AAV9-MEDIATED GENE THERAPY OF CHOLINE ACETYLTRANSFERASE DEFICIENT MICE.


Journal

Human gene therapy
ISSN: 1557-7422
Titre abrégé: Hum Gene Ther
Pays: United States
ID NLM: 9008950

Informations de publication

Date de publication:
01 Feb 2024
Historique:
medline: 1 2 2024
pubmed: 1 2 2024
entrez: 1 2 2024
Statut: aheadofprint

Résumé

The enzyme choline acetyltransferase (ChAT) synthesizes acetylcholine from acetyl-CoA and choline at the neuromuscular junction and at the nerve terminals of cholinergic neurons. Mutations in the ChAT gene (

Identifiants

pubmed: 38299967
doi: 10.1089/hum.2023.173
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Auteurs

Cameron V Lin (CV)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States; cvlin@ucdavis.edu.

Clementine A D Thomas (CAD)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States; cadthomas@ucdavis.edu.

Thanh L Huynh (TL)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States; tlhuynh@ucdavis.edu.

David T Wei (DT)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States; dtwei@ucdavis.edu.

Jaime N Young (JN)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States; jnyyoung@ucdavis.edu.

Anahid S Aivazian (AS)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States; asaivazian@ucdavis.edu.

Abigail McInnes (A)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States; amcinnes@ucdavis.edu.

Jixiang Xu (J)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States; jxxxu@ucdavis.edu.

Sarah E Cook (SE)

University of California Davis School of Veterinary Medicine, 70733, Anatomic Pathology, Davis, California, United States; sestevens@ucdavis.edu.

Jessica Vazquez (J)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States; jesvazquez@ucdavis.edu.

Ricardo A Maselli (RA)

University of California Davis School of Medicine, 12218, Neurology , Davis, California, United States.
2210 Rockwell Dr, 2210 Rockwell Dr, Davis, California, United States; ramaselli@ucdavis.edu.

Classifications MeSH