Prospective study to characterize adalimumab exposure in pediatric patients with rheumatic diseases.

Drug exposure Heterogeneity Pharmacodynamics Pharmacokinetics Target concentration Therapeutic drug monitoring bDMARDs

Journal

Pediatric rheumatology online journal
ISSN: 1546-0096
Titre abrégé: Pediatr Rheumatol Online J
Pays: England
ID NLM: 101248897

Informations de publication

Date de publication:
02 Jan 2024
Historique:
received: 30 08 2023
accepted: 15 11 2023
medline: 4 1 2024
pubmed: 4 1 2024
entrez: 3 1 2024
Statut: epublish

Résumé

In pediatric rheumatic diseases (PRD), adalimumab is dosed using fixed weight-based bands irrespective of methotrexate co-treatment, disease activity (DA) or other factors that might influence adalimumab pharmacokinetics (PK). In rheumatoid arthritis (RA) adalimumab exposure between 2-8 mg/L is associated with clinical response. PRD data on adalimumab is scarce. Therefore, this study aimed to analyze adalimumab PK and its variability in PRD treated with/without methotrexate. A two-center prospective study in PRD patients aged 2-18 years treated with adalimumab and methotrexate (G Twenty-eight patients (14 per group), diagnosed with juvenile idiopathic arthritis (71.4%), non-infectious uveitis (25%) or chronic recurrent multifocal osteomyelitis (3.6%) completed the study. G This study revealed a high heterogeneity in adalimumab exposure in PRD. Adalimumab exposure tended to be higher with methotrexate co-treatment compared to adalimumab monotherapy although differences were not statistically significant. Most children showed adalimumab exposure exceeding those reported for RA with clinical response, particularly with methotrexate co-treatment. This highlights the need of further investigations to establish model-based personalized treatment strategies in PRD to avoid under- and overexposure. NCT04042792 , registered 02.08.2019.

Sections du résumé

BACKGROUND BACKGROUND
In pediatric rheumatic diseases (PRD), adalimumab is dosed using fixed weight-based bands irrespective of methotrexate co-treatment, disease activity (DA) or other factors that might influence adalimumab pharmacokinetics (PK). In rheumatoid arthritis (RA) adalimumab exposure between 2-8 mg/L is associated with clinical response. PRD data on adalimumab is scarce. Therefore, this study aimed to analyze adalimumab PK and its variability in PRD treated with/without methotrexate.
METHODS METHODS
A two-center prospective study in PRD patients aged 2-18 years treated with adalimumab and methotrexate (G
RESULTS RESULTS
Twenty-eight patients (14 per group), diagnosed with juvenile idiopathic arthritis (71.4%), non-infectious uveitis (25%) or chronic recurrent multifocal osteomyelitis (3.6%) completed the study. G
CONCLUSION CONCLUSIONS
This study revealed a high heterogeneity in adalimumab exposure in PRD. Adalimumab exposure tended to be higher with methotrexate co-treatment compared to adalimumab monotherapy although differences were not statistically significant. Most children showed adalimumab exposure exceeding those reported for RA with clinical response, particularly with methotrexate co-treatment. This highlights the need of further investigations to establish model-based personalized treatment strategies in PRD to avoid under- and overexposure.
TRIAL REGISTRATION BACKGROUND
NCT04042792 , registered 02.08.2019.

Identifiants

pubmed: 38167019
doi: 10.1186/s12969-023-00930-8
pii: 10.1186/s12969-023-00930-8
doi:

Banques de données

ClinicalTrials.gov
['NCT04042792']

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

5

Informations de copyright

© 2023. The Author(s).

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Auteurs

Tatjana Welzel (T)

Pediatric Pharmacology and Pharmacometrics, University Children's Hospital Basel, University of Basel, Basel, Switzerland. tatjana.welzel@ukbb.ch.
Division of Pediatric Rheumatology, Department of Pediatrics and Autoinflammation Reference Centre Tuebingen (arcT), University Hospital Tuebingen, Tuebingen, Germany. tatjana.welzel@ukbb.ch.
Pediatric Rheumatology, University Children's Hospital Basel, University of Basel, Basel, Switzerland. tatjana.welzel@ukbb.ch.
Pediatric Research Center, University Children's Hospital Basel, University of Basel, Basel, Switzerland. tatjana.welzel@ukbb.ch.

Klervi Golhen (K)

Pediatric Pharmacology and Pharmacometrics, University Children's Hospital Basel, University of Basel, Basel, Switzerland.

Andrew Atkinson (A)

Pediatric Pharmacology and Pharmacometrics, University Children's Hospital Basel, University of Basel, Basel, Switzerland.
Pediatric Research Center, University Children's Hospital Basel, University of Basel, Basel, Switzerland.
Division of Infectious Diseases, Washington University School of Medicine in St. Louis, St. Louis, MO, USA.

Verena Gotta (V)

Pediatric Pharmacology and Pharmacometrics, University Children's Hospital Basel, University of Basel, Basel, Switzerland.

David Ternant (D)

Pediatric Pharmacology and Pharmacometrics, University Children's Hospital Basel, University of Basel, Basel, Switzerland.
Université de Tours, service de pharmacologie médicale, Tours France, Université de Tours, EA 4245 T2I, Tours, France.

Jasmin B Kuemmerle-Deschner (JB)

Division of Pediatric Rheumatology, Department of Pediatrics and Autoinflammation Reference Centre Tuebingen (arcT), University Hospital Tuebingen, Tuebingen, Germany.

Christine Michler (C)

Division of Pediatric Rheumatology, Department of Pediatrics and Autoinflammation Reference Centre Tuebingen (arcT), University Hospital Tuebingen, Tuebingen, Germany.

Gilbert Koch (G)

Pediatric Pharmacology and Pharmacometrics, University Children's Hospital Basel, University of Basel, Basel, Switzerland.

Johannes N van den Anker (JN)

Pediatric Pharmacology and Pharmacometrics, University Children's Hospital Basel, University of Basel, Basel, Switzerland.

Marc Pfister (M)

Pediatric Pharmacology and Pharmacometrics, University Children's Hospital Basel, University of Basel, Basel, Switzerland.

Andreas Woerner (A)

Pediatric Rheumatology, University Children's Hospital Basel, University of Basel, Basel, Switzerland.

Classifications MeSH