Long-term health-related quality of life and mental health in patients with immune thrombotic thrombocytopenic purpura.

FACT-Cog Fatigue HADS HRQoL TTP

Journal

Annals of hematology
ISSN: 1432-0584
Titre abrégé: Ann Hematol
Pays: Germany
ID NLM: 9107334

Informations de publication

Date de publication:
27 Apr 2024
Historique:
received: 17 12 2023
accepted: 20 04 2024
medline: 27 4 2024
pubmed: 27 4 2024
entrez: 26 4 2024
Statut: aheadofprint

Résumé

Immune thrombotic thrombocytopenic purpura (iTTP) is a rare and potentially life-threatening disorder. Treatment advances have lowered morbidity rates, but past acute events can still cause long-term consequences, reducing health-related quality of life (HRQoL) and determining cognitive impairment, anxiety, and depression. We aimed to investigate these aspects and the role of caplacizumab and rituximab: 39 patients were evaluated using the Medical Outcomes Study 36-Item Short Form Health Survey (SF-36), the FACIT-Fatigue, the Hospital Anxiety and Depression Scale, and the Functional Assessment in Cancer Therapy-Cognitive Function questionnaires. The median age at study inclusion was 50 years (IQR 38-60), and the median follow-up from diagnosis was 97 months (IQR 14-182); 82% of patients were female, and 36% had one or more recurrences. Caplacizumab was administered in 16 patients (41%), as well as rituximab. ITTP patients reported lower physical and mental HRQoL scores than the general population. No differences in physical or mental domains were observed between patients treated or not with caplacizumab, while those who received rituximab reported lower scores in mental health. Neurological impairment at diagnosis correlated with worse fatigue. The majority of patients (72%) reported anxiety or depression (82%). ITTP had a significant impact on the long-term cognitive function, fatigue, depression, and anxiety levels of patients, with a negative effect on their HRQoL. Our findings underscore the need to pay special attention to patients' long-term physical and mental health, regardless of the medical treatments received.

Identifiants

pubmed: 38671298
doi: 10.1007/s00277-024-05771-3
pii: 10.1007/s00277-024-05771-3
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024. The Author(s).

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Auteurs

Olga Mulas (O)

SC Ematologia e CTMO, Ospedale Businco, ARNAS Brotzu, Cagliari, Italy.
Dipartimento di Scienze Mediche e Sanità Pubblica, Università di Cagliari, Cagliari, Italy.

Fabio Efficace (F)

Health Outcomes Research Unit, Italian Group for Adult Hematologic Diseases (GIMEMA) Data Center, Rome, 00161, Italy.

Alessandro Costa (A)

Dipartimento di Scienze Mediche e Sanità Pubblica, Università di Cagliari, Cagliari, Italy.

Thomas Baldi (T)

Health Outcomes Research Unit, Italian Group for Adult Hematologic Diseases (GIMEMA) Data Center, Rome, 00161, Italy.

Filippo Zerbini (F)

Dipartimento di Scienze Mediche e Sanità Pubblica, Università di Cagliari, Cagliari, Italy.

Daniela Mantovani (D)

SC Ematologia e CTMO, Ospedale Businco, ARNAS Brotzu, Cagliari, Italy.

Emanuela Morelli (E)

Dipartimento di Scienze Mediche e Sanità Pubblica, Università di Cagliari, Cagliari, Italy.

Daniela Perra (D)

Dipartimento di Scienze Mediche e Sanità Pubblica, Università di Cagliari, Cagliari, Italy.

Giorgio La Nasa (G)

SC Ematologia e CTMO, Ospedale Businco, ARNAS Brotzu, Cagliari, Italy.
Dipartimento di Scienze Mediche e Sanità Pubblica, Università di Cagliari, Cagliari, Italy.

Giovanni Caocci (G)

SC Ematologia e CTMO, Ospedale Businco, ARNAS Brotzu, Cagliari, Italy. giovanni.caocci@unica.it.
Dipartimento di Scienze Mediche e Sanità Pubblica, Università di Cagliari, Cagliari, Italy. giovanni.caocci@unica.it.

Classifications MeSH