Prasinezumab slows motor progression in rapidly progressing early-stage Parkinson's disease.


Journal

Nature medicine
ISSN: 1546-170X
Titre abrégé: Nat Med
Pays: United States
ID NLM: 9502015

Informations de publication

Date de publication:
Apr 2024
Historique:
received: 30 06 2023
accepted: 23 02 2024
pubmed: 16 4 2024
medline: 16 4 2024
entrez: 15 4 2024
Statut: ppublish

Résumé

Prasinezumab, a monoclonal antibody that binds aggregated α-synuclein, is being investigated as a potential disease-modifying therapy in early-stage Parkinson's disease. Although in the PASADENA phase 2 study, the primary endpoint (Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) sum of Parts I + II + III) was not met, prasinezumab-treated individuals exhibited slower progression of motor signs than placebo-treated participants (MDS-UPDRS Part III). We report here an exploratory analysis assessing whether prasinezumab showed greater benefits on motor signs progression in prespecified subgroups with faster motor progression. Prasinezumab's potential effects on disease progression were assessed in four prespecified and six exploratory subpopulations of PASADENA: use of monoamine oxidase B inhibitors at baseline (yes versus no); Hoehn and Yahr stage (2 versus 1); rapid eye movement sleep behavior disorder (yes versus no); data-driven subphenotypes (diffuse malignant versus nondiffuse malignant); age at baseline (≥60 years versus <60 years); sex (male versus female); disease duration (>12 months versus <12 months); age at diagnosis (≥60 years versus <60 years); motor subphenotypes (akinetic-rigid versus tremor-dominant); and motor subphenotypes (postural instability gait dysfunction versus tremor-dominant). In these subpopulations, the effect of prasinezumab on slowing motor signs progression (MDS-UPDRS Part III) was greater in the rapidly progressing subpopulations (for example, participants who were diffuse malignant or taking monoamine oxidase B inhibitors at baseline). This exploratory analysis suggests that, in a trial of 1-year duration, prasinezumab might reduce motor progression to a greater extent in individuals with more rapidly progressing Parkinson's disease. However, because this was a post hoc analysis, additional randomized clinical trials are needed to validate these findings.

Identifiants

pubmed: 38622249
doi: 10.1038/s41591-024-02886-y
pii: 10.1038/s41591-024-02886-y
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1096-1103

Informations de copyright

© 2024. The Author(s).

Références

Stefanis, L. α-Synuclein in Parkinson’s disease. Cold Spring Harb. Perspect. Med. 2, a009399 (2012).
doi: 10.1101/cshperspect.a009399 pubmed: 22355802 pmcid: 3281589
Schenk, D. B. et al. First-in-human assessment of PRX002, an anti-α-synuclein monoclonal antibody, in healthy volunteers. Mov. Disord. 32, 211–218 (2017).
doi: 10.1002/mds.26878 pubmed: 27886407
Jankovic, J. et al. Safety and tolerability of multiple ascending doses of PRX002/RG7935, an anti-α-synuclein monoclonal antibody, in patients with Parkinson disease: a randomized clinical trial. JAMA Neurol. 75, 1206–1214 (2018).
doi: 10.1001/jamaneurol.2018.1487 pubmed: 29913017 pmcid: 6233845
Pagano, G. et al. Trial of prasinezumab in early-stage Parkinson’s disease. N. Engl. J. Med. 387, 421–432 (2022).
doi: 10.1056/NEJMoa2202867 pubmed: 35921451
Goetz, C. G. et al. Movement Disorder Society-sponsored revision of the Unified Parkinson’s Disease Rating Scale (MDS-UPDRS): scale presentation and clinimetric testing results. Mov. Disord. 23, 2129–2170 (2008).
doi: 10.1002/mds.22340 pubmed: 19025984
Lang, A. E. et al. Trial of cinpanemab in early Parkinson’s disease. N. Engl. J. Med. 387, 408–420 (2022).
doi: 10.1056/NEJMoa2203395 pubmed: 35921450
Simuni, T. et al. Baseline prevalence and longitudinal evolution of non-motor symptoms in early Parkinson’s disease: the PPMI cohort. J. Neurol. Neurosurg. Psychiatry 89, 78–88 (2018).
doi: 10.1136/jnnp-2017-316213 pubmed: 28986467
Simuni, T. et al. Longitudinal change of clinical and biological measures in early Parkinson’s disease: Parkinson’s progression markers initiative cohort. Mov. Disord. 33, 771–782 (2018).
doi: 10.1002/mds.27361 pubmed: 29572948 pmcid: 6001458
Horváth, K. et al. Minimal clinically important difference on the Motor Examination part of MDS-UPDRS. Parkinsonism Relat. Disord. 21, 1421–1426 (2015).
doi: 10.1016/j.parkreldis.2015.10.006 pubmed: 26578041
Pagano, G. et al. A Phase II study to evaluate the safety and efficacy of prasinezumab in early Parkinson’s disease (PASADENA): rationale, design, and baseline data. Front. Neurol. 12, 705407 (2021).
doi: 10.3389/fneur.2021.705407 pubmed: 34659081 pmcid: 8518716
Mollenhauer, B. et al. Baseline predictors for progression 4 years after Parkinson’s disease diagnosis in the De Novo Parkinson Cohort (DeNoPa). Mov. Disord. 34, 67–77 (2019).
doi: 10.1002/mds.27492 pubmed: 30468694
Zolfaghari, S. et al. Self-report versus clinician examination in early Parkinson’s disease. Mov. Disord. 37, 585–597 (2022).
doi: 10.1002/mds.28884 pubmed: 34897818
Joza, S. et al. Progression of clinical markers in prodromal Parkinson’s disease and dementia with Lewy bodies: a multicentre study. Brain 146, 3258–3272 (2023).
doi: 10.1093/brain/awad072 pubmed: 36881989
Calabresi, P. et al. Alpha-synuclein in Parkinson’s disease and other synucleinopathies: from overt neurodegeneration back to early synaptic dysfunction. Cell Death Dis. 14, 176 (2023).
doi: 10.1038/s41419-023-05672-9 pubmed: 36859484 pmcid: 9977911
Cascella, R. et al. The release of toxic oligomers from α-synuclein fibrils induces dysfunction in neuronal cells. Nat. Commun. 12, 1814 (2021).
doi: 10.1038/s41467-021-21937-3 pubmed: 33753734 pmcid: 7985515

Auteurs

Gennaro Pagano (G)

Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center Basel, Basel, Switzerland. Gennaro.Pagano@Roche.com.
University of Exeter Medical School, London, UK. Gennaro.Pagano@Roche.com.

Kirsten I Taylor (KI)

Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center Basel, Basel, Switzerland.

Judith Anzures Cabrera (J)

Roche Products Ltd, Welwyn Garden City, UK.

Tanya Simuni (T)

Department of Neurology, Northwestern University Feinberg School of Medicine, Chicago, IL, USA.

Kenneth Marek (K)

Institute for Neurodegenerative Disorders, New Haven, CT, USA.

Ronald B Postuma (RB)

Department of Neurology, Montreal Neurological Institute, McGill University, Montreal, Quebec, Canada.

Nicola Pavese (N)

Clinical Ageing Research Unit, Newcastle University, Newcastle upon Tyne, UK.

Fabrizio Stocchi (F)

The Institute for Research and Medical Care (IRCCS) San Raffaele Pisana, University San Raffaele Roma, Rome, Italy.

Kathrin Brockmann (K)

Hertie Institute for Clinical Brain Research and German Center for Neurodegenerative Diseases (DZNE), University of Tübingen, Tübingen, Germany.

Hanno Svoboda (H)

Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center Basel, Basel, Switzerland.
Roche Diagnostics GmbH, Penzberg, Germany.

Dylan Trundell (D)

Roche Products Ltd, Welwyn Garden City, UK.

Annabelle Monnet (A)

F. Hoffmann-La Roche Ltd, Basel, Switzerland.

Rachelle Doody (R)

F. Hoffmann-La Roche Ltd, Basel, Switzerland.

Paulo Fontoura (P)

F. Hoffmann-La Roche Ltd, Basel, Switzerland.

Geoffrey A Kerchner (GA)

Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center Basel, Basel, Switzerland.

Patrik Brundin (P)

Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center Basel, Basel, Switzerland.

Tania Nikolcheva (T)

F. Hoffmann-La Roche Ltd, Basel, Switzerland.

Azad Bonni (A)

Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center Basel, Basel, Switzerland.

Classifications MeSH