Enhancing Temozolomide (TMZ) chemosensitivity using CRISPR-dCas9-mediated downregulation of O

CRISPR-dCas9 Glioblastoma MGMT TMZ

Journal

Journal of neuro-oncology
ISSN: 1573-7373
Titre abrégé: J Neurooncol
Pays: United States
ID NLM: 8309335

Informations de publication

Date de publication:
19 May 2024
Historique:
received: 29 03 2024
accepted: 02 05 2024
medline: 19 5 2024
pubmed: 19 5 2024
entrez: 19 5 2024
Statut: aheadofprint

Résumé

Glioblastoma (GBM) stands out as the most prevalent and aggressive intracranial tumor, notorious for its poor prognosis. The current standard-of-care for GBM patients involves surgical resection followed by radiotherapy, combined with concurrent and adjuvant chemotherapy using Temozolomide (TMZ). The effectiveness of TMZ primarily relies on the activity of O In this study, we employed fusions of catalytically-inactive Cas9 (dCas9) to DNA methyltransferases (dCas9-DNMT3A) to selectively downregulation MGMT transcription by inducing methylation at MGMT promoter and K-M enhancer. Our findings demonstrate a significant reduction in MGMT expression, leading to intensified TMZ sensitivity in the HEK293T cell line. This study serves as a proof of concept for the utilization of CRISPR-based gene suppression to overcome TMZ resistance and enhance the lethal effect of TMZ in glioblastoma tumor cells.

Identifiants

pubmed: 38762829
doi: 10.1007/s11060-024-04708-0
pii: 10.1007/s11060-024-04708-0
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024. The Author(s), under exclusive licence to Springer Science+Business Media, LLC, part of Springer Nature.

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Auteurs

Yasamin Yousefi (Y)

Department of Medical Genetics, Faculty of Medicine, Mashhad University of Medical Sciences, Mashhad, Iran.
Department of chemistry, Faculty of Science, Ferdowsi University of Mashhad, Mashhad, Iran.

Reza Nejati (R)

Department of Pathology, Fox Chase Cancer Center, Temple University Health System, 19111, Philadelphia, PA, USA.

Atiye Eslahi (A)

Department of Medical Genetics, Faculty of Medicine, Mashhad University of Medical Sciences, Mashhad, Iran.

Farzaneh Alizadeh (F)

Department of Medical Genetics, Faculty of Medicine, Mashhad University of Medical Sciences, Mashhad, Iran.

Shima Farrokhi (S)

Department of Medical Genetics, Faculty of Medicine, Mashhad University of Medical Sciences, Mashhad, Iran.

Ahmad Asoodeh (A)

Department of chemistry, Faculty of Science, Ferdowsi University of Mashhad, Mashhad, Iran. Asoodeh@um.ac.ir.

Majid Mojarrad (M)

Department of Medical Genetics, Faculty of Medicine, Mashhad University of Medical Sciences, Mashhad, Iran. mojaradm@mums.ac.ir.

Classifications MeSH