First Case of a Dominant De Novo

Cranio-lenticulo-sutural dysplasia SEC23A genotype–phenotype correlation literature overview neurological manifestations

Journal

Genes
ISSN: 2073-4425
Titre abrégé: Genes (Basel)
Pays: Switzerland
ID NLM: 101551097

Informations de publication

Date de publication:
20 Jan 2024
Historique:
received: 22 12 2023
revised: 15 01 2024
accepted: 19 01 2024
medline: 26 1 2024
pubmed: 26 1 2024
entrez: 26 1 2024
Statut: epublish

Résumé

Cranio-lenticulo-sutural dysplasia (CLSD, OMIM #607812) is a rare genetic condition characterized by late-closing fontanels, skeletal defects, dysmorphisms, and congenital cataracts that are caused by bi-allelic or monoallelic variants in the

Identifiants

pubmed: 38275611
pii: genes15010130
doi: 10.3390/genes15010130
pii:
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Auteurs

Elia Marco Paolo Minale (EMP)

U.O.C. Genetica Medica, A.O.U. Federico II, 80131 Naples, Italy.
Department of Molecular Medicine and Medical Biotechnology, University Federico II, 80131 Naples, Italy.

Alessandro De Falco (A)

U.O.C. Genetica Medica, A.O.U. Federico II, 80131 Naples, Italy.
Department of Molecular Medicine and Medical Biotechnology, University Federico II, 80131 Naples, Italy.

Emanuele Agolini (E)

Laboratory of Medical Genetics, Ospedale Pediatrico Bambino Gesù, IRCCS, 00165 Rome, Italy.

Antonio Novelli (A)

Laboratory of Medical Genetics, Ospedale Pediatrico Bambino Gesù, IRCCS, 00165 Rome, Italy.

Roberta Russo (R)

Department of Molecular Medicine and Medical Biotechnology, University Federico II, 80131 Naples, Italy.
CEINGE Biotecnologie Avanzate, 80145 Naples, Italy.

Immacolata Andolfo (I)

Department of Molecular Medicine and Medical Biotechnology, University Federico II, 80131 Naples, Italy.
CEINGE Biotecnologie Avanzate, 80145 Naples, Italy.

Achille Iolascon (A)

U.O.C. Genetica Medica, A.O.U. Federico II, 80131 Naples, Italy.
Department of Molecular Medicine and Medical Biotechnology, University Federico II, 80131 Naples, Italy.
CEINGE Biotecnologie Avanzate, 80145 Naples, Italy.

Carmelo Piscopo (C)

Medical and Laboratory Genetic Unit, Antonio Cardarelli Hospital, 80131 Naples, Italy.

Classifications MeSH