TIM-3, LAG-3, or 2B4 gene disruptions increase the anti-tumor response of engineered T cells.

CRISPR/Cas9 TCR - T cell receptor adoptive T cell immunotherapy genome editing inhibitory receptor

Journal

Frontiers in immunology
ISSN: 1664-3224
Titre abrégé: Front Immunol
Pays: Switzerland
ID NLM: 101560960

Informations de publication

Date de publication:
2024
Historique:
received: 10 10 2023
accepted: 05 02 2024
medline: 21 3 2024
pubmed: 21 3 2024
entrez: 21 3 2024
Statut: epublish

Résumé

In adoptive T cell therapy, the long term therapeutic benefits in patients treated with engineered tumor specific T cells are limited by the lack of long term persistence of the infused cellular products and by the immunosuppressive mechanisms active in the tumor microenvironment. Exhausted T cells infiltrating the tumor are characterized by loss of effector functions triggered by multiple inhibitory receptors (IRs). In patients, IR blockade reverts T cell exhaustion but has low selectivity, potentially unleashing autoreactive clones and resulting in clinical autoimmune side effects. Furthermore, loss of long term protective immunity in cell therapy has been ascribed to the effector memory phenotype of the infused cells. We simultaneously redirected T cell specificity towards the NY-ESO-1 antigen via TCR gene editing (TCR We show that upon chronic stimulation, TCR These results highlight that TIM-3, LAG-3, and 2B4 disruptions increase the therapeutic benefit of tumor specific cellular products and suggest distinct, non-redundant roles for IRs in anti-tumor responses.

Sections du résumé

Background UNASSIGNED
In adoptive T cell therapy, the long term therapeutic benefits in patients treated with engineered tumor specific T cells are limited by the lack of long term persistence of the infused cellular products and by the immunosuppressive mechanisms active in the tumor microenvironment. Exhausted T cells infiltrating the tumor are characterized by loss of effector functions triggered by multiple inhibitory receptors (IRs). In patients, IR blockade reverts T cell exhaustion but has low selectivity, potentially unleashing autoreactive clones and resulting in clinical autoimmune side effects. Furthermore, loss of long term protective immunity in cell therapy has been ascribed to the effector memory phenotype of the infused cells.
Methods UNASSIGNED
We simultaneously redirected T cell specificity towards the NY-ESO-1 antigen via TCR gene editing (TCR
Results UNASSIGNED
We show that upon chronic stimulation, TCR
Conclusion UNASSIGNED
These results highlight that TIM-3, LAG-3, and 2B4 disruptions increase the therapeutic benefit of tumor specific cellular products and suggest distinct, non-redundant roles for IRs in anti-tumor responses.

Identifiants

pubmed: 38510235
doi: 10.3389/fimmu.2024.1315283
pmc: PMC10953820
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1315283

Informations de copyright

Copyright © 2024 Cianciotti, Magnani, Ugolini, Camisa, Merelli, Vavassori, Potenza, Imparato, Manfredi, Abbati, Perani, Spinelli, Shifrut, Ciceri, Vago, Di Micco, Naldini, Genovese, Ruggiero and Bonini.

Déclaration de conflit d'intérêts

CB, ER, ZM, BC, AP, LV, FC, PG, LN and BCC are inventors on different patents on cancer immunotherapy and genetic engineering. CB has been member of Advisory Board and Consultant for Molmed, Intellia, TxCell, Novartis, GSK, Allogene, Kite/Gilead, Miltenyi, Kiadis, Evir, Janssen and received research support from Molmed s.p.a and Intellia Therapeutics. LV received royalties and research support from GEN-DX and research support from Moderna Therapeutics. The remaining authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest. The author(s) declared that they were an editorial board member of Frontiers, at the time of submission. This had no impact on the peer review process and the final decision.

Auteurs

Beatrice Claudia Cianciotti (BC)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Zulma Irene Magnani (ZI)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Alessia Ugolini (A)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Barbara Camisa (B)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
Innovative Immunotherapies Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Ivan Merelli (I)

Institute for Biomedical Technologies, National Research Council, Segrate, Italy.

Valentina Vavassori (V)

Gene Transfer Technologies and New Gene Therapy Strategies Unit, San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Alessia Potenza (A)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Antonio Imparato (A)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Francesco Manfredi (F)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Danilo Abbati (D)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Laura Perani (L)

Experimental Imaging Centre, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Antonello Spinelli (A)

Experimental Imaging Centre, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Eric Shifrut (E)

The School of Neurobiology, Biochemistry and Biophysics, The George S. Wise Faculty of Life Sciences, Tel Aviv University, Tel Aviv, Israel.
Department of Pathology, Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel.
Dotan Center for Advanced Therapies, Tel Aviv Sourasky Medical Center, Tel Aviv, Israel.

Fabio Ciceri (F)

Hematology and Bone Marrow Transplantation Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
Università Vita-Salute San Raffaele, Milan, Italy.

Luca Vago (L)

Università Vita-Salute San Raffaele, Milan, Italy.
Unit of Immunogenetics, Leukemia Genomics and Immunobiology, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Raffaella Di Micco (R)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Luigi Naldini (L)

Gene Transfer Technologies and New Gene Therapy Strategies Unit, San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Università Vita-Salute San Raffaele, Milan, Italy.

Pietro Genovese (P)

Gene Transfer Technologies and New Gene Therapy Strategies Unit, San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Gene Therapy Program, Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Department of Pediatric Oncology, Harvard Medical School, Boston, MA, United States.

Eliana Ruggiero (E)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Chiara Bonini (C)

Experimental Hematology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
Università Vita-Salute San Raffaele, Milan, Italy.

Classifications MeSH