Compromised transcription-mRNA export factor THOC2 causes R-loop accumulation, DNA damage and adverse neurodevelopment.


Journal

Nature communications
ISSN: 2041-1723
Titre abrégé: Nat Commun
Pays: England
ID NLM: 101528555

Informations de publication

Date de publication:
08 Feb 2024
Historique:
received: 16 06 2023
accepted: 15 01 2024
medline: 9 2 2024
pubmed: 9 2 2024
entrez: 8 2 2024
Statut: epublish

Résumé

We implicated the X-chromosome THOC2 gene, which encodes the largest subunit of the highly-conserved TREX (Transcription-Export) complex, in a clinically complex neurodevelopmental disorder with intellectual disability as the core phenotype. To study the molecular pathology of this essential eukaryotic gene, we generated a mouse model based on a hypomorphic Thoc2 exon 37-38 deletion variant of a patient with ID, speech delay, hypotonia, and microcephaly. The Thoc2 exon 37-38 deletion male (Thoc2

Identifiants

pubmed: 38331934
doi: 10.1038/s41467-024-45121-5
pii: 10.1038/s41467-024-45121-5
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1210

Subventions

Organisme : Department of Health | National Health and Medical Research Council (NHMRC)
ID : APP1155224
Organisme : Department of Health | National Health and Medical Research Council (NHMRC)
ID : APP1163240

Informations de copyright

© 2024. The Author(s).

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Auteurs

Rudrarup Bhattacharjee (R)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.

Lachlan A Jolly (LA)

Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.
School of Biomedicine, The University of Adelaide, Adelaide, SA, 5005, Australia.

Mark A Corbett (MA)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.

Ing Chee Wee (IC)

Discipline of Anatomy and Pathology, School of Biomedicine, The University of Adelaide, Adelaide, SA, 5005, Australia.

Sushma R Rao (SR)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Proteomics, Metabolomics and MS-imaging Core Facility, South Australian Health and Medical Research Institute, and Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.

Alison E Gardner (AE)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.

Tarin Ritchie (T)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.

Eline J H van Hugte (EJH)

Department of Human Genetics, Radboudumc, Donders Institute for Brain, Cognition, and Behavior, Nijmegen, 6500, HB, the Netherlands.

Ummi Ciptasari (U)

Department of Human Genetics, Radboudumc, Donders Institute for Brain, Cognition, and Behavior, Nijmegen, 6500, HB, the Netherlands.

Sandra Piltz (S)

Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.
School of Biomedicine, The University of Adelaide, Adelaide, SA, 5005, Australia.
South Australian Health and Medical Research Institute, Adelaide, SA, 5000, Australia.

Jacqueline E Noll (JE)

School of Biomedicine, Faculty of Health and Medical Sciences, University of Adelaide and Precision Cancer Medicine Theme, Solid Tumour Program, South Australian Health and Medical Research Institute, Adelaide, SA, 5000, Australia.

Nazzmer Nazri (N)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Childhood Dementia Research Group, College of Medicine and Public Health, Flinders Health & Medical Research Institute, Flinders University, Bedford Park, Adelaide, SA, 5042, Australia.

Clare L van Eyk (CL)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.

Melissa White (M)

Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.
School of Biomedicine, The University of Adelaide, Adelaide, SA, 5005, Australia.
South Australian Health and Medical Research Institute, Adelaide, SA, 5000, Australia.

Dani Fornarino (D)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.

Cathryn Poulton (C)

Undiagnosed Diseases Program, Genetic Services of WA, King Edward Memorial Hospital, Subiaco, WA, 6008, Australia.

Gareth Baynam (G)

Undiagnosed Diseases Program, Genetic Services of WA, King Edward Memorial Hospital, Subiaco, WA, 6008, Australia.
Western Australian Register of Developmental Anomalies, King Edward Memorial Hospital, Subiaco, WA, 6008, Australia.
Rare Care Centre, Perth Children's Hospital, Nedlands, WA, 6009, Australia.

Lyndsey E Collins-Praino (LE)

Discipline of Anatomy and Pathology, School of Biomedicine, The University of Adelaide, Adelaide, SA, 5005, Australia.

Marten F Snel (MF)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Proteomics, Metabolomics and MS-imaging Core Facility, South Australian Health and Medical Research Institute, and Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.

Nael Nadif Kasri (N)

Department of Human Genetics, Radboudumc, Donders Institute for Brain, Cognition, and Behavior, Nijmegen, 6500, HB, the Netherlands.

Kim M Hemsley (KM)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Childhood Dementia Research Group, College of Medicine and Public Health, Flinders Health & Medical Research Institute, Flinders University, Bedford Park, Adelaide, SA, 5042, Australia.

Paul Q Thomas (PQ)

Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.
School of Biomedicine, The University of Adelaide, Adelaide, SA, 5005, Australia.
South Australian Health and Medical Research Institute, Adelaide, SA, 5000, Australia.

Raman Kumar (R)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia.
Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia.

Jozef Gecz (J)

Adelaide Medical School, The University of Adelaide, Adelaide, SA, 5005, Australia. jozef.gecz@adelaide.edu.au.
Robinson Research Institute, The University of Adelaide, Adelaide, SA, 5005, Australia. jozef.gecz@adelaide.edu.au.

Classifications MeSH