Validation of the predictive value of BDNF -87 methylation for antidepressant treatment success in severely depressed patients-a randomized rater-blinded trial.

BDNF Biomarker Major depressive disorder RCT

Journal

Trials
ISSN: 1745-6215
Titre abrégé: Trials
Pays: England
ID NLM: 101263253

Informations de publication

Date de publication:
09 Apr 2024
Historique:
received: 24 11 2023
accepted: 18 03 2024
medline: 10 4 2024
pubmed: 10 4 2024
entrez: 9 4 2024
Statut: epublish

Résumé

Brain-derived neurotrophic factor (BDNF) is essential for antidepressant treatment of major depressive disorder (MDD). Our repeated studies suggest that DNA methylation of a specific CpG site in the promoter region of exon IV of the BDNF gene (CpG -87) might be predictive of the efficacy of monoaminergic antidepressants such as selective serotonin reuptake inhibitors (SSRIs), serotonin-norepinephrine reuptake inhibitors (SNRIs), and others. This trial aims to evaluate whether knowing the biomarker is non-inferior to treatment-as-usual (TAU) regarding remission rates while exhibiting significantly fewer adverse events (AE). The BDNF trial is a prospective, randomized, rater-blinded diagnostic study conducted at five university hospitals in Germany. The study's main hypothesis is that {1} knowing the methylation status of CpG -87 is non-inferior to not knowing it with respect to the remission rate while it significantly reduces the AE rate in patients experiencing at least one AE. The baseline assessment will occur upon hospitalization and a follow-up assessment on day 49 (± 3). A telephone follow-up will be conducted on day 70 (± 3). A total of 256 patients will be recruited, and methylation will be evaluated in all participants. They will be randomly assigned to either the marker or the TAU group. In the marker group, the methylation results will be shared with both the patient and their treating physician. In the TAU group, neither the patients nor their treating physicians will receive the marker status. The primary endpoints include the rate of patients achieving remission on day 49 (± 3), defined as a score of ≤ 10 on the Hamilton Depression Rating Scale (HDRS-24), and the occurrence of AE. The trial protocol has received approval from the Institutional Review Boards at the five participating universities. This trial holds significance in generating valuable data on a predictive biomarker for antidepressant treatment in patients with MDD. The findings will be shared with study participants, disseminated through professional society meetings, and published in peer-reviewed journals. German Clinical Trial Register DRKS00032503. Registered on 17 August 2023.

Sections du résumé

BACKGROUND BACKGROUND
Brain-derived neurotrophic factor (BDNF) is essential for antidepressant treatment of major depressive disorder (MDD). Our repeated studies suggest that DNA methylation of a specific CpG site in the promoter region of exon IV of the BDNF gene (CpG -87) might be predictive of the efficacy of monoaminergic antidepressants such as selective serotonin reuptake inhibitors (SSRIs), serotonin-norepinephrine reuptake inhibitors (SNRIs), and others. This trial aims to evaluate whether knowing the biomarker is non-inferior to treatment-as-usual (TAU) regarding remission rates while exhibiting significantly fewer adverse events (AE).
METHODS METHODS
The BDNF trial is a prospective, randomized, rater-blinded diagnostic study conducted at five university hospitals in Germany. The study's main hypothesis is that {1} knowing the methylation status of CpG -87 is non-inferior to not knowing it with respect to the remission rate while it significantly reduces the AE rate in patients experiencing at least one AE. The baseline assessment will occur upon hospitalization and a follow-up assessment on day 49 (± 3). A telephone follow-up will be conducted on day 70 (± 3). A total of 256 patients will be recruited, and methylation will be evaluated in all participants. They will be randomly assigned to either the marker or the TAU group. In the marker group, the methylation results will be shared with both the patient and their treating physician. In the TAU group, neither the patients nor their treating physicians will receive the marker status. The primary endpoints include the rate of patients achieving remission on day 49 (± 3), defined as a score of ≤ 10 on the Hamilton Depression Rating Scale (HDRS-24), and the occurrence of AE.
ETHICS AND DISSEMINATION BACKGROUND
The trial protocol has received approval from the Institutional Review Boards at the five participating universities. This trial holds significance in generating valuable data on a predictive biomarker for antidepressant treatment in patients with MDD. The findings will be shared with study participants, disseminated through professional society meetings, and published in peer-reviewed journals.
TRIAL REGISTRATION BACKGROUND
German Clinical Trial Register DRKS00032503. Registered on 17 August 2023.

Identifiants

pubmed: 38594753
doi: 10.1186/s13063-024-08061-5
pii: 10.1186/s13063-024-08061-5
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

247

Subventions

Organisme : Bundesministerium für Bildung und Forschung
ID : 01EK2204A

Informations de copyright

© 2024. The Author(s).

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Auteurs

Hannah Benedictine Maier (HB)

Department of Psychiatry, Social Psychiatry, and Psychotherapy, Hannover Medical School, Carl-Neuberg-Str. 1, Hannover, 30625, Germany. Maier.Hannah@mh-hannover.de.

Alexandra Neyazi (A)

Department of Psychiatry, Social Psychiatry, and Psychotherapy, Hannover Medical School, Carl-Neuberg-Str. 1, Hannover, 30625, Germany.
Department of Psychiatry and Psychotherapy, Otto von Guericke University Magdeburg (OVGU), Magdeburg, Germany.

Gabriel L Bundies (GL)

Department of Psychiatry, Social Psychiatry, and Psychotherapy, Hannover Medical School, Carl-Neuberg-Str. 1, Hannover, 30625, Germany.

Fiona Meyer-Bockenkamp (F)

Department of Psychiatry, Social Psychiatry, and Psychotherapy, Hannover Medical School, Carl-Neuberg-Str. 1, Hannover, 30625, Germany.

Stefan Bleich (S)

Department of Psychiatry, Social Psychiatry, and Psychotherapy, Hannover Medical School, Carl-Neuberg-Str. 1, Hannover, 30625, Germany.

Hansi Pathak (H)

Department of Psychiatry, Social Psychiatry, and Psychotherapy, Hannover Medical School, Carl-Neuberg-Str. 1, Hannover, 30625, Germany.

Yvonne Ziert (Y)

Institute of Biostatistics, Hannover Medical School, Hannover, Germany.

Barbara Neuhaus (B)

Center for Clinial Trials (ZKS), Hannover Medical School, Hannover, Germany.

Franz-Josef Müller (FJ)

Department of Psychiatry and Psychotherapy, University Hospital Schleswig Holstein, Kiel, Germany.
Department of Genome Regulation, Max Planck Institute for Molecular Genetics, Berlin, Germany.

Iris Pollmann (I)

Department of Psychiatry and Psychotherapy, University Hospital Schleswig Holstein, Kiel, Germany.

Thomas Illig (T)

Hannover Unified Biobank, Hannover Medical School, Hannover, Germany.

Stefanie Mücke (S)

Hannover Unified Biobank, Hannover Medical School, Hannover, Germany.

Meike Müller (M)

Department of Biomarker Analysis and Development, Fraunhofer Institute for Toxicology and Experimental Medicine ITEM, Hannover, Germany.

Brinja Kira Möller (BK)

Department of Biomarker Analysis and Development, Fraunhofer Institute for Toxicology and Experimental Medicine ITEM, Hannover, Germany.

Steffen Oeltze-Jafra (S)

Peter L. Reichertz Institute for Medical Informatics, Hannover Medical School, Hannover, Germany.

Tim Kacprowski (T)

Division Data Science in Biomedicine, Peter L. Reichertz Institute of Technische Universität Braunschweig and Hannover Medical School, Braunschweig, Germany.
Braunschweig Integrated Centre for Systems Biology, Technische Universität Braunschweig, Braunschweig, Germany.

Jan Voges (J)

Institut Für Informationsverarbeitung, Leibniz University Hannover, Hannover, Germany.

Fabian Müntefering (F)

Institut Für Informationsverarbeitung, Leibniz University Hannover, Hannover, Germany.

Josef Scheiber (J)

BioVariance GmbH, Tirschenreuth, Germany.

Andreas Reif (A)

Department for Psychiatry, Psychosomatics and Psychotherapy, University Hospital Frankfurt - Goethe University, Frankfurt, Germany.
Fraunhofer Institute for Translational Medicine and Pharmacology ITMP, Theodor-Stern-Kai 7, Frankfurt Am Main, 60596, Germany.

Mareike Aichholzer (M)

Department for Psychiatry, Psychosomatics and Psychotherapy, University Hospital Frankfurt - Goethe University, Frankfurt, Germany.

Christine Reif-Leonhard (C)

Department for Psychiatry, Psychosomatics and Psychotherapy, University Hospital Frankfurt - Goethe University, Frankfurt, Germany.

Maren Schmidt-Kassow (M)

Department for Psychiatry, Psychosomatics and Psychotherapy, University Hospital Frankfurt - Goethe University, Frankfurt, Germany.

Ulrich Hegerl (U)

German Foundation for Depression and Suicide Prevention, Leipzig, Germany.
Senckenberg Distinguished Professorship, Department of Psychiatry, Psychosomatics, and Psychotherapy, Goethe Universität Frankfurt Am Main, Frankfurt, Germany.

Hanna Reich (H)

Department for Psychiatry, Psychosomatics and Psychotherapy, University Hospital Frankfurt - Goethe University, Frankfurt, Germany.
German Foundation for Depression and Suicide Prevention, Leipzig, Germany.

Stefan Unterecker (S)

Department of Psychiatry, Psychosomatics and Psychotherapy, University Hospital Würzburg (UKW), Würzburg, Germany.

Heike Weber (H)

Department of Psychiatry, Psychosomatics and Psychotherapy, University Hospital Würzburg (UKW), Würzburg, Germany.

Jürgen Deckert (J)

Department of Psychiatry, Psychosomatics and Psychotherapy, University Hospital Würzburg (UKW), Würzburg, Germany.

Nicole Bössel-Debbert (N)

Department of Psychiatry and Psychotherapy, University Medicine Greifswald, Greifswald, Germany.

Hans J Grabe (HJ)

Department of Psychiatry and Psychotherapy, University Medicine Greifswald, Greifswald, Germany.

Michael Lucht (M)

Department of Psychiatry and Psychotherapy, University Medicine Greifswald, Greifswald, Germany.

Helge Frieling (H)

Department of Psychiatry, Social Psychiatry, and Psychotherapy, Hannover Medical School, Carl-Neuberg-Str. 1, Hannover, 30625, Germany.

Classifications MeSH