Hematological features and alternate diagnoses in critically ill thrombotic antiphospholipid syndrome patients.

ADAMTS13 Antiphospholipid syndrome Catastrophic antiphospholipid syndrome Heparin-induced thrombocytopenia Intensive care unit

Journal

Clinical rheumatology
ISSN: 1434-9949
Titre abrégé: Clin Rheumatol
Pays: Germany
ID NLM: 8211469

Informations de publication

Date de publication:
29 Jul 2024
Historique:
received: 12 03 2024
accepted: 26 06 2024
revised: 14 05 2024
medline: 29 7 2024
pubmed: 29 7 2024
entrez: 29 7 2024
Statut: aheadofprint

Résumé

Severe thrombotic antiphospholipid syndrome (APS) frequently affects the kidney, heart, and central nervous system. The precise frequency, clinical picture, differential diagnoses, and outcome of APS-related hematological involvement are lacking, especially in patients requiring ICU admission. This study aimed to describe the hematological manifestations associated with critically ill thrombotic APS patients and catastrophic antiphospholipid syndrome. This French, national, multicenter, retrospective study, conducted, from January 2000 to September 2018, included all APS patients admitted to 24 participating centers' ICUs with any new thrombotic manifestation. The prevalence of hematological manifestations and their associated outcomes were studied. One hundred and thirty-four patients, female 72%, median [IQR] age 45 [34-56] years, with 152 episodes were included. Anemia was present in 95% of episodes and thrombocytopenia in 93%. The lowest values for hemoglobin and platelets were 7.1 [6.3-8.8] g/dL and 38 [21-60] g/L, respectively. The lowest platelet count below 20 g/L was significantly associated with a higher in-ICU mortality rate (50%, p < 0.0001). A thrombotic microangiopathy syndrome (TMA) syndrome was seen in 16 patients (12%) and was associated with higher in-hospital mortality (p = 0.05). Median ADAMTS-13 levels were 44% [27-74]. Anti-ADAMTS13 antibodies were tested in 11 patients and found negative in all. A suspicion of heparin-induced thrombocytopenia (HIT) was raised in 66 patients but only four patients were classified as definite HIT. Disseminated intravascular coagulation (DIC) was seen in 51% of patients. Thrombocytopenia is very frequent in severe APS patients and may be related to TMA, HIT, or DIC. Deciphering the mechanisms of thrombocytopenia is decisive in CAPS patients. Key Points • Thrombocytopenia is the hallmark laboratory finding in CAPS. • A complete thrombotic microangiopathy pattern is infrequent in CAPS patients. • Alternate diagnoses of CAPS, especially heparin-induced thrombocytopenia, need to be adequately investigated.

Identifiants

pubmed: 39073513
doi: 10.1007/s10067-024-07051-x
pii: 10.1007/s10067-024-07051-x
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024. The Author(s), under exclusive licence to International League of Associations for Rheumatology (ILAR).

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Auteurs

Levi-Dan Azoulay (LD)

Syndrome Des Anticorps Anti-Phospholipides Et Autres Maladies Auto-Immunes Systémiques Rares, Sorbonne Université, Assistance Publique-Hôpitaux de Paris (AP-HP), Hôpital La Pitié-Salpêtrière, Institut E3M, Service de Médecine Interne 2, Centre de Référence National Lupus Systémique, Paris, France.

Thomas Frapard (T)

Syndrome Des Anticorps Anti-Phospholipides Et Autres Maladies Auto-Immunes Systémiques Rares, Sorbonne Université, Assistance Publique-Hôpitaux de Paris (AP-HP), Hôpital La Pitié-Salpêtrière, Institut E3M, Service de Médecine Interne 2, Centre de Référence National Lupus Systémique, Paris, France.

Romaric Larcher (R)

Service de Médecine Intensive-Réanimation, Hôpital Lapeyronie, Centre Hospitalier Universitaire (CHU) de Montpellier, PhyMedExp, Université de Montpellier, INSERM, CNRS, Montpellier, France.

Frédéric Pène (F)

Service de Médecine Intensive-Réanimation, Hôpital Cochin, Hôpitaux Universitaires Paris Centre, APHP, Université Paris Descartes, Paris, France.

Laurent Argaud (L)

Service de Médecine Intensive-Réanimation, Hôpital Edouard-Herriot, Hospices Civils de Lyon, Lyon, France.

Julien Mayaux (J)

AP-HP, Hôpital La Pitié-Salpêtrière, Service de Pneumologie, Médecine Intensive Et Réanimation Médicale, Département R3S, Sorbonne Université, INSERM UMRS1158, Neurophysiologie Respiratoire Expérimentale Et Clinique, Paris, France.

Matthieu Jamme (M)

Sorbonne Université, AP-HP, Hôpital Tenon, Service d'Urgences Néphrologiques Et de Transplantation Rénale, Paris, France.

Remi Coudroy (R)

CHU de Poitiers, Service de Médecine Intensive Réanimation, Université de Poitiers, INSERM CIC 1402, IS-ALIVE Research Group, 86000, Poitiers, France.

Alexis Mathian (A)

Syndrome Des Anticorps Anti-Phospholipides Et Autres Maladies Auto-Immunes Systémiques Rares, Sorbonne Université, Assistance Publique-Hôpitaux de Paris (AP-HP), Hôpital La Pitié-Salpêtrière, Institut E3M, Service de Médecine Interne 2, Centre de Référence National Lupus Systémique, Paris, France.

Aude Gibelin (A)

Service de Médecine Intensive Réanimation, Hôpital Tenon, AP-HP, Faculté de Médecine Sorbonne Université, Paris, France.

Elie Azoulay (E)

Service de Médecine Intensive-Réanimation, Hôpital Saint-Louis, AP-HP, Paris, France.

Yacine Tandjaoui-Lambiotte (Y)

Pneumologie & Infectiologie, CH Saint Denis, 93200, Saint Denis, France.
INSERM UMR 1137 IAME, Paris, France.
INSERM UMR 1272 Hypoxie & Poumon, Bobigny, France.

Auguste Dargent (A)

Service de Médecine Intensive-Réanimation, CHU Dijon, INSERM UMR 1231 LabEx Lipstic, Dijon, France.

François-Michel Beloncle (FM)

Département de Médecine Intensive-Réanimation Et Médecine Hyperbare, CHU d'Angers, Université d'Angers, Angers, France.

Jean-Herlé Raphalen (JH)

Service d'Anesthésie Et de Réanimation, Hôpital Necker, Université Paris Descartes, AP-HP, Paris, France.

Nicolas Bréchot (N)

Service de Médecine Intensive-Réanimation, Hôpital Européen George-Pompidou, Université Paris Descartes, AP-HP, Paris, France.

Nicolas de Prost (N)

Service de Médecine Intensive-Réanimation, CHU Henri-Mondor, AP-HP, Créteil, France.

Jérôme Devaquet (J)

Service de Réanimation Polyvalente, Hôpital Foch, Suresnes, France.

Damien Contou (D)

Service de Réanimation Polyvalente, Centre Hospitalier Victor-Dupouy, Argenteuil, France.

Samuel Gaugain (S)

Département d'Anesthésie Et Réanimation, Hôpital Saint-Louis-Lariboisière, Université Paris Diderot, AP-HP, Paris, France.

Pierre Trouiller (P)

Service de Réanimation Polyvalente Et Unité de Surveillance Continue, Hôpital Antoine-Béclère, Hôpitaux Universitaires Paris-Sud, AP-HP, Clamart, France.

Steven Grangé (S)

Service de Néphrologie, Hôpital Charles-Nicolle, CHU de Rouen, Rouen, France.

Stanislas Ledochowski (S)

Service de Réanimation Polyvalente, Médipôle Lyon-Villeurbanne, Ramsay Santé, Villeurbanne, France.

Jérémie Lemarie (J)

Service de Réanimation Médicale, Hôpital Central, CHRU de Nancy, Nancy, France.

Stanislas Faguer (S)

Département de Néphrologie Et Transplantation d'Organes, Unité de Réanimation, Centre de Référence Des Maladies Rénales Rares, Hôpital Rangueil, CHU de Toulouse, Toulouse, France.

Vincent Degos (V)

Département d'Anesthésie-Réanimation, Unité d'Anesthésie-Réanimation Tête Et Cou, Sorbonne Université, Hôpital La Pitié-Salpêtrière, APHP, Paris, France.

Corinne Frere (C)

Sorbonne Université, AP-HP, Hôpital La Pitié-Salpêtrière, Service d'Hematologie Biologique Et d'Hemostase, Paris, France.

Paul Quentric (P)

Syndrome Des Anticorps Anti-Phospholipides Et Autres Maladies Auto-Immunes Systémiques Rares, Sorbonne Université, Assistance Publique-Hôpitaux de Paris (AP-HP), Hôpital La Pitié-Salpêtrière, Institut E3M, Service de Médecine Interne 2, Centre de Référence National Lupus Systémique, Paris, France.
Sorbonne Université, Inserm, Centre d'Immunologie Et Des Maladies Infectieuses, CIMI-Paris, Paris, France.

Quentin Moyon (Q)

Syndrome Des Anticorps Anti-Phospholipides Et Autres Maladies Auto-Immunes Systémiques Rares, Sorbonne Université, Assistance Publique-Hôpitaux de Paris (AP-HP), Hôpital La Pitié-Salpêtrière, Institut E3M, Service de Médecine Interne 2, Centre de Référence National Lupus Systémique, Paris, France.
Sorbonne Université, APHP, Hôpital La Pitié-Salpêtrière, Service de Médecine Intensive-Réanimation, Paris, France.
Sorbonne Université, INSERM, UMRS_1166-ICAN, Institut de Cardiométabolisme Et Nutrition (ICAN), Paris, France.

Charles-Edouard Luyt (CE)

Sorbonne Université, Inserm, Centre d'Immunologie Et Des Maladies Infectieuses, CIMI-Paris, Paris, France.
Sorbonne Université, APHP, Hôpital La Pitié-Salpêtrière, Service de Médecine Intensive-Réanimation, Paris, France.

Alain Combes (A)

Sorbonne Université, APHP, Hôpital La Pitié-Salpêtrière, Service de Médecine Intensive-Réanimation, Paris, France.
Sorbonne Université, INSERM, UMRS_1166-ICAN, Institut de Cardiométabolisme Et Nutrition (ICAN), Paris, France.

Zahir Amoura (Z)

Syndrome Des Anticorps Anti-Phospholipides Et Autres Maladies Auto-Immunes Systémiques Rares, Sorbonne Université, Assistance Publique-Hôpitaux de Paris (AP-HP), Hôpital La Pitié-Salpêtrière, Institut E3M, Service de Médecine Interne 2, Centre de Référence National Lupus Systémique, Paris, France.
Sorbonne Université, Inserm, Centre d'Immunologie Et Des Maladies Infectieuses, CIMI-Paris, Paris, France.

Marc Pineton de Chambrun (M)

Syndrome Des Anticorps Anti-Phospholipides Et Autres Maladies Auto-Immunes Systémiques Rares, Sorbonne Université, Assistance Publique-Hôpitaux de Paris (AP-HP), Hôpital La Pitié-Salpêtrière, Institut E3M, Service de Médecine Interne 2, Centre de Référence National Lupus Systémique, Paris, France. marc.pinetondechambrun@aphp.fr.
Sorbonne Université, Inserm, Centre d'Immunologie Et Des Maladies Infectieuses, CIMI-Paris, Paris, France. marc.pinetondechambrun@aphp.fr.
Sorbonne Université, APHP, Hôpital La Pitié-Salpêtrière, Service de Médecine Intensive-Réanimation, Paris, France. marc.pinetondechambrun@aphp.fr.
Sorbonne Université, INSERM, UMRS_1166-ICAN, Institut de Cardiométabolisme Et Nutrition (ICAN), Paris, France. marc.pinetondechambrun@aphp.fr.

Classifications MeSH