FGF12 copy number variant associated with epileptic encephalopathy.

CNV FGF12 duplications epileptic encephalopathy

Journal

Clinical genetics
ISSN: 1399-0004
Titre abrégé: Clin Genet
Pays: Denmark
ID NLM: 0253664

Informations de publication

Date de publication:
08 May 2024
Historique:
revised: 23 04 2024
received: 02 04 2024
accepted: 25 04 2024
medline: 8 5 2024
pubmed: 8 5 2024
entrez: 8 5 2024
Statut: aheadofprint

Résumé

FGF12 related epilepsy presents with variable phenotypes. We report another patient with a duplication involving the FGF12 gene who presented similar to other published cases having normal early development and responded to phenytoin.

Identifiants

pubmed: 38715525
doi: 10.1111/cge.14542
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : TGen Foundation

Informations de copyright

© 2024 John Wiley & Sons A/S. Published by John Wiley & Sons Ltd.

Références

Shi RM, Kobayashi T, Kikuchi A, et al. Phenytoin‐responsive epileptic encephalopathy with a tandem duplication involving FGF12. Neurol Genet. 2017;3:e133.
Oda Y, Uchiyama Y, Motomura A, et al. Entire FGF12 duplication by complex chromosomal rearrangements associated with West syndrome. J Hum Genet. 2019;64:1005‐1014.
Verheyen S, Speicher MR, Ramler B, Plecko B. Childhood‐onset epileptic encephalopathy due to FGF12 exon 1–4 tandem duplication. Neurol Genet. 2020;6:e494. doi:10.1212/NXG.0000000000000494
Willemsen MH, Goel H, Verhoeven JS, et al. Epilepsy phenotype in individuals with chromosomal duplication encompassing FGF12. Epilepsia Open. 2020;5:301‐306.
Seiffert S, Pendziwiat M, Bierhals T, et al. Modulating effects of FGF12 variants on NaV12 and NaV16 being associated with developmental and epileptic encephalopathy and autism spectrum disorder: a case series. eBioMedicine. 2022;83:104234. doi:10.1016/j.ebiom.2022.104234

Auteurs

Anna Abraham (A)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Keri Ramsey (K)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Newell Belnap (N)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Szabolcs Szelinger (S)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Wayne Jepsen (W)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Chris Balak (C)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Meredith Sanchez-Castillo (M)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Marcus Naymik (M)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Anna Bonfitto (A)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Sampathkumar Rangasamy (S)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Semyon Kruglyak (S)

Element Biosciences, San Diego, California, USA.

Matthew Huentelman (M)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Vinodh Narayanan (V)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, Arizona, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, Arizona, USA.

Classifications MeSH