Mild limb girdle muscular dystrophy R9 phenotype caused by novel compound heterozygous FKRP gene mutation.

Dystroglycanopathy FKRP LGMDR9 limb girdle muscular dystrophy α-Dystroglycan

Journal

Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology
ISSN: 2532-1900
Titre abrégé: Acta Myol
Pays: Italy
ID NLM: 9811169

Informations de publication

Date de publication:
2023
Historique:
received: 14 11 2023
accepted: 19 12 2023
medline: 26 2 2024
pubmed: 26 2 2024
entrez: 26 2 2024
Statut: epublish

Résumé

Fukutin-related protein (FKRP) mutations cause a broad spectrum of muscular dystrophies, from a relatively mild limb-girdle muscular dystrophy type 9 (LGMDR9) to severe congenital muscular dystrophy (CMD). This study aims to report two siblings belonging to a non-consanguineous Tunisian family harboring a novel compound heterozygous

Identifiants

pubmed: 38406381
doi: 10.36185/2532-1900-391
pmc: PMC10883327
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

106-112

Informations de copyright

©2023 Gaetano Conte Academy - Mediterranean Society of Myology, Naples, Italy.

Déclaration de conflit d'intérêts

The authors declare that they have no conflicts of interest.

Auteurs

Ikhlass Belhassen (I)

Laboratory of Neurogenetics, Parkinson Disease and Cerebrovascular Diseases (LR-12-SP-19), Habib Bourguiba University Hospital, University of Sfax, Tunisia.
Clinical Investigation Center, Habib Bourguiba University Hospital, Sfax, Tunisia.

Rita Menassa (R)

Service de Biochimie et Biologie Moléculaire, Centre de Biologie et Pathologie Est, Hospices Civils de Lyon, France.

Salma Sakka (S)

Laboratory of Neurogenetics, Parkinson Disease and Cerebrovascular Diseases (LR-12-SP-19), Habib Bourguiba University Hospital, University of Sfax, Tunisia.
Clinical Investigation Center, Habib Bourguiba University Hospital, Sfax, Tunisia.

Laurence Michel-Calemard (L)

Service de Biochimie et Biologie Moléculaire, Centre de Biologie et Pathologie Est, Hospices Civils de Lyon, France.

Nathalie Streichenberger (N)

Centre de Pathologie et Neuropathologie Est, Hospices Civils de Lyon; Université Claude Bernard Lyon1, Lyon, France.

Dorra Ben Ayed (DB)

Laboratory of Neurogenetics, Parkinson Disease and Cerebrovascular Diseases (LR-12-SP-19), Habib Bourguiba University Hospital, University of Sfax, Tunisia.
Clinical Investigation Center, Habib Bourguiba University Hospital, Sfax, Tunisia.

Nadia Bouattour (N)

Laboratory of Neurogenetics, Parkinson Disease and Cerebrovascular Diseases (LR-12-SP-19), Habib Bourguiba University Hospital, University of Sfax, Tunisia.
Clinical Investigation Center, Habib Bourguiba University Hospital, Sfax, Tunisia.

Mariem Dammak (M)

Laboratory of Neurogenetics, Parkinson Disease and Cerebrovascular Diseases (LR-12-SP-19), Habib Bourguiba University Hospital, University of Sfax, Tunisia.
Clinical Investigation Center, Habib Bourguiba University Hospital, Sfax, Tunisia.

Chokri Mhiri (C)

Laboratory of Neurogenetics, Parkinson Disease and Cerebrovascular Diseases (LR-12-SP-19), Habib Bourguiba University Hospital, University of Sfax, Tunisia.
Clinical Investigation Center, Habib Bourguiba University Hospital, Sfax, Tunisia.

Classifications MeSH