Consensus guideline for the diagnosis and management of pituitary adenomas in childhood and adolescence: Part 2, specific diseases.


Journal

Nature reviews. Endocrinology
ISSN: 1759-5037
Titre abrégé: Nat Rev Endocrinol
Pays: England
ID NLM: 101500078

Informations de publication

Date de publication:
09 Feb 2024
Historique:
accepted: 19 12 2023
medline: 10 2 2024
pubmed: 10 2 2024
entrez: 9 2 2024
Statut: aheadofprint

Résumé

Pituitary adenomas are rare in children and young people under the age of 19 (hereafter referred to as CYP) but they pose some different diagnostic and management challenges in this age group than in adults. These rare neoplasms can disrupt maturational, visual, intellectual and developmental processes and, in CYP, they tend to have more occult presentation, aggressive behaviour and are more likely to have a genetic basis than in adults. Through standardized AGREE II methodology, literature review and Delphi consensus, a multidisciplinary expert group developed 74 pragmatic management recommendations aimed at optimizing care for CYP in the first-ever comprehensive consensus guideline to cover the care of CYP with pituitary adenoma. Part 2 of this consensus guideline details 57 recommendations for paediatric patients with prolactinomas, Cushing disease, growth hormone excess causing gigantism and acromegaly, clinically non-functioning adenomas, and the rare TSHomas. Compared with adult patients with pituitary adenomas, we highlight that, in the CYP group, there is a greater proportion of functioning tumours, including macroprolactinomas, greater likelihood of underlying genetic disease, more corticotrophinomas in boys aged under 10 years than in girls and difficulty of peri-pubertal diagnosis of growth hormone excess. Collaboration with pituitary specialists caring for adult patients, as part of commissioned and centralized multidisciplinary teams, is key for optimizing management, transition and lifelong care and facilitates the collection of health-related quality of survival outcomes of novel medical, surgical and radiotherapeutic treatments, which are currently largely missing.

Identifiants

pubmed: 38336898
doi: 10.1038/s41574-023-00949-7
pii: 10.1038/s41574-023-00949-7
doi:

Types de publication

Journal Article Review

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024. Springer Nature Limited.

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Auteurs

Márta Korbonits (M)

Centre for Endocrinology, William Harvey Research Institute, Barts and the London School of Medicine and Dentistry, Queen Mary University of London, London, UK. m.korbonits@qmul.ac.uk.

Joanne C Blair (JC)

Alder Hey Children's Hospital, Liverpool, UK.

Anna Boguslawska (A)

Department of Endocrinology, Jagiellonian University Medical College, Krakow, Poland.

John Ayuk (J)

University Hospitals Birmingham NHS Foundation Trust, Birmingham, UK.

Justin H Davies (JH)

University Hospital Southampton NHS Foundation Trust, Southampton, UK.

Maralyn R Druce (MR)

Centre for Endocrinology, William Harvey Research Institute, Barts and the London School of Medicine and Dentistry, Queen Mary University of London, London, UK.

Jane Evanson (J)

Neuroradiology, Barts Health NHS Trust, London, UK.

Daniel Flanagan (D)

Plymouth Hospitals NHS Trust, Plymouth, UK.

Nigel Glynn (N)

Centre for Endocrinology, William Harvey Research Institute, Barts and the London School of Medicine and Dentistry, Queen Mary University of London, London, UK.

Claire E Higham (CE)

The Christie NHS Foundation Trust, Manchester, UK.

Thomas S Jacques (TS)

Great Ormond Street Institute of Child Health, University College London, London, UK.
Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.

Saurabh Sinha (S)

Sheffield Children's and Sheffield Teaching Hospitals NHS Foundation Trust, Sheffield, UK.

Ian Simmons (I)

The Leeds Teaching Hospitals NHS Trust, Leeds, UK.

Nicky Thorp (N)

The Christie NHS Foundation Trust, Manchester, UK.

Francesca M Swords (FM)

Norwich and Norfolk NHS Foundation Trust, Norwich, UK.

Helen L Storr (HL)

Centre for Endocrinology, William Harvey Research Institute, Barts and the London School of Medicine and Dentistry, Queen Mary University of London, London, UK.

Helen A Spoudeas (HA)

Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.
University College London Hospitals NHS Foundation Trust, London, UK.

Classifications MeSH