Outcomes of infants and children with bronchopulmonary dysplasia-associated pulmonary hypertension who required home ventilation.


Journal

Pediatric research
ISSN: 1530-0447
Titre abrégé: Pediatr Res
Pays: United States
ID NLM: 0100714

Informations de publication

Date de publication:
24 Aug 2024
Historique:
received: 09 05 2024
accepted: 05 08 2024
medline: 26 8 2024
pubmed: 26 8 2024
entrez: 24 8 2024
Statut: aheadofprint

Résumé

To characterize a cohort of ventilator-dependent infants and children with bronchopulmonary dysplasia-associated pulmonary hypertension (BPD-PH) and to describe their cardiorespiratory outcomes. Subjects with BPD on chronic home ventilation were recruited from outpatient clinics. PH was defined by its presence on ≥1 cardiac catheterization or echocardiogram on or after 36 weeks post-menstrual age. Kaplan-Meier analysis was used to compare the timing of key events. Of the 154 subjects, 93 (60.4%) had PH and of those, 52 (55.9%) required PH-specific medications. The ages at tracheostomy, transition to home ventilator, and hospital discharge were older in those with PH. Most subjects were weaned off oxygen and liberated from the ventilator by 5 years of age, which did not occur later in subjects with PH. The mortality rate after initial discharge was 2.6%. The majority of infants with BPD-PH receiving chronic invasive ventilation at home survived after initial discharge. Subjects with BPD-PH improved over time as evidenced by weaning off oxygen and PH medications, ventilator liberation, and tracheostomy decannulation. While the presence of PH was not associated with later ventilator liberation or decannulation, the use of PH medications may be a marker of a more protracted disease trajectory. There is limited data on long-term outcomes of children with bronchopulmonary dysplasia (BPD) who receive chronic invasive ventilation at home, and no data on those with the comorbidity of pulmonary hypertension (PH). Almost all subjects with BPD-PH who were on chronic invasive ventilation at home survived after their initial hospital discharge. Subjects with BPD-PH improved over time as evidenced by weaning off oxygen, PH medications, liberation from the ventilator, and tracheostomy decannulation. The presence of PH did not result in later ventilator liberation or decannulation; however, the use of outpatient PH medications was associated with later ventilation liberation and decannulation.

Sections du résumé

BACKGROUND BACKGROUND
To characterize a cohort of ventilator-dependent infants and children with bronchopulmonary dysplasia-associated pulmonary hypertension (BPD-PH) and to describe their cardiorespiratory outcomes.
METHODS METHODS
Subjects with BPD on chronic home ventilation were recruited from outpatient clinics. PH was defined by its presence on ≥1 cardiac catheterization or echocardiogram on or after 36 weeks post-menstrual age. Kaplan-Meier analysis was used to compare the timing of key events.
RESULTS RESULTS
Of the 154 subjects, 93 (60.4%) had PH and of those, 52 (55.9%) required PH-specific medications. The ages at tracheostomy, transition to home ventilator, and hospital discharge were older in those with PH. Most subjects were weaned off oxygen and liberated from the ventilator by 5 years of age, which did not occur later in subjects with PH. The mortality rate after initial discharge was 2.6%.
CONCLUSIONS CONCLUSIONS
The majority of infants with BPD-PH receiving chronic invasive ventilation at home survived after initial discharge. Subjects with BPD-PH improved over time as evidenced by weaning off oxygen and PH medications, ventilator liberation, and tracheostomy decannulation. While the presence of PH was not associated with later ventilator liberation or decannulation, the use of PH medications may be a marker of a more protracted disease trajectory.
IMPACT STATEMENT UNASSIGNED
There is limited data on long-term outcomes of children with bronchopulmonary dysplasia (BPD) who receive chronic invasive ventilation at home, and no data on those with the comorbidity of pulmonary hypertension (PH). Almost all subjects with BPD-PH who were on chronic invasive ventilation at home survived after their initial hospital discharge. Subjects with BPD-PH improved over time as evidenced by weaning off oxygen, PH medications, liberation from the ventilator, and tracheostomy decannulation. The presence of PH did not result in later ventilator liberation or decannulation; however, the use of outpatient PH medications was associated with later ventilation liberation and decannulation.

Identifiants

pubmed: 39181986
doi: 10.1038/s41390-024-03495-8
pii: 10.1038/s41390-024-03495-8
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024. The Author(s), under exclusive licence to the International Pediatric Research Foundation, Inc.

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Auteurs

Gangaram G Akangire (GG)

Division of Neonatology, Children's Mercy-Kansas City and University of Missouri Kansas City School of Medicine, Kansas City, MO, USA.

Winston Manimtim (W)

Division of Neonatology, Children's Mercy-Kansas City and University of Missouri Kansas City School of Medicine, Kansas City, MO, USA.

Amit Agarwal (A)

Division of Pulmonary Medicine, Arkansas Children's Hospital and University of Arkansas for Medical Sciences, Little Rock, AR, USA.

Stamatia Alexiou (S)

Division of Pulmonary Medicine, Children's Hospital of Philadelphia and University of Pennsylvania, Philadelphia, PA, USA.

Brianna C Aoyama (BC)

Eudowood Division of Pediatric Respiratory Sciences, Johns Hopkins University, Baltimore, MD, USA.

Eric D Austin (ED)

Pulmonary Medicine, Vanderbilt University and Vanderbilt University Medical Center, Nashville, TN, USA.

Manvi Bansal (M)

Pulmonology and Sleep Medicine, Children's Hospital of Los Angeles, Los Angeles, CA, USA.

Julie L Fierro (JL)

Division of Pulmonary Medicine, Children's Hospital of Philadelphia and University of Pennsylvania, Philadelphia, PA, USA.

Lystra P Hayden (LP)

Division of Pulmonary Medicine, Boston Children's Hospital and Harvard Medical School, Boston, MA, USA.

Jacob A Kaslow (JA)

Pulmonary Medicine, Vanderbilt University and Vanderbilt University Medical Center, Nashville, TN, USA.

Khanh V Lai (KV)

Division of Pediatric Pulmonary and Sleep Medicine, University of Utah, Salt Lake City, UT, USA.

Jonathan C Levin (JC)

Division of Pulmonary Medicine, Boston Children's Hospital and Harvard Medical School, Boston, MA, USA.
Division of Newborn Medicine, Boston Children's Hospital and Harvard Medical School, Boston, MA, USA.

Audrey N Miller (AN)

Division of Neonatology, Nationwide Children's Hospital and Ohio State University, Columbus, OH, USA.

Jessica L Rice (JL)

Division of Pulmonary Medicine, Children's Hospital of Philadelphia and University of Pennsylvania, Philadelphia, PA, USA.

Michael C Tracy (MC)

Division of Pediatric Pulmonary, Asthma and Sleep Medicine, Stanford University, Stanford, CA, USA.

Christopher D Baker (CD)

Section of Pulmonary and Sleep Medicine, Department of Pediatrics, University of Colorado School of Medicine, Aurora, CO, USA.

Sarah E Bauer (SE)

Division of Pediatric Pulmonology, Allergy and Sleep Medicine, Riley Children's Hospital and Indiana University, Indianapolis, IN, USA.

A Ioana Cristea (AI)

Division of Pediatric Pulmonology, Allergy and Sleep Medicine, Riley Children's Hospital and Indiana University, Indianapolis, IN, USA.

Sara K Dawson (SK)

Department of Pediatrics, Medical College of Wisconsin Milwaukee, Wisconsin, USA.

Laurie Eldredge (L)

Division of Pediatric Pulmonary and Sleep Medicine, Seattle Children's Hospital and University of Washington, Seattle, WA, USA.

Jennifer K Henningfeld (JK)

Department of Pediatrics, Medical College of Wisconsin Milwaukee, Wisconsin, USA.

Robin L McKinney (RL)

Department of Pediatrics, Brown University School of Medicine, Providence, RI, USA.

Roopa Siddaiah (R)

Pediatric Pulmonology, Penn State Health, Hershey, PA, USA.

Natalie M Villafranco (NM)

Pulmonary Medicine, Texas Children's Hospital and Baylor College of Medicine, Houston, TX, USA.

Steven H Abman (SH)

Section of Pulmonary and Sleep Medicine, Department of Pediatrics, University of Colorado School of Medicine, Aurora, CO, USA.

Sharon A McGrath-Morrow (SA)

Division of Pulmonary Medicine, Children's Hospital of Philadelphia and University of Pennsylvania, Philadelphia, PA, USA.

Joseph M Collaco (JM)

Eudowood Division of Pediatric Respiratory Sciences, Johns Hopkins University, Baltimore, MD, USA. mcollac1@jhmi.edu.

Classifications MeSH