Novel presentation of AADC deficiency as a mild phenotype with exercise-induced dystonic crises: A case report.

AADC Aromatic l-amino acid decarboxylase deficiency Case report Exome sequencing Neurometabolic disorder

Journal

Heliyon
ISSN: 2405-8440
Titre abrégé: Heliyon
Pays: England
ID NLM: 101672560

Informations de publication

Date de publication:
15 Jan 2024
Historique:
received: 18 08 2023
revised: 20 10 2023
accepted: 12 12 2023
medline: 9 1 2024
pubmed: 9 1 2024
entrez: 9 1 2024
Statut: epublish

Résumé

Aromatic l-amino acid decarboxylase (AADC) deficiency is a rare autosomal recessive neurometabolic disorder caused by biallelic pathogenic variants in the

Identifiants

pubmed: 38192810
doi: 10.1016/j.heliyon.2023.e23746
pii: S2405-8440(23)10954-6
pmc: PMC10772193
doi:

Types de publication

Case Reports

Langues

eng

Pagination

e23746

Informations de copyright

© 2023 The Authors. Published by Elsevier Ltd.

Déclaration de conflit d'intérêts

The authors declare that they have no known competing financial interests or personal relationships that could have appeared to influence the work reported in this paper.

Auteurs

Liene Thys (L)

Department of Paediatric Neurology, Antwerp University Hospital, Edegem, Belgium.

Marije Meuwissen (M)

Department of Medical Genetics, Antwerp University Hospital/University of Antwerp, Edegem, Wilrijk, Belgium.

Katrien Janssens (K)

Department of Medical Genetics, Antwerp University Hospital/University of Antwerp, Edegem, Wilrijk, Belgium.

Diane Beysen (D)

Department of Paediatric Neurology, Antwerp University Hospital, Edegem, Belgium.

Classifications MeSH