Severe Meningococcal Meningitis Revealing a Novel Form of Properdin Deficiency in a Previously Healthy 13-year-old Child.


Journal

The Pediatric infectious disease journal
ISSN: 1532-0987
Titre abrégé: Pediatr Infect Dis J
Pays: United States
ID NLM: 8701858

Informations de publication

Date de publication:
10 May 2024
Historique:
medline: 16 5 2024
pubmed: 16 5 2024
entrez: 16 5 2024
Statut: aheadofprint

Résumé

A 13-year-old boy was admitted with severe meningococcal meningitis. Immunologic workup revealed a properdin deficiency, and genetic sequencing of CFP identified a novel, private and predicted pathogenic variant in exon 8. The patient received broad immunizations and penicillin prophylaxis. Children with invasive meningococcal disease should be tested for complement deficiency.

Identifiants

pubmed: 38753997
doi: 10.1097/INF.0000000000004397
pii: 00006454-990000000-00866
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

Copyright © 2024 Wolters Kluwer Health, Inc. All rights reserved.

Déclaration de conflit d'intérêts

The authors have no conflicts of interest to disclose.

Références

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Auteurs

Martina Bevacqua (M)

From the Department of General Pediatrics and Pediatric Infectious Diseases.

Paul Bastard (P)

Pediatric Hematology-Immunology and Rheumatology Unit, Necker-Enfants Malades Hospital, APHP, Université Paris Cité.
Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Necker-Enfants Malades Hospital.
Imagine Institute, Paris Cité University, Paris, France.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, New York.

Yael Pinhas (Y)

From the Department of General Pediatrics and Pediatric Infectious Diseases.

Mélodie Aubart (M)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Necker-Enfants Malades Hospital.
Pediatric Neurology Department.

Charles-Joris Roux (CJ)

Department of Pediatric Radiology, Necker-Enfants Malades Hospital, APHP.

Muhamed-Kheir Taha (MK)

National Reference Center for Meningococci and Haemophilus influenzae, Invasive Bacterial Infections Unit, Institut Pasteur, Université Paris Cité, Paris, France.

Jérémie F Cohen (JF)

From the Department of General Pediatrics and Pediatric Infectious Diseases.

Classifications MeSH