Mild retinitis pigmentosa, including sector retinitis pigmentosa associated with 2 pathogenic variants in

Usher syndrome ciliopathies dystrophy genetic hearing loss inherited retinal disease inherited retinal dystrophy retinitis pigmentosa sector retinitis pigmentosa

Journal

Ophthalmic genetics
ISSN: 1744-5094
Titre abrégé: Ophthalmic Genet
Pays: England
ID NLM: 9436057

Informations de publication

Date de publication:
02 Aug 2024
Historique:
medline: 2 8 2024
pubmed: 2 8 2024
entrez: 2 8 2024
Statut: aheadofprint

Résumé

Biallelic pathogenic variants in Clinical examination included medical history, comprehensive ophthalmologic examination, and multimodal retinal imaging, and in case 1 and 2, full-field electroretinography (ERG). Genetic analysis was performed in all cases, and segregation testing of proband relatives was performed in case 1 and 3. Three unrelated cases presented with variable clinical phenotype for USH1 and were found to have two pathogenic variants in Patients harbouring c.5237 G > A: p.Arg1746Gln variants in

Sections du résumé

BACKGROUND UNASSIGNED
Biallelic pathogenic variants in
MATERIALS AND METHODS UNASSIGNED
Clinical examination included medical history, comprehensive ophthalmologic examination, and multimodal retinal imaging, and in case 1 and 2, full-field electroretinography (ERG). Genetic analysis was performed in all cases, and segregation testing of proband relatives was performed in case 1 and 3.
RESULTS UNASSIGNED
Three unrelated cases presented with variable clinical phenotype for USH1 and were found to have two pathogenic variants in
CONCLUSION UNASSIGNED
Patients harbouring c.5237 G > A: p.Arg1746Gln variants in

Identifiants

pubmed: 39092760
doi: 10.1080/13816810.2024.2362210
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1-6

Auteurs

Pankaja Dhoble (P)

Genetics, Moorfields Eye Hospital NHS Foundation Trust, London, UK.

Thales A C de Guimarães (TAC)

Genetics, Moorfields Eye Hospital NHS Foundation Trust, London, UK.
UCL Institute of Ophthalmology, University College London, London, UK.

Andrew R Webster (AR)

Genetics, Moorfields Eye Hospital NHS Foundation Trust, London, UK.
UCL Institute of Ophthalmology, University College London, London, UK.

Michel Michaelides (M)

Genetics, Moorfields Eye Hospital NHS Foundation Trust, London, UK.
UCL Institute of Ophthalmology, University College London, London, UK.

Classifications MeSH