Split intein-mediated protein trans-splicing to express large dystrophins.
Journal
Nature
ISSN: 1476-4687
Titre abrégé: Nature
Pays: England
ID NLM: 0410462
Informations de publication
Date de publication:
17 Jul 2024
17 Jul 2024
Historique:
received:
09
05
2023
accepted:
12
06
2024
medline:
18
7
2024
pubmed:
18
7
2024
entrez:
17
7
2024
Statut:
aheadofprint
Résumé
Gene replacement using adeno-associated virus (AAV) vectors is a promising therapeutic approach for many diseases
Identifiants
pubmed: 39020181
doi: 10.1038/s41586-024-07710-8
pii: 10.1038/s41586-024-07710-8
doi:
Types de publication
Journal Article
Langues
eng
Sous-ensembles de citation
IM
Informations de copyright
© 2024. The Author(s), under exclusive licence to Springer Nature Limited.
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