The unfolded protein response regulates ER exit sites via SNRPB-dependent RNA splicing and contributes to bone development.

COPII Endoplasmic Reticulum Proteostasis Sec16A Splicing

Journal

The EMBO journal
ISSN: 1460-2075
Titre abrégé: EMBO J
Pays: England
ID NLM: 8208664

Informations de publication

Date de publication:
19 Aug 2024
Historique:
received: 28 09 2023
accepted: 24 07 2024
revised: 08 07 2024
medline: 20 8 2024
pubmed: 20 8 2024
entrez: 19 8 2024
Statut: aheadofprint

Résumé

Splicing and endoplasmic reticulum (ER)-proteostasis are two key processes that ultimately regulate the functional proteins that are produced by a cell. However, the extent to which these processes interact remains poorly understood. Here, we identify SNRPB and other components of the Sm-ring, as targets of the unfolded protein response and novel regulators of export from the ER. Mechanistically, The Sm-ring regulates the splicing of components of the ER export machinery, including Sec16A, a component of ER exit sites. Loss of function of SNRPB is causally linked to cerebro-costo-mandibular syndrome (CCMS), a genetic disease characterized by bone defects. We show that heterozygous deletion of SNRPB in mice resulted in bone defects reminiscent of CCMS and that knockdown of SNRPB delays the trafficking of type-I collagen. Silencing SNRPB inhibited osteogenesis in vitro, which could be rescued by overexpression of Sec16A. This rescue indicates that the role of SNRPB in osteogenesis is linked to its effects on ER-export. Finally, we show that SNRPB is a target for the unfolded protein response, which supports a mechanistic link between the spliceosome and ER-proteostasis. Our work highlights components of the Sm-ring as a novel node in the proteostasis network, shedding light on CCMS pathophysiology.

Identifiants

pubmed: 39160274
doi: 10.1038/s44318-024-00208-z
pii: 10.1038/s44318-024-00208-z
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Austrian Science Fund (FWF)
ID : P 36600
Organisme : Austrian Science Fund (FWF)
ID : P 35832
Organisme : Austrian Science Fund (FWF)
ID : FG2000
Organisme : Austrian Science Fund (FWF)
ID : ESP634
Organisme : Norges Forskningsråd (Forskningsrådet)
ID : 302452
Organisme : Norges Forskningsråd (Forskningsrådet)
ID : 262652
Organisme : Wellcome Trust
ID : 208015
Pays : United Kingdom
Organisme : EC | Horizon Europe | Excellent Science | HORIZON EUROPE Marie Sklodowska-Curie Actions (MSCA)
ID : 860035
Organisme : EC | Horizon Europe | Excellent Science | HORIZON EUROPE Marie Sklodowska-Curie Actions (MSCA)
ID : 859962

Informations de copyright

© 2024. The Author(s).

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Auteurs

Muhammad Zahoor (M)

Institute of Basic Medical Sciences, University of Oslo, Oslo, Norway. mzkhaans@yahoo.com.
Centre for Cancer Cell Reprogramming, Institute of Clinical Medicine, University of Oslo, Oslo, Norway. mzkhaans@yahoo.com.

Yanchen Dong (Y)

Research Institute of the McGill University Health Centre at Glen Site, Montreal, QC, H4A 3J1, Canada.
Department of Human Genetics, McGill University, Montreal, QC, H3A 0G1, Canada.

Marco Preussner (M)

Institute of Chemistry and Biochemistry, Freie Universität Berlin, Laboratory of RNA Biochemistry, Takustrasse 6, 14195, Berlin, Germany.

Veronika Reiterer (V)

Institute of Pathophysiology, Medical University of Innsbruck, Innrain 80, 6020, Innsbruck, Austria.

Sabrina Shameen Alam (S)

Research Institute of the McGill University Health Centre at Glen Site, Montreal, QC, H4A 3J1, Canada.
Department of Human Genetics, McGill University, Montreal, QC, H3A 0G1, Canada.

Margot Haun (M)

Institute of Pathophysiology, Medical University of Innsbruck, Innrain 80, 6020, Innsbruck, Austria.

Utku Horzum (U)

Institute of Pathophysiology, Medical University of Innsbruck, Innrain 80, 6020, Innsbruck, Austria.

Yannick Frey (Y)

Institute of Pathophysiology, Medical University of Innsbruck, Innrain 80, 6020, Innsbruck, Austria.

Renata Hajdu (R)

Institute of Pathophysiology, Medical University of Innsbruck, Innrain 80, 6020, Innsbruck, Austria.

Stephan Geley (S)

Institute of Pathophysiology, Medical University of Innsbruck, Innrain 80, 6020, Innsbruck, Austria.

Valerie Cormier-Daire (V)

Clinical Genetics Department, Université de Paris, INSERM UMR 1163, Imagine Institute, Necker Enfants Malades Hospital, Paris, France.

Florian Heyd (F)

Institute of Chemistry and Biochemistry, Freie Universität Berlin, Laboratory of RNA Biochemistry, Takustrasse 6, 14195, Berlin, Germany.

Loydie A Jerome-Majewska (LA)

Research Institute of the McGill University Health Centre at Glen Site, Montreal, QC, H4A 3J1, Canada. loydie.majewska@mcgill.ca.
Department of Human Genetics, McGill University, Montreal, QC, H3A 0G1, Canada. loydie.majewska@mcgill.ca.
Department of Anatomy and Cell Biology, McGill University, Montreal, QC, H3A 2B2, Canada. loydie.majewska@mcgill.ca.
Department of Pediatrics, McGill University, Montreal, QC, H4A 3J1, Canada. loydie.majewska@mcgill.ca.

Hesso Farhan (H)

Institute of Basic Medical Sciences, University of Oslo, Oslo, Norway. hesso.farhan@i-med.ac.at.
Institute of Pathophysiology, Medical University of Innsbruck, Innrain 80, 6020, Innsbruck, Austria. hesso.farhan@i-med.ac.at.

Classifications MeSH