The Efficacy of Tradipitant in Patients with Diabetic and Idiopathic Gastroparesis in Phase III Randomized Placebo-Controlled Clinical Trial.

GCSI NK-1 RCT diabetes gastroparesis nausea vomiting

Journal

Clinical gastroenterology and hepatology : the official clinical practice journal of the American Gastroenterological Association
ISSN: 1542-7714
Titre abrégé: Clin Gastroenterol Hepatol
Pays: United States
ID NLM: 101160775

Informations de publication

Date de publication:
16 Jan 2024
Historique:
received: 29 09 2023
revised: 13 12 2023
accepted: 02 01 2024
medline: 19 1 2024
pubmed: 19 1 2024
entrez: 18 1 2024
Statut: aheadofprint

Résumé

Neurokinin receptor 1 (NK1R) antagonists are effective in reducing nausea and vomiting in chemo-therapy induced emesis. We investigated the safety and efficacy of tradipitant, an NK1R antagonist, in patients with idiopathic and diabetic gastroparesis. 201 adults with gastroparesis were randomly assigned to oral tradipitant 85 mg (n = 102) or placebo (n = 99) twice daily for 12 weeks. Symptoms were assessed by a daily symptom dairy, Gastroparesis Cardinal Symptom Index scores, and other patient-reported questionnaires. Blood levels were monitored for an exposure-response analysis. The primary outcome was change from baseline to week 12 in average nausea severity, measured by daily symptom diary. The ITT population did not meet the pre-specified primary endpoint at Week 12 (difference in nausea severity change drug vs. placebo, P = .741) or pre-specified secondary endpoints. Post hoc analyses were performed to control for drug exposure, rescue medications, and baseline severity inflation. Subjects with high blood levels of tradipitant significantly improved average nausea severity beginning at early time points Weeks 2 through Week 4. In post hoc sensitivity analyses, tradipitant treatment demonstrated strengthened effects, with statistically significant improvements in nausea at Week 12. Although tradipitant did not reach significance in the ITT population, a pharmacokinetic exposure-response analysis demonstrated significant effects with adequate tradipitant exposure. When accounting for confounding factors such as baseline severity inflation and rescue medication, a statistically significant effect was also observed. These findings suggest that tradipitant has potential as a treatment for the symptom of nausea in gastroparesis. [ClincialTrials.gov number, NCT04028492].

Sections du résumé

BACKGROUND BACKGROUND
Neurokinin receptor 1 (NK1R) antagonists are effective in reducing nausea and vomiting in chemo-therapy induced emesis. We investigated the safety and efficacy of tradipitant, an NK1R antagonist, in patients with idiopathic and diabetic gastroparesis.
METHODS METHODS
201 adults with gastroparesis were randomly assigned to oral tradipitant 85 mg (n = 102) or placebo (n = 99) twice daily for 12 weeks. Symptoms were assessed by a daily symptom dairy, Gastroparesis Cardinal Symptom Index scores, and other patient-reported questionnaires. Blood levels were monitored for an exposure-response analysis. The primary outcome was change from baseline to week 12 in average nausea severity, measured by daily symptom diary.
RESULTS RESULTS
The ITT population did not meet the pre-specified primary endpoint at Week 12 (difference in nausea severity change drug vs. placebo, P = .741) or pre-specified secondary endpoints. Post hoc analyses were performed to control for drug exposure, rescue medications, and baseline severity inflation. Subjects with high blood levels of tradipitant significantly improved average nausea severity beginning at early time points Weeks 2 through Week 4. In post hoc sensitivity analyses, tradipitant treatment demonstrated strengthened effects, with statistically significant improvements in nausea at Week 12.
CONCLUSIONS CONCLUSIONS
Although tradipitant did not reach significance in the ITT population, a pharmacokinetic exposure-response analysis demonstrated significant effects with adequate tradipitant exposure. When accounting for confounding factors such as baseline severity inflation and rescue medication, a statistically significant effect was also observed. These findings suggest that tradipitant has potential as a treatment for the symptom of nausea in gastroparesis. [ClincialTrials.gov number, NCT04028492].

Identifiants

pubmed: 38237696
pii: S1542-3565(24)00050-8
doi: 10.1016/j.cgh.2024.01.005
pii:
doi:

Banques de données

ClinicalTrials.gov
['NCT04028492']

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

Copyright © 2024 AGA Institute. Published by Elsevier Inc. All rights reserved.

Auteurs

Jesse L Carlin (JL)

Vanda Pharmaceuticals, Inc., Washington, DC. Electronic address: Jesse.Carlin@vandapharma.com.

Christos Polymeropoulos (C)

Vanda Pharmaceuticals, Inc., Washington, DC.

Michael Camilleri (M)

Division of Gastroenterology and Hepatology, Department of Internal Medicine, Mayo Clinic, Rochester, MN, USA.

Anthony Lembo (A)

Digestive Disease Institute, Cleveland Clinic Cleveland, Ohio, USA.

Michaela Fisher (M)

Vanda Pharmaceuticals, Inc., Washington, DC.

Caleigh Kupersmith (C)

Vanda Pharmaceuticals, Inc., Washington, DC.

Darby Madonick (D)

Vanda Pharmaceuticals, Inc., Washington, DC.

Paula Moszczynski (P)

Vanda Pharmaceuticals, Inc., Washington, DC.

Sandra Smieszek (S)

Vanda Pharmaceuticals, Inc., Washington, DC.

Changfu Xiao (C)

Vanda Pharmaceuticals, Inc., Washington, DC.

Gunther Birznieks (G)

Vanda Pharmaceuticals, Inc., Washington, DC.

Mihael H Polymeropoulos (MH)

Vanda Pharmaceuticals, Inc., Washington, DC.

Classifications MeSH