Identification of a novel

RPGR gene X-linked inheritance mutation primary ciliary dyskinesia retinitis pigmentosa

Journal

Frontiers in pediatrics
ISSN: 2296-2360
Titre abrégé: Front Pediatr
Pays: Switzerland
ID NLM: 101615492

Informations de publication

Date de publication:
2024
Historique:
received: 16 11 2023
accepted: 10 01 2024
medline: 9 2 2024
pubmed: 9 2 2024
entrez: 9 2 2024
Statut: epublish

Résumé

The mutations in the Two young brothers from a non-consanguineous Slovak family with diagnosed retinal dystrophy and recurrent respiratory infections were examined. Suspected PCD was diagnosed based on a PICADAR questionnaire, nasal nitric oxide analysis, transmission electron microscopy, high-speed video microscopy analysis, and genetic testing. We identified a novel frameshift The identified novel pathogenic mutation in the

Sections du résumé

Background UNASSIGNED
The mutations in the
Methods UNASSIGNED
Two young brothers from a non-consanguineous Slovak family with diagnosed retinal dystrophy and recurrent respiratory infections were examined. Suspected PCD was diagnosed based on a PICADAR questionnaire, nasal nitric oxide analysis, transmission electron microscopy, high-speed video microscopy analysis, and genetic testing.
Results UNASSIGNED
We identified a novel frameshift
Conclusion UNASSIGNED
The identified novel pathogenic mutation in the

Identifiants

pubmed: 38333087
doi: 10.3389/fped.2024.1339664
pmc: PMC10850321
doi:

Types de publication

Case Reports

Langues

eng

Pagination

1339664

Informations de copyright

© 2024 Kolkova, Durdik, Holubekova, Durdikova, Jesenak and Banovcin.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

Auteurs

Zuzana Kolkova (Z)

Biomedical Center Martin, Jessenius Faculty of Medicine in Martin, Comenius University in Bratislava, Martin, Slovakia.

Peter Durdik (P)

Department of Pediatrics, Jessenius Faculty of Medicine in Martin, Comenius University in Bratislava, Martin, Slovakia.
Department of Pediatrics, University Hospital Martin, Martin, Slovakia.

Veronika Holubekova (V)

Biomedical Center Martin, Jessenius Faculty of Medicine in Martin, Comenius University in Bratislava, Martin, Slovakia.

Anna Durdikova (A)

Department of Pediatrics, Jessenius Faculty of Medicine in Martin, Comenius University in Bratislava, Martin, Slovakia.
Department of Pediatrics, University Hospital Martin, Martin, Slovakia.

Milos Jesenak (M)

Department of Pediatrics, Jessenius Faculty of Medicine in Martin, Comenius University in Bratislava, Martin, Slovakia.
Department of Pediatrics, University Hospital Martin, Martin, Slovakia.
Department of Pulmonology and Phthisiology, Jessenius Faculty of Medicine in Martin, Comenius University in Bratislava, University Hospital in Martin, Martin, Slovakia.
Department of Clinical Immunology and Allergology, University Hospital in Martin, Martin, Slovakia.

Peter Banovcin (P)

Department of Pediatrics, Jessenius Faculty of Medicine in Martin, Comenius University in Bratislava, Martin, Slovakia.
Department of Pediatrics, University Hospital Martin, Martin, Slovakia.

Classifications MeSH