Newborn Screening for X-Linked Adrenoleukodystrophy (X-ALD): Biochemical, Molecular, and Clinical Characteristics of Other Genetic Conditions.

ABCD1 gene PEX genes X-linked adrenoleukodystrophy (X-ALD) Zellweger spectrum disorder (ZSD) newborn screening (NBS)

Journal

Genes
ISSN: 2073-4425
Titre abrégé: Genes (Basel)
Pays: Switzerland
ID NLM: 101551097

Informations de publication

Date de publication:
26 Jun 2024
Historique:
received: 09 05 2024
revised: 20 06 2024
accepted: 24 06 2024
medline: 27 7 2024
pubmed: 27 7 2024
entrez: 27 7 2024
Statut: epublish

Résumé

The state of California (CA) added X-linked adrenoleukodystrophy (X-ALD) to newborn screening (NBS) in 2016 via the measurement of C26:0-lysophosphatidylcholine (C26:0-LPC) in a two-tier fashion, followed by sequencing of the

Identifiants

pubmed: 39062617
pii: genes15070838
doi: 10.3390/genes15070838
pii:
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Auteurs

Carlos F Mares Beltran (CF)

Division of Metabolic Disorders, Children's Hospital of Orange County (CHOC), Orange, CA 92868, USA.
Division of Medical Genetics, Albany Medical Center (AMC), Albany, NY 12208, USA.

Christina G Tise (CG)

Division of Medical Genetics, Department of Pediatrics, Lucile Packard Children's Hospital, Stanford University, Stanford, CA 94304, USA.

Rebekah Barrick (R)

Division of Metabolic Disorders, Children's Hospital of Orange County (CHOC), Orange, CA 92868, USA.

Annie D Niehaus (AD)

Division of Medical Genetics, Department of Pediatrics, Lucile Packard Children's Hospital, Stanford University, Stanford, CA 94304, USA.

Rebecca Sponberg (R)

Division of Metabolic Disorders, Children's Hospital of Orange County (CHOC), Orange, CA 92868, USA.

Richard Chang (R)

Division of Metabolic Disorders, Children's Hospital of Orange County (CHOC), Orange, CA 92868, USA.

Gregory M Enns (GM)

Division of Medical Genetics, Department of Pediatrics, Lucile Packard Children's Hospital, Stanford University, Stanford, CA 94304, USA.

Jose E Abdenur (JE)

Division of Metabolic Disorders, Children's Hospital of Orange County (CHOC), Orange, CA 92868, USA.

Classifications MeSH