Single center clinical analysis of macrophage activation syndrome complicating juvenile rheumatic diseases.


Journal

Pediatric rheumatology online journal
ISSN: 1546-0096
Titre abrégé: Pediatr Rheumatol Online J
Pays: England
ID NLM: 101248897

Informations de publication

Date de publication:
23 May 2024
Historique:
received: 05 11 2023
accepted: 25 04 2024
medline: 24 5 2024
pubmed: 24 5 2024
entrez: 23 5 2024
Statut: epublish

Résumé

Macrophage activation syndrome (MAS), an example of secondary hemophagocytic lymphohistiocytosis, is a potentially fatal complication of rheumatic diseases. We aimed to study the clinical and laboratory characteristics, treatment schemes, and outcomes of different rheumatic disorders associated with MAS in children. Early warning indicators of MAS have also been investigated to enable clinicians to make a prompt and accurate diagnosis. Fifty-five patients with rheumatic diseases complicated by MAS were enrolled between January 2017 and December 2022. Clinical and laboratory data were collected before disease onset, at diagnosis, and after treatment with MAS, and data were compared between patients with systemic juvenile idiopathic arthritis (sJIA), Kawasaki disease (KD), and systemic lupus erythematosus (SLE). A random forest model was established to show the importance score of each variable with a significant difference. Most (81.8%) instances of MAS occurred during the initial diagnosis of the underlying disease. Compared to the active stage of sJIA, the platelet count, erythrocyte sedimentation rate, and fibrinogen level in sJIA-MAS were significantly decreased, whereas ferritin, ferritin/erythrocyte sedimentation rate, aspartate aminotransferase, alanine aminotransferase, lactate dehydrogenase, and D-dimer levels were significantly increased. Ferritin level, ferritin/erythrocyte sedimentation rate, and platelet count had the greatest predictive value for sJIA-MAS. The level of IL-18 in the sJIA-MAS group was significantly higher than in the active sJIA group, whereas IL-6 levels were significantly lower. Most patients with MAS were treated with methylprednisolone pulse combined with cyclosporine, and no deaths occurred. Thrombocytopenia, ferritin levels, the ferritin/erythrocyte sedimentation rate, and elevated aspartate aminotransferase levels can predict the occurrence of MAS in patients with sJIA. Additionally, our analysis indicates that IL-18 plays an important role in the pathogenesis of MAS in sJIA-MAS.

Sections du résumé

BACKGROUND BACKGROUND
Macrophage activation syndrome (MAS), an example of secondary hemophagocytic lymphohistiocytosis, is a potentially fatal complication of rheumatic diseases. We aimed to study the clinical and laboratory characteristics, treatment schemes, and outcomes of different rheumatic disorders associated with MAS in children. Early warning indicators of MAS have also been investigated to enable clinicians to make a prompt and accurate diagnosis.
METHODS METHODS
Fifty-five patients with rheumatic diseases complicated by MAS were enrolled between January 2017 and December 2022. Clinical and laboratory data were collected before disease onset, at diagnosis, and after treatment with MAS, and data were compared between patients with systemic juvenile idiopathic arthritis (sJIA), Kawasaki disease (KD), and systemic lupus erythematosus (SLE). A random forest model was established to show the importance score of each variable with a significant difference.
RESULTS RESULTS
Most (81.8%) instances of MAS occurred during the initial diagnosis of the underlying disease. Compared to the active stage of sJIA, the platelet count, erythrocyte sedimentation rate, and fibrinogen level in sJIA-MAS were significantly decreased, whereas ferritin, ferritin/erythrocyte sedimentation rate, aspartate aminotransferase, alanine aminotransferase, lactate dehydrogenase, and D-dimer levels were significantly increased. Ferritin level, ferritin/erythrocyte sedimentation rate, and platelet count had the greatest predictive value for sJIA-MAS. The level of IL-18 in the sJIA-MAS group was significantly higher than in the active sJIA group, whereas IL-6 levels were significantly lower. Most patients with MAS were treated with methylprednisolone pulse combined with cyclosporine, and no deaths occurred.
CONCLUSIONS CONCLUSIONS
Thrombocytopenia, ferritin levels, the ferritin/erythrocyte sedimentation rate, and elevated aspartate aminotransferase levels can predict the occurrence of MAS in patients with sJIA. Additionally, our analysis indicates that IL-18 plays an important role in the pathogenesis of MAS in sJIA-MAS.

Identifiants

pubmed: 38783316
doi: 10.1186/s12969-024-00991-3
pii: 10.1186/s12969-024-00991-3
doi:

Substances chimiques

Ferritins 9007-73-2

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

58

Subventions

Organisme : National Natural Science Foundation of China
ID : 81202345
Organisme : National Natural Science Foundation of China
ID : 81771762, and 82271838

Informations de copyright

© 2024. The Author(s).

Références

Ravelli A, Davì S, Minoia F, Martini A, Cron RQ. Macrophage activation syndrome. Hematol Oncol Clin North Am. 2015;29:927–41. https://doi.org/10.1016/j.hoc.2015.06.010 .
doi: 10.1016/j.hoc.2015.06.010 pubmed: 26461152
Ravelli A, Grom AA, Behrens EM, Cron RQ. Macrophage activation syndrome as part of systemic juvenile idiopathic arthritis: diagnosis, genetics, pathophysiology and treatment. Genes Immun. 2012;13:289–98. https://doi.org/10.1038/gene.2012.3 .
doi: 10.1038/gene.2012.3 pubmed: 22418018
Cron RQ, Davi S, Minoia F, Ravelli A. Clinical features and correct diagnosis of macrophage activation syndrome. Expert Rev Clin Immunol. 2015;11:1043–53. https://doi.org/10.1586/1744666X.2015.1058159 .
doi: 10.1586/1744666X.2015.1058159 pubmed: 26082353
Behrens EM, Beukelman T, Paessler M, Cron RQ. Occult macrophage activation syndrome in patients with systemic juvenile idiopathic arthritis. J Rheumatol. 2007;34:1133–8. PMID:17343315.
pubmed: 17343315
Zeng HS, Xiong XY, Wei YD, Wang HW, Luo XP. Macrophage activation syndrome in 13 children with systemic-onset juvenile idiopathic arthritis. World J Pediatr. 2008;4:97–101. https://doi.org/10.1007/s12519-008-0018-6 .
doi: 10.1007/s12519-008-0018-6 pubmed: 18661762 pmcid: 7102092
Minoia F, Davì S, Horne A, Demirkaya E, Bovis F, Li C, et al. Clinical features, treatment, and outcome of macrophage activation syndrome complicating systemic juvenile idiopathic arthritis: a multinational, multicenter study of 362 patients. Arthritis Rheumatol. 2014;66:3160–9. https://doi.org/10.1002/art.38802 .
doi: 10.1002/art.38802 pubmed: 25077692
Ravelli A, Minoia F, Davì S, Horne A, Bovis F, Pistorio A, et al. Expert consensus on dynamics of laboratory tests for diagnosis of macrophage activation syndrome complicating systemic juvenile idiopathic arthritis. RMD Open. 2016;2:e000161. https://doi.org/10.1136/rmdopen-2015-000161 .
doi: 10.1136/rmdopen-2015-000161 pubmed: 26848401 pmcid: 4731834
Crayne CB, Albeituni S, Nichols KE, Cron RQ. The immunology of macrophage activation syndrome. Front Immunol. 2019;10:119. https://doi.org/10.3389/fimmu.2019.00119 .
doi: 10.3389/fimmu.2019.00119 pubmed: 30774631 pmcid: 6367262
Kaufman KM, Linghu B, Szustakowski JD, Husami A, Yang F, Zhang K, et al. Whole-exome sequencing reveals overlap between macrophage activation syndrome in systemic juvenile idiopathic arthritis and familial hemophagocytic lymphohistiocytosis. Arthritis Rheumatol. 2014;66:3486–95. https://doi.org/10.1002/art.38793 .
doi: 10.1002/art.38793 pubmed: 25047945 pmcid: 4321811
Vastert SJ, van Wijk R, D’Urbano LE, de Vooght KM, de Jager W, Ravelli A, et al. Mutations in the perforin gene can be linked to macrophage activation syndrome in patients with systemic onset juvenile idiopathic arthritis. Rheumatol (Oxf Engl). 2010;49:441–9. https://doi.org/10.1093/rheumatology/kep418 .
doi: 10.1093/rheumatology/kep418
Zhang K, Biroschak J, Glass DN, Thompson SD, Finkel T, Passo MH, et al. Macrophage activation syndrome in patients with systemic juvenile idiopathic arthritis is associated with MUNC13-4 polymorphisms. Arthritis Rheum. 2008;58:2892–6. https://doi.org/10.1002/art.23734 .
doi: 10.1002/art.23734 pubmed: 18759271 pmcid: 2779064
Gupta S, Weitzman S. Primary and secondary hemophagocytic lymphohistiocytosis: clinical features, pathogenesis and therapy. Expert Rev Clin Immunol. 2010;6:137–54. https://doi.org/10.1586/eci.09.58 .
doi: 10.1586/eci.09.58 pubmed: 20383897
Tripathy R, Panda AK, Das BK. Serum ferritin level correlates with SLEDAI scores and renal involvement in SLE. Lupus. 2015;24(1):82–9. https://doi.org/10.1177/0961203314552290 .
doi: 10.1177/0961203314552290 pubmed: 25253568
Petty RE, Southwood TR, Manners P, Baum J, Glass DN, Goldenberg J, et al. International League of Associations for Rheumatology classification of juvenile idiopathic arthritis: second revision. Edmonton, 2001. J Rheumatol. 2004;31(2):390–2. PMID: 14760812.
pubmed: 14760812
Newburger JW, Takahashi M, Gerber MA, Gewitz MH, Tani LY, Burns JC, et al. Diagnosis, treatment, and long-term management of Kawasaki disease: a statement for health professionals from the Committee on Rheumatic Fever, Endocarditis and Kawasaki Disease, Council on Cardiovascular Disease in the Young, American Heart Association. Circulation. 2004;110:2747–71. https://doi.org/10.1161/01.CIR.0000145143.19711.78 .
doi: 10.1161/01.CIR.0000145143.19711.78 pubmed: 15505111
Petri M, Orbai AM, Alarcón GS, et al. Derivation and validation of the systemic Lupus International collaborating clinics classification criteria for systemic lupus erythematosus. Arthritis Rheum. 2012;64(8):2677–86. https://doi.org/10.1002/art.34473 .
doi: 10.1002/art.34473 pubmed: 22553077 pmcid: 3409311
Ravelli A, Minoia F, Davì S, Horne A, Bovis F, Pistorio A, et al. 2016 classification criteria for macrophage activation syndrome complicating systemic juvenile idiopathic arthritis: a European League Against Rheumatism/American College of Rheumatology/Paediatric Rheumatology International Trials Organisation Collaborative Initiative. Arthritis Rheumatol. 2016;68:566–76. https://doi.org/10.1002/art.39332 .
doi: 10.1002/art.39332 pubmed: 26314788
Parodi A, Davì S, Pringe AB, Pistorio A, Ruperto N, Magni-Manzoni S, et al. Macrophage activation syndrome in juvenile systemic lupus erythematosus: a multinational multicenter study of thirty-eight patients. Arthritis Rheum. 2009;60:3388–99. https://doi.org/10.1002/art.24883 .
doi: 10.1002/art.24883 pubmed: 19877067
Schulert GS, Yasin S, Carey B, Chalk C, Do T, Schapiro AH, et al. Systemic juvenile idiopathic arthritis-associated lung disease: characterization and risk factors. Arthritis Rheumatol. 2019;71:1943–54. https://doi.org/10.1002/art.41073 .
doi: 10.1002/art.41073 pubmed: 31379071 pmcid: 6817389
Guo L, Xu Y, Qian X, et al. Sudden hypotension and increased serum Interferon-γ and Interleukin-10 predict early macrophage activation syndrome in patients with systemic juvenile idiopathic arthritis. J Pediatr. 2021;235:203–e2113. https://doi.org/10.1016/j.jpeds.2021.02.008 .
doi: 10.1016/j.jpeds.2021.02.008 pubmed: 33581106
Lerkvaleekul B, Vilaiyuk S. Macrophage activation syndrome: early diagnosis is key. Open Access Rheumatol. 2018;10:117–28. https://doi.org/10.2147/OARRR.S151013 .
doi: 10.2147/OARRR.S151013 pubmed: 30214327 pmcid: 6124446
Han SB, Lee SY. Macrophage activation syndrome in children with Kawasaki disease: diagnostic and therapeutic approaches. World J Pediatr. 2020;16:566–74. https://doi.org/10.1007/s12519-020-00360-6 .
doi: 10.1007/s12519-020-00360-6 pubmed: 32418074
Naveen R, Jain A, Muhammed H, et al. Macrophage activation syndrome in systemic lupus erythematosus and systemic-onset juvenile idiopathic arthritis: a retrospective study of similarities and dissimilarities. Rheumatol Int. 2021;41(3):625–31. https://doi.org/10.1007/s00296-020-04763-6 .
doi: 10.1007/s00296-020-04763-6 pubmed: 33388903
Eloseily EMA, Minoia F, Crayne CB, Beukelman T, Ravelli A, Cron RQ. Ferritin to erythrocyte sedimentation rate ratio: simple measure to identify macrophage activation syndrome in systemic juvenile idiopathic arthritis. ACR Open Rheumatol. 2019;1(6):345–9. https://doi.org/10.1002/acr2.11048 .
doi: 10.1002/acr2.11048 pubmed: 31777812 pmcid: 6857981
Sen ES, Clarke SL, Ramanan AV. Macrophage activation syndrome. Indian J Pediatr. 2016;83:248–53. https://doi.org/10.1007/s12098-015-1877-1 .
doi: 10.1007/s12098-015-1877-1 pubmed: 26400031
Mizuta M, Shimizu M, Irabu H, Usami M, Inoue N, Nakagishi Y, et al. Comparison of serum cytokine profiles in macrophage activation syndrome complicating different background rheumatic diseases in children. Rheumatol (Oxf Engl). 2021;60:231–8. https://doi.org/10.1093/rheumatology/keaa299 .
doi: 10.1093/rheumatology/keaa299
Weiss ES, Girard-Guyonvarc’h C, Holzinger D, de Jesus AA, Tariq Z, Picarsic J, et al. Interleukin-18 diagnostically distinguishes and pathogenically promotes human and murine macrophage activation syndrome. Blood. 2018;131(13):1442–55. https://doi.org/10.1182/blood-2017-12-820852 .
doi: 10.1182/blood-2017-12-820852 pubmed: 29326099 pmcid: 5877443
McClain KL, Allen CE. Fire behind the fury: il-18 and MAS. Blood. 2018;131:1393–4. https://doi.org/10.1182/blood-2018-02-828186 .
doi: 10.1182/blood-2018-02-828186 pubmed: 29599143
Yasin S, Fall N, Brown RA, Henderlight M, Canna SW, Girard-Guyonvarc’H C, et al. IL-18 as a biomarker linking systemic juvenile idiopathic arthritis and macrophage activation syndrome. Rheumatol (Oxf Engl). 2020;59:361–6. https://doi.org/10.1093/rheumatology/kez282 .
doi: 10.1093/rheumatology/kez282
Lin CI, Yu HH, Lee JH, Wang LC, Lin YT, Yang YH, et al. Clinical analysis of macrophage activation syndrome in pediatric patients with autoimmune diseases. Clin Rheumatol. 2012;31:1223–30. https://doi.org/10.1007/s10067-012-1998-0 .
doi: 10.1007/s10067-012-1998-0 pubmed: 22615046
Miettunen PM, Narendran A, Jayanthan A, Behrens EM, Cron RQ. Successful treatment of severe paediatric rheumatic disease-associated macrophage activation syndrome with interleukin-1 inhibition following conventional immunosuppressive therapy: case series with 12 patients. Rheumatol (Oxf Engl). 2011;50:417–9. https://doi.org/10.1093/rheumatology/keq218 .
doi: 10.1093/rheumatology/keq218
Xiong W, Lahita RG. Pragmatic approaches to therapy for systemic lupus erythematosus. Nat Rev Rheumatol. 2014;10:97–107. https://doi.org/10.1038/nrrheum.2013.157 .
doi: 10.1038/nrrheum.2013.157 pubmed: 24166241
Eloseily EM, Weiser P, Crayne CB, Haines H, Mannion ML, Stoll ML, et al. Benefit of anakinra in treating pediatric secondary hemophagocytic lymphohistiocytosis. Arthritis Rheumatol. 2020;72:326–34. https://doi.org/10.1002/art.41103 .
doi: 10.1002/art.41103 pubmed: 31513353
Wu J, Sun L, Tang X, Zheng Q, Guo L, Xu L, et al. Effective therapy of tocilizumab on systemic juvenile idiopathic arthritis-associated refractory macrophage activation syndrome. Mod Rheumatol. 2022;32:1114–21. https://doi.org/10.1093/mr/roab119 .
doi: 10.1093/mr/roab119 pubmed: 34971386
De Benedetti F, Grom AA, Brogan PA, Bracaglia C, Pardeo M, Marucci G, et al. Efficacy and safety of emapalumab in macrophage activation syndrome. Ann Rheum Dis. 2023;82:857–65. https://doi.org/10.1136/ard-2022-223739 .
doi: 10.1136/ard-2022-223739 pubmed: 37001971
Junga Z, Stitt R, Tracy C, Keith M. Novel use of Rituximab in macrophage activation syndrome secondary to systemic lupus erythematosus. BMJ Case Rep. 2017;2017:bcr2017221347. https://doi.org/10.1136/bcr-2017-221347 .
doi: 10.1136/bcr-2017-221347 pubmed: 28827301 pmcid: 5624074

Auteurs

Shuoyin Huang (S)

Department of Rheumatology and Immunology, Children's Hospital of Nanjing Medical University, Nanjing, 210008, China.

Yingying Liu (Y)

Department of Rheumatology and Immunology, Children's Hospital of Nanjing Medical University, Nanjing, 210008, China.

Wu Yan (W)

Department of Child Health Care, Children's Hospital of Nanjing Medical University, Nanjing, China.

Tonghao Zhang (T)

Department of Rheumatology and Immunology, Children's Hospital of Nanjing Medical University, Nanjing, 210008, China.

Panpan Wang (P)

Department of Rheumatology and Immunology, Children's Hospital of Nanjing Medical University, Nanjing, 210008, China.

Meifang Zhu (M)

Department of Rheumatology and Immunology, Children's Hospital of Nanjing Medical University, Nanjing, 210008, China.

Xiaohua Zhang (X)

Department of Rheumatology and Immunology, Children's Hospital of Nanjing Medical University, Nanjing, 210008, China.

Peng Zhou (P)

Department of Rheumatology and Immunology, Children's Hospital of Nanjing Medical University, Nanjing, 210008, China.

Zhidan Fan (Z)

Department of Rheumatology and Immunology, Children's Hospital of Nanjing Medical University, Nanjing, 210008, China. zhidanfan@njmu.edu.cn.

Haiguo Yu (H)

Department of Rheumatology and Immunology, Children's Hospital of Nanjing Medical University, Nanjing, 210008, China. haiguo_yu@njmu.edu.cn.

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