Knockout and Replacement Gene Surgery to Treat Rhodopsin-Mediated Autosomal Dominant Retinitis Pigmentosa.
adeno-associated viral vectors
autosomal dominant retinitis pigmentosa
gene editing
gene therapy
rhodopsin
Journal
Human gene therapy
ISSN: 1557-7422
Titre abrégé: Hum Gene Ther
Pays: United States
ID NLM: 9008950
Informations de publication
Date de publication:
Mar 2024
Mar 2024
Historique:
pubmed:
18
2
2024
medline:
18
2
2024
entrez:
18
2
2024
Statut:
ppublish
Résumé
Mutations in the rhodopsin (
Identifiants
pubmed: 38368562
doi: 10.1089/hum.2023.201
doi:
Types de publication
Journal Article
Langues
eng
Sous-ensembles de citation
IM