Sotos Syndrome: Deep Neuroimaging Phenotyping Reveals a High Prevalence of Malformations of Cortical Development.


Journal

AJNR. American journal of neuroradiology
ISSN: 1936-959X
Titre abrégé: AJNR Am J Neuroradiol
Pays: United States
ID NLM: 8003708

Informations de publication

Date de publication:
15 Aug 2024
Historique:
received: 21 03 2024
accepted: 16 05 2024
medline: 16 8 2024
pubmed: 16 8 2024
entrez: 15 8 2024
Statut: aheadofprint

Résumé

Sotos syndrome is a rare autosomal dominant condition caused by pathogenic mutations in the This multicenter, multinational, retrospective observational cohort study systematically analyzed the clinical characteristics and neuroimaging features of 77 individuals with genetically diagnosed Sotos syndrome, via central consensus review with 3 pediatric neuroradiologists. In addition to previously described features, malformations of cortical development were identified in most patients (95.0%), typically dysgyria (92.2%) and polymicrogyria (22.1%), varying in location and distribution. Incomplete rotation of the hippocampus was observed in 50.6% of patients and was associated with other imaging findings, in particular with dysgyria (100% versus 84.2%, Our findings show a link between the genetic-biochemical basis and the neuroimaging features and aid in better understanding the underlying clinical manifestations and possible treatment options. These findings have yet to be described to this extent and correspond with recent studies that show that

Sections du résumé

BACKGROUND AND PURPOSE OBJECTIVE
Sotos syndrome is a rare autosomal dominant condition caused by pathogenic mutations in the
MATERIALS AND METHODS METHODS
This multicenter, multinational, retrospective observational cohort study systematically analyzed the clinical characteristics and neuroimaging features of 77 individuals with genetically diagnosed Sotos syndrome, via central consensus review with 3 pediatric neuroradiologists.
RESULTS RESULTS
In addition to previously described features, malformations of cortical development were identified in most patients (95.0%), typically dysgyria (92.2%) and polymicrogyria (22.1%), varying in location and distribution. Incomplete rotation of the hippocampus was observed in 50.6% of patients and was associated with other imaging findings, in particular with dysgyria (100% versus 84.2%,
CONCLUSIONS CONCLUSIONS
Our findings show a link between the genetic-biochemical basis and the neuroimaging features and aid in better understanding the underlying clinical manifestations and possible treatment options. These findings have yet to be described to this extent and correspond with recent studies that show that

Identifiants

pubmed: 39147584
pii: ajnr.A8364
doi: 10.3174/ajnr.A8364
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024 by American Journal of Neuroradiology.

Auteurs

Bar Neeman (B)

From the Department of Radiology (B.N., L.B.-S.), Tel-Aviv Sourasky Medical Center, Tel-Aviv, Israel.
Faculty of Medicine (B.N., L.B.-S.), Tel-Aviv University, Tel-Aviv, Israel.

Sniya Sudhakar (S)

Department of Radiology (S.S., A.B., F.D., U.L., K.M.), Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.

Asthik Biswas (A)

Department of Radiology (S.S., A.B., F.D., U.L., K.M.), Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.

Jessica Rosenblum (J)

Center of Medical Genetics (J.R.), Antwerp University Hospital/University of Antwerp, Antwerp, Belgium.

Jai Sidpra (J)

Developmental Biology and Cancer Section (J.S., K.M.), University College London Great Ormond Street Institute of Child Health, London, UK.

Felice D'Arco (F)

Department of Radiology (S.S., A.B., F.D., U.L., K.M.), Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.

Ulrike Löbel (U)

Department of Radiology (S.S., A.B., F.D., U.L., K.M.), Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.

Marta Gómez-Chiari (M)

Diagnostic Imaging Department (M.G.-C.), Hospital Sant Joan de Déu, Barcelona, Spain.
Institut de Recerca Sant Joan de Déu,(M.G.-C., M.S., M.B.), Barcelona, Spain.

Mercedes Serrano (M)

Institut de Recerca Sant Joan de Déu,(M.G.-C., M.S., M.B.), Barcelona, Spain.
Neuropediatric Department (M.S.), Hospital Sant Joan de Déu, U-703 Centre for Biomedical Research on Rare Diseases, Barcelona, Spain.

Mercè Bolasell (M)

Institut de Recerca Sant Joan de Déu,(M.G.-C., M.S., M.B.), Barcelona, Spain.
Department of Genetic and Molecular Medicine/IPER (M.B.), Institut de Recerca, Hospital Sant Joan de Déu Barcelona, Barcelona, Spain.

Kartik Reddy (K)

Department of Radiology and Imaging Sciences (K.R.), Emory University School of Medicine, Atlanta, Georgia.

Liat Ben-Sira (L)

From the Department of Radiology (B.N., L.B.-S.), Tel-Aviv Sourasky Medical Center, Tel-Aviv, Israel.
Faculty of Medicine (B.N., L.B.-S.), Tel-Aviv University, Tel-Aviv, Israel.

Reem Zakzouk (R)

Division of Neuroradiology (R.Z.), Department of Radiology, Prince Sultan Military Medical City, Riyadh, Saudi Arabia.

Amal Al-Hashem (A)

Division of Genetics (A.A.-H.), Department of Pediatrics, Prince Sultan Military Medical City, Riyadh, Saudi Arabia.

David M Mirsky (DM)

Department of Radiology (D.M.M.), Children's Hospital Colorado, University of Colorado School of Medicine, Aurora, Colorado.

Rajan Patel (R)

Texas Children's Hospital (R.P.), Baylor College of Medicine, Houston, Texas.

Rupa Radhakrishnan (R)

Department of Radiology and Imaging Sciences (R.R.), Indiana University School of Medicine, Indianapolis, Indiana.

Karuna Shekdar (K)

Department of Radiology (K.S., M.T.W.), Children's Hospital of Philadelphia, Philadelphia, Pennsylvania.

Matthew T Whitehead (MT)

Department of Radiology (K.S., M.T.W.), Children's Hospital of Philadelphia, Philadelphia, Pennsylvania.
Perelman School of Medicine (M.T.W.), University of Pennsylvania, Philadelphia, Pennsylvania.

Kish Mankad (K)

Department of Radiology (S.S., A.B., F.D., U.L., K.M.), Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.
Developmental Biology and Cancer Section (J.S., K.M.), University College London Great Ormond Street Institute of Child Health, London, UK.

Classifications MeSH