Calculating the power of a planned individual participant data meta-analysis to examine prognostic factor effects for a binary outcome.

individual participant data (IPD) meta‐analysis power predictor effects prognostic factor effects sample size

Journal

Research synthesis methods
ISSN: 1759-2887
Titre abrégé: Res Synth Methods
Pays: England
ID NLM: 101543738

Informations de publication

Date de publication:
24 Jul 2024
Historique:
revised: 09 05 2024
received: 17 01 2024
accepted: 26 06 2024
medline: 24 7 2024
pubmed: 24 7 2024
entrez: 24 7 2024
Statut: aheadofprint

Résumé

Collecting data for an individual participant data meta-analysis (IPDMA) project can be time consuming and resource intensive and could still have insufficient power to answer the question of interest. Therefore, researchers should consider the power of their planned IPDMA before collecting IPD. Here we propose a method to estimate the power of a planned IPDMA project aiming to synthesise multiple cohort studies to investigate the (unadjusted or adjusted) effects of potential prognostic factors for a binary outcome. We consider both binary and continuous factors and provide a three-step approach to estimating the power in advance of collecting IPD, under an assumption of the true prognostic effect of each factor of interest. The first step uses routinely available (published) aggregate data for each study to approximate Fisher's information matrix and thereby estimate the anticipated variance of the unadjusted prognostic factor effect in each study. These variances are then used in step 2 to estimate the anticipated variance of the summary prognostic effect from the IPDMA. Finally, step 3 uses this variance to estimate the corresponding IPDMA power, based on a two-sided Wald test and the assumed true effect. Extensions are provided to adjust the power calculation for the presence of additional covariates correlated with the prognostic factor of interest (by using a variance inflation factor) and to allow for between-study heterogeneity in prognostic effects. An example is provided for illustration, and Stata code is supplied to enable researchers to implement the method.

Identifiants

pubmed: 39046258
doi: 10.1002/jrsm.1737
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Engineering & Physical Sciences Research Council (EPSRC)
ID : EP/Y018516/1
Organisme : Medical Research Council - National Institute for Health and Care Research (MRC-NIHR)
ID : MR/V038168/1
Organisme : Cancer Research UK
ID : C49297/A27294
Pays : United Kingdom

Informations de copyright

© 2024 The Author(s). Research Synthesis Methods published by John Wiley & Sons Ltd.

Références

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Auteurs

Rebecca Whittle (R)

Institute of Applied Health Research, College of Medical and Dental Sciences, University of Birmingham, Birmingham, UK.
National Institute for Health and Care Research (NIHR) Birmingham Biomedical Research Centre, UK.

Joie Ensor (J)

Institute of Applied Health Research, College of Medical and Dental Sciences, University of Birmingham, Birmingham, UK.
National Institute for Health and Care Research (NIHR) Birmingham Biomedical Research Centre, UK.

Miriam Hattle (M)

Institute of Applied Health Research, College of Medical and Dental Sciences, University of Birmingham, Birmingham, UK.
National Institute for Health and Care Research (NIHR) Birmingham Biomedical Research Centre, UK.

Paula Dhiman (P)

Centre for Statistics in Medicine, Nuffield Department of Orthopaedics, Rheumatology and Musculoskeletal Sciences, University of Oxford, Oxford, UK.

Gary S Collins (GS)

Centre for Statistics in Medicine, Nuffield Department of Orthopaedics, Rheumatology and Musculoskeletal Sciences, University of Oxford, Oxford, UK.

Richard D Riley (RD)

Institute of Applied Health Research, College of Medical and Dental Sciences, University of Birmingham, Birmingham, UK.
National Institute for Health and Care Research (NIHR) Birmingham Biomedical Research Centre, UK.

Classifications MeSH