TBCRC 039: a phase II study of preoperative ruxolitinib with or without paclitaxel for triple-negative inflammatory breast cancer.

Inflammatory breast cancer Neoadjuvant Paclitaxel Ruxolitinib Triple negative

Journal

Breast cancer research : BCR
ISSN: 1465-542X
Titre abrégé: Breast Cancer Res
Pays: England
ID NLM: 100927353

Informations de publication

Date de publication:
31 Jan 2024
Historique:
received: 14 09 2023
accepted: 18 01 2024
medline: 1 2 2024
pubmed: 1 2 2024
entrez: 31 1 2024
Statut: epublish

Résumé

Patients with inflammatory breast cancer (IBC) have overall poor clinical outcomes, with triple-negative IBC (TN-IBC) being associated with the worst survival, warranting the investigation of novel therapies. Preclinical studies implied that ruxolitinib (RUX), a JAK1/2 inhibitor, may be an effective therapy for TN-IBC. We conducted a randomized phase II study with nested window-of-opportunity in TN-IBC. Treatment-naïve patients received a 7-day run-in of RUX alone or RUX plus paclitaxel (PAC). After the run-in, those who received RUX alone proceeded to neoadjuvant therapy with either RUX + PAC or PAC alone for 12 weeks; those who had received RUX + PAC continued treatment for 12 weeks. All patients subsequently received 4 cycles of doxorubicin plus cyclophosphamide prior to surgery. Research tumor biopsies were performed at baseline (pre-run-in) and after run-in therapy. Tumors were evaluated for phosphorylated STAT3 (pSTAT3) by immunostaining, and a subset was also analyzed by RNA-seq. The primary endpoint was the percent of pSTAT3-positive pre-run-in tumors that became pSTAT3-negative. Secondary endpoints included pathologic complete response (pCR). Overall, 23 patients were enrolled, of whom 21 completed preoperative therapy. Two patients achieved pCR (8.7%). pSTAT3 and IL-6/JAK/STAT3 signaling decreased in post-run-in biopsies of RUX-treated samples, while sustained treatment with RUX + PAC upregulated IL-6/JAK/STAT3 signaling compared to RUX alone. Both treatments decreased GZMB In summary, the use of RUX in TN-IBC was associated with a decrease in pSTAT3 levels despite lack of clinical benefit. Cancer cell-specific-targeting of JAK2/STAT3 or combinations with immunotherapy may be required for further evaluation of JAK2/STAT3 signaling as a cancer therapeutic target. www. gov , NCT02876302. Registered 23 August 2016.

Sections du résumé

BACKGROUND BACKGROUND
Patients with inflammatory breast cancer (IBC) have overall poor clinical outcomes, with triple-negative IBC (TN-IBC) being associated with the worst survival, warranting the investigation of novel therapies. Preclinical studies implied that ruxolitinib (RUX), a JAK1/2 inhibitor, may be an effective therapy for TN-IBC.
METHODS METHODS
We conducted a randomized phase II study with nested window-of-opportunity in TN-IBC. Treatment-naïve patients received a 7-day run-in of RUX alone or RUX plus paclitaxel (PAC). After the run-in, those who received RUX alone proceeded to neoadjuvant therapy with either RUX + PAC or PAC alone for 12 weeks; those who had received RUX + PAC continued treatment for 12 weeks. All patients subsequently received 4 cycles of doxorubicin plus cyclophosphamide prior to surgery. Research tumor biopsies were performed at baseline (pre-run-in) and after run-in therapy. Tumors were evaluated for phosphorylated STAT3 (pSTAT3) by immunostaining, and a subset was also analyzed by RNA-seq. The primary endpoint was the percent of pSTAT3-positive pre-run-in tumors that became pSTAT3-negative. Secondary endpoints included pathologic complete response (pCR).
RESULTS RESULTS
Overall, 23 patients were enrolled, of whom 21 completed preoperative therapy. Two patients achieved pCR (8.7%). pSTAT3 and IL-6/JAK/STAT3 signaling decreased in post-run-in biopsies of RUX-treated samples, while sustained treatment with RUX + PAC upregulated IL-6/JAK/STAT3 signaling compared to RUX alone. Both treatments decreased GZMB
CONCLUSION CONCLUSIONS
In summary, the use of RUX in TN-IBC was associated with a decrease in pSTAT3 levels despite lack of clinical benefit. Cancer cell-specific-targeting of JAK2/STAT3 or combinations with immunotherapy may be required for further evaluation of JAK2/STAT3 signaling as a cancer therapeutic target.
TRIAL REGISTRATION BACKGROUND
www.
CLINICALTRIALS RESULTS
gov , NCT02876302. Registered 23 August 2016.

Identifiants

pubmed: 38297352
doi: 10.1186/s13058-024-01774-0
pii: 10.1186/s13058-024-01774-0
doi:

Banques de données

ClinicalTrials.gov
['NCT02876302']

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

20

Subventions

Organisme : National Cancer Institute, United States
ID : T32CA236754
Organisme : National Cancer Institute, United States
ID : CA197623

Informations de copyright

© 2024. The Author(s).

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Auteurs

Filipa Lynce (F)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA. Filipa_Lynce@dfci.harvard.edu.
Harvard Medical School, Boston, MA, USA. Filipa_Lynce@dfci.harvard.edu.
Brigham and Women's Hospital, Boston, MA, USA. Filipa_Lynce@dfci.harvard.edu.

Laura E Stevens (LE)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Zheqi Li (Z)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Jane E Brock (JE)

Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Anushree Gulvady (A)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Ying Huang (Y)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Faina Nakhlis (F)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Ashka Patel (A)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Jeremy M Force (JM)

Duke University, Durham, NC, USA.

Tufia C Haddad (TC)

Mayo Clinic, Rochester, MN, USA.

Naoto Ueno (N)

MD Anderson Cancer Center, Houston, TX, USA.

Vered Stearns (V)

Johns Hopkins University, Baltimore, MA, USA.

Antonio C Wolff (AC)

Johns Hopkins University, Baltimore, MA, USA.

Amy S Clark (AS)

University of Pennsylvania, Philadelphia, PA, USA.

Jennifer R Bellon (JR)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Edward T Richardson (ET)

Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Justin M Balko (JM)

Vanderbilt University Medical Center, Nashville, TN, USA.

Ian E Krop (IE)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.
Yale Cancer Center, New Haven, CT, USA.

Eric P Winer (EP)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.
Yale Cancer Center, New Haven, CT, USA.

Paulina Lange (P)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.

E Shelley Hwang (ES)

Duke University, Durham, NC, USA.

Tari A King (TA)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Sara M Tolaney (SM)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Alastair Thompson (A)

Baylor College of Medicine, Houston, TX, USA.

Gaorav P Gupta (GP)

University of North Carolina, Chapel Hill, NC, USA.

Elizabeth A Mittendorf (EA)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Meredith M Regan (MM)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.

Beth Overmoyer (B)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA.
Harvard Medical School, Boston, MA, USA.
Brigham and Women's Hospital, Boston, MA, USA.

Kornelia Polyak (K)

Dana-Farber Cancer Institute, 450 Brookline Ave., Boston, MA, 02215, USA. kornelia_polyak@dfci.harvard.edu.
Harvard Medical School, Boston, MA, USA. kornelia_polyak@dfci.harvard.edu.
Brigham and Women's Hospital, Boston, MA, USA. kornelia_polyak@dfci.harvard.edu.

Classifications MeSH