Safety, immunogenicity and efficacy of the self-amplifying mRNA ARCT-154 COVID-19 vaccine: pooled phase 1, 2, 3a and 3b randomized, controlled trials.


Journal

Nature communications
ISSN: 2041-1723
Titre abrégé: Nat Commun
Pays: England
ID NLM: 101528555

Informations de publication

Date de publication:
14 May 2024
Historique:
received: 05 09 2023
accepted: 16 04 2024
medline: 15 5 2024
pubmed: 15 5 2024
entrez: 14 5 2024
Statut: epublish

Résumé

Combination of waning immunity and lower effectiveness against new SARS-CoV-2 variants of approved COVID-19 vaccines necessitates new vaccines. We evaluated two doses, 28 days apart, of ARCT-154, a self-amplifying mRNA COVID-19 vaccine, compared with saline placebo in an integrated phase 1/2/3a/3b controlled, observer-blind trial in Vietnamese adults (ClinicalTrial.gov identifier: NCT05012943). Primary safety and reactogenicity outcomes were unsolicited adverse events (AE) 28 days after each dose, solicited local and systemic AE 7 days after each dose, and serious AEs throughout the study. Primary immunogenicity outcome was the immune response as neutralizing antibodies 28 days after the second dose. Efficacy against COVID-19 was assessed as primary and secondary outcomes in phase 3b. ARCT-154 was well tolerated with generally mild-moderate transient AEs. Four weeks after the second dose 94.1% (95% CI: 92.1-95.8) of vaccinees seroconverted for neutralizing antibodies, with a geometric mean-fold rise from baseline of 14.5 (95% CI: 13.6-15.5). Of 640 cases of confirmed COVID-19 eligible for efficacy analysis most were due to the Delta (B.1.617.2) variant. Efficacy of ARCT-154 was 56.6% (95% CI: 48.7- 63.3) against any COVID-19, and 95.3% (80.5-98.9) against severe COVID-19. ARCT-154 vaccination is well tolerated, immunogenic and efficacious, particularly against severe COVID-19 disease.

Identifiants

pubmed: 38744844
doi: 10.1038/s41467-024-47905-1
pii: 10.1038/s41467-024-47905-1
doi:

Types de publication

Journal Article Randomized Controlled Trial Clinical Trial, Phase I Clinical Trial, Phase III Clinical Trial, Phase II

Langues

eng

Sous-ensembles de citation

IM

Pagination

4081

Informations de copyright

© 2024. The Author(s).

Références

Lenharo M. WHO declares end to COVID-19's emergency phase. Nature https://doi.org/10.1038/d41586-023-01559-z (2023).
Jacobs, J. L., Haidar, G. & Mellors, J. W. COVID-19: challenges of viral variants. Ann. Rev. Med. 74, 31–53 (2023).
doi: 10.1146/annurev-med-042921-020956 pubmed: 35850493
Shao, W. et al. Effectiveness of COVID-19 vaccines against SARS-CoV-2 variants of concern in real-world: a literature review and meta-analysis. Emerg. Microbes. Infect. 11, 2383–2392 (2022).
doi: 10.1080/22221751.2022.2122582 pubmed: 36069511 pmcid: 9542696
Cocherie, T. et al. Epidemiology and characteristics of SARS-CoV-2 Variants of Concern: the impacts of the Spike mutations. Microorganisms 11, 30 (2022).
doi: 10.3390/microorganisms11010030 pubmed: 36677322 pmcid: 9866527
Bernal, J. L. et al. Effectiveness of covid-19 vaccines against the B.1.617.2 (Delta) variant. N. Engl. J. Med. 385, 585–594 (2021).
doi: 10.1056/NEJMoa2108891
Buchan, S. A. et al. Estimated effectiveness of COVID-19 vaccines against Omicron or Delta symptomatic infection and severe outcomes. JAMA Netw. Open 5, e2232760 (2022).
doi: 10.1001/jamanetworkopen.2022.32760 pubmed: 36136332 pmcid: 9500552
Risk, M. et al. Comparative effectiveness of coronavirus disease 2019 (COVID-19) vaccines against the Delta variant. Clin. Infect. Dis. 75, e623–e629 (2022).
doi: 10.1093/cid/ciac106 pubmed: 35137006 pmcid: 9047165
Tseng, H. F. et al. Effectiveness of mRNA-1273 against SARS-CoV-2 Omicron and Delta variants. Nat. Med. 28, 1063–1071 (2022).
doi: 10.1038/s41591-022-01753-y pubmed: 35189624 pmcid: 9117141
Andrejko, K. L. et al. Waning of 2-dose BNT162b2 and mRNA-1273 vaccine effectiveness against symptomatic SARS-CoV-2 infection accounting for depletion-of-susceptibles bias. Am J Epidemiol 192, 895–907 (2023).
doi: 10.1093/aje/kwad017 pubmed: 36702469 pmcid: 10236522
Wolter, N. et al. Early assessment of the clinical severity of the SARS-CoV-2 omicron variant in South Africa: a data linkage study. Lancet 399, 437–446 (2022).
doi: 10.1016/S0140-6736(22)00017-4 pubmed: 35065011 pmcid: 8769664
He, X., Hong, W., Pan, X., Lu, G. & Wei, X. SARS-CoV-2 omicron variant: characteristics and prevention. MedComm 2, 838–845 (2021).
doi: 10.1002/mco2.110 pubmed: 34957469 pmcid: 8693031
Lundstrom, K. Self-replicating RNA viruses for vaccine development against infectious diseases and cancer. Vaccines (Basel) 9, 1187 (2021).
doi: 10.3390/vaccines9101187 pubmed: 34696295
Bloom, K., van den Berg, F. & Arbuthnot, P. Self-amplifying RNA vaccines for infectious diseases. Gene Ther. 28, 117–129 (2021).
doi: 10.1038/s41434-020-00204-y pubmed: 33093657
Lundstrom, K. The potential of self-amplifying RNA vaccines for infectious diseases and COVID-19. Vaccine Res. 7, 25–37 (2020).
doi: 10.29252/vacres.7.1.25
Vogel, A. B. et al. Self-amplifying RNA vaccines give equivalent protection against influenza to mRNA vaccines but at much lower doses. Mol. Ther. 26, 446–455 (2018).
doi: 10.1016/j.ymthe.2017.11.017 pubmed: 29275847
Komori, M. et al. saRNA vaccine expressing membrane-anchored RBD elicits broad and durable immunity against SARS-CoV-2 variants of concern. Nat. Commun. 14, 2810 (2023).
doi: 10.1038/s41467-023-38457-x pubmed: 37208330 pmcid: 10199074
Pollock, K. M. et al. Safety and immunogenicity of a self-amplifying RNA vaccine against COVID-19: COVAC1, a phase I, dose-ranging trial. EClinicalMedicine 44, 101262 (2022).
doi: 10.1016/j.eclinm.2021.101262 pubmed: 35043093 pmcid: 8759012
Palmer, C. D. et al. GRT-R910: a self-amplifying mRNA SARS-CoV-2 vaccine boosts immunity for ≥6 months in previously-vaccinated older adults. Nat. Commun. 14, 3274 (2023).
doi: 10.1038/s41467-023-39053-9 pubmed: 37280238 pmcid: 10242235
Low, J. G. et al. A phase I/2 randomized, double-blinded, placebo controlled ascending dose trial to assess the safety, tolerability and immunogenicity of ARCT-021 in healthy adults. npj Vaccines 7, 161 (2022).
doi: 10.1038/s41541-022-00590-x pubmed: 36513697 pmcid: 9745278
Polack, F. P. et al. Safety and efficacy of the BNT162b2 mRNA Covid-19 vaccine. N. Engl. J. Med. 383, 2603–2615 (2020).
doi: 10.1056/NEJMoa2034577 pubmed: 33301246
Baden, L. R. et al. Efficacy and safety of the mRNA-1273 SARS-CoV-2 vaccine. N. Engl. J. Med. 384, 403–416 (2021).
doi: 10.1056/NEJMoa2035389 pubmed: 33378609
The Institute for Health Metrics and Evaluation (IHME). COVID-19 vaccine efficacy summary, November 18, 2022. Available at: https://www.healthdata.org/research-analysis/diseases-injuries/covid/covid-19-vaccine-efficacy-summary Accessed on November 14, 2023.
Tsang, N. N. Y., So, H. C., Cowling, B. J., Leung, G. M. & Ip, D. K. M. Effectiveness of BNT162b2 and CoronaVac COVID-19 vaccination against asymptomatic and symptomatic infection of SARS-CoV-2 omicron BA.2 in Hong Kong: a prospective cohort study. Lancet Infect. Dis. 23, 421–434 (2023).
doi: 10.1016/S1473-3099(22)00732-0 pubmed: 36521506
Walsh, E. E. et al. Safety and immunogenicity of two RNA-based Covid-19 vaccine candidates. N. Engl. J. Med. 383, 2439–2450 (2020).
doi: 10.1056/NEJMoa2027906 pubmed: 33053279
Oda, Y. et al. Immunogenicity and safety of a booster dose of a self-amplifying RNA COVID-19 vaccine (ARCT-154) versus BNT162b2 mRNA COVID-19 vaccine: a double-blind, multicentre, randomised, controlled, phase 3, non-inferiority trial. Lancet Infect. Dis. 24, 351–360 (2024).
doi: 10.1016/S1473-3099(23)00650-3 pubmed: 38141632
Khoury, D. S. et al. Neutralizing antibody levels are highly predictive of immune protection from symptomatic SARS-CoV-2 infection. Nat. Med. 27, 1205–1211 (2021).
doi: 10.1038/s41591-021-01377-8 pubmed: 34002089
Jones, J. M. et al. Estimates of SARS-CoV-2 seroprevalence and incidence of primary SARS-CoV-2 infections among blood donors, by COVID-19 vaccination status - United States, April 2021-September 2022. MMWR Morb. Mortal. Wkly. Rep. 72, 601–605 (2023).
doi: 10.15585/mmwr.mm7222a3 pubmed: 37262007 pmcid: 10243484
Oda, Y. et al. Comment: persistence of immune responses of a self amplifying RNA COVID-19 vaccine (ARCT-154) versus BNT162b2. Lancet Infect. Dis. 24, 341–343 (2024).
doi: 10.1016/S1473-3099(24)00060-4 pubmed: 38310906
Regan, J. J. et al. Use of updated COVID-19 vaccines 2023–2024 formula for persons aged ≥6 Months: Recommendations of the Advisory Committee on Immunization Practices — United States, September 2023. Morb Mortal Wkly Rep 72, 1140–1146 (2023).
doi: 10.15585/mmwr.mm7242e1
de Alwis, R. et al. A single dose of self-transcribing and replicating RNA-based SARS-CoV-2 vaccine produces protective adaptive immunity in mice. Mol. Ther. 29, 1970–1983 (2021).
doi: 10.1016/j.ymthe.2021.04.001 pubmed: 33823303 pmcid: 8019652
Szubert, A. J. et al. COVAC1 phase 2a expanded safety and immunogenicity study of a self-amplifying RNA vaccine against SARS-CoV-2. eClinicalMedicine 56, 101823 (2023).
doi: 10.1016/j.eclinm.2022.101823 pubmed: 36684396 pmcid: 9837478
CDC. Underlying medical conditions associated with higher risk for severe COVID-19: information for healthcare professionals/Summary of Conditions with Evidence. 13 May 2021. Available at: https://www.cdc.gov/coronavirus/2019-ncov/hcp/clinical-care/underlyingconditions.html (updated Feb 9, 2023) Accessed on August 1, 2023.
Pagano, M. & Gauvreau, K. Principles of Biostatistics 2nd edn (Chapman and Hall/CRC, 2018).
Deeks, J. J. & Higgins J. P. T. Statistical algorithms in Review Manager 5. Available from https://training.cochrane.org/ (2010).

Auteurs

Nhân Thị Hồ (NT)

Vinmec-VinUni Institute of Immunology, Vinmec Healthcare System, Hanoi, Vietnam.

Steven G Hughes (SG)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Van Thanh Ta (VT)

Hanoi Medical University, Hanoi, Vietnam.

Lân Trọng Phan (LT)

Pasteur Institute, Ho Chi Minh City, Vietnam.

Quyết Đỗ (Q)

Vietnam Military Medical University, Hanoi, Vietnam.

Thượng Vũ Nguyễn (TV)

Pasteur Institute, Ho Chi Minh City, Vietnam.

Anh Thị Văn Phạm (ATV)

Hanoi Medical University, Hanoi, Vietnam.

Mai Thị Ngọc Đặng (M)

Hanoi Medical University, Hanoi, Vietnam.

Lượng Viết Nguyễn (LV)

Vietnam Military Medical University, Hanoi, Vietnam.

Quang Vinh Trịnh (QV)

Hanoi Medical University, Hanoi, Vietnam.

Hùng Ngọc Phạm (HN)

Vietnam Military Medical University, Hanoi, Vietnam.

Mến Văn Chử (MV)

Vietnam Military Medical University, Hanoi, Vietnam.

Toàn Trọng Nguyễn (TT)

Pasteur Institute, Ho Chi Minh City, Vietnam.

Quang Chấn Lương (QC)

Pasteur Institute, Ho Chi Minh City, Vietnam.

Vy Thị Tường Lê (VT)

Pasteur Institute, Ho Chi Minh City, Vietnam.

Thắng Văn Nguyễn (TV)

Vietnam Military Medical University, Hanoi, Vietnam.

Lý-Thi-Lê Trần (LT)

Hi-tech Center, Vinmec Healthcare System, Hanoi, Vietnam.
Vietnam Biocare Biotechnology Jointstock Company, Hanoi, Vietnam.

Anh Thi Van Luu (A)

Vietnam Biocare Biotechnology Jointstock Company, Hanoi, Vietnam.

Anh Ngoc Nguyen (AN)

Vietnam Biocare Biotechnology Jointstock Company, Hanoi, Vietnam.

Nhung-Thi-Hong Nguyen (NT)

Vinmec-VinUni Institute of Immunology, Vinmec Healthcare System, Hanoi, Vietnam.

Hai-Son Vu (HS)

Vinmec-VinUni Institute of Immunology, Vinmec Healthcare System, Hanoi, Vietnam.

Jonathan M Edelman (JM)

CSL Sequiris Inc, New Jersey, USA.

Suezanne Parker (S)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Brian Sullivan (B)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Sean Sullivan (S)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Qian Ruan (Q)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Brenda Clemente (B)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Brian Luk (B)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Kelly Lindert (K)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Dina Berdieva (D)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Kat Murphy (K)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Rose Sekulovich (R)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Benjamin Greener (B)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Igor Smolenov (I)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Pad Chivukula (P)

Arcturus Therapeutics, Inc, San Diego, CA, USA.

Vân Thu Nguyễn (VT)

Vietnam Biocare Biotechnology Jointstock Company, Hanoi, Vietnam.

Xuan-Hung Nguyen (XH)

Vinmec-VinUni Institute of Immunology, Vinmec Healthcare System, Hanoi, Vietnam. v.hungnx1@vinmec.com.
Hi-tech Center, Vinmec Healthcare System, Hanoi, Vietnam. v.hungnx1@vinmec.com.
College of Health Sciences, Vin University, Hanoi, Vietnam. v.hungnx1@vinmec.com.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH