institute of Clinical Neurophysiology, University Medical Center Ljubljana, 1000 Ljubljana, Slovenia.

Borut Peterlin (B)

Clinical Institute of Genomic Medicine, University Medical Center, 1000 Ljubljana, Slovenia.
Faculty of Medicine, University of Ljubljana, 1000 Ljubljana, Slovenia.

Classifications MeSH