ERBB2/ ERBB3-mutated S100/ SOX10-positive unclassified high-grade uterine sarcoma: first detailed description of a novel entity.

EGFR Molecular profiling; nerve sheath tumor Targeted therapy Tyrosine kinase fusions Undifferentiated uterine sarcoma

Journal

Virchows Archiv : an international journal of pathology
ISSN: 1432-2307
Titre abrégé: Virchows Arch
Pays: Germany
ID NLM: 9423843

Informations de publication

Date de publication:
28 Aug 2024
Historique:
received: 25 07 2024
accepted: 19 08 2024
revised: 25 07 2024
medline: 28 8 2024
pubmed: 28 8 2024
entrez: 28 8 2024
Statut: aheadofprint

Résumé

With the increasing use of innovative next generation sequencing (NGS) platforms in routine diagnostic and research settings, the genetic landscape of uterine sarcomas has been dynamically evolving during the last two decades. Notably, the majority of recently recognized genotypes in uterine sarcomas represent gene fusions, while recurrent oncogene mutations of diagnostic and/ or therapeutic value have been rare. Recently, a distinctive aggressive uterine sarcoma expressing S100 and SOX10, but otherwise lacking diagnostic morphological, immunophenotypic and molecular features of other uterine malignancies has been presented in a scientific abstract form (USCAP, 2023), but detailed description and delineation of the entity is still missing. We herein describe two high-grade unclassified uterine sarcomas characterized by spindle to round cell morphology and diffuse expression of S100 and SOX10, originating in the uterine body and cervix of 53- and 45-year-old women and carrying an ERBB3 (p.Glu928Gly) and an ERBB2 (p.Val777Leu) mutation, respectively. Both tumors harbored in addition genomic HER2 amplification, ATRX mutation and CDKN2A deletion. Methylation studies revealed a methylome most similar to MPNST-like tumors, but distinct from melanoma, MPNST, clear cell sarcoma, and endometrial stromal sarcoma. Case 1 died of progressive peritoneal metastases after multiple trials of chemotherapy 47 months after diagnosis. Case 2 is a recent case who presented with a cervical mass, which was biopsied. This study defines a novel heretofore unrecognized aggressive uterine sarcoma with unique phenotypic and genotypic features. Given the potential value of targeting HER2, recognizing this tumor type is mandatory for appropriate therapeutic strategies and for better future delineation of the entity.

Identifiants

pubmed: 39196362
doi: 10.1007/s00428-024-03908-3
pii: 10.1007/s00428-024-03908-3
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024. The Author(s).

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Auteurs

Abbas Agaimy (A)

Institute of Pathology, Erlangen University Hospital, Friedrich Alexander University of Erlangen-Nuremberg, Erlangen, Germany. abbas.agaimy@uk-erlangen.de.
Comprehensive Cancer Center, European Metropolitan Area Erlangen-Nuremberg (CCC ER-EMN), Erlangen, Germany. abbas.agaimy@uk-erlangen.de.

Josephine K Dermawan (JK)

Department of Pathology and Laboratory Medicine, Cleveland Clinic, Cleveland, Ohio, USA.

Florian Haller (F)

Institute of Pathology, Erlangen University Hospital, Friedrich Alexander University of Erlangen-Nuremberg, Erlangen, Germany.
Comprehensive Cancer Center, European Metropolitan Area Erlangen-Nuremberg (CCC ER-EMN), Erlangen, Germany.

Sabine Semrau (S)

Department of Radiation Oncology, University Hospital, Friedrich-Alexander-University Erlangen-Nürnberg (FAU), Erlangen, Germany.

Norbert Meidenbauer (N)

Department of Internal Medicine 5-Hematology and Oncology, Erlangen University Hospital, Friedrich Alexander University of Erlangen-Nuremberg, Erlangen, Germany.

Robert Stoehr (R)

Institute of Pathology, Erlangen University Hospital, Friedrich Alexander University of Erlangen-Nuremberg, Erlangen, Germany.
Comprehensive Cancer Center, European Metropolitan Area Erlangen-Nuremberg (CCC ER-EMN), Erlangen, Germany.

Sigurd Lax (S)

Department of Pathology, Hospital Graz II, Academic Teaching Hospital of the Medical University Graz, Graz, Austria.
School of Medicine, Johannes Kepler University Linz, Linz, Austria.

Arndt Hartmann (A)

Institute of Pathology, Erlangen University Hospital, Friedrich Alexander University of Erlangen-Nuremberg, Erlangen, Germany.
Comprehensive Cancer Center, European Metropolitan Area Erlangen-Nuremberg (CCC ER-EMN), Erlangen, Germany.

Ying S Zou (YS)

Department of Pathology, The Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.

Deyin Xing (D)

Department of Pathology, The Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.

Lars Tögel (L)

Institute of Pathology, Erlangen University Hospital, Friedrich Alexander University of Erlangen-Nuremberg, Erlangen, Germany.
Comprehensive Cancer Center, European Metropolitan Area Erlangen-Nuremberg (CCC ER-EMN), Erlangen, Germany.

John M Gross (JM)

Department of Pathology, The Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.

Michael Michal (M)

Department of Pathology, Faculty of Medicine in Plzeň, Charles University, Plzeň, Czech Republic.
Biotical Laboratory, Ltd, Plzeň, Czech Republic.

Classifications MeSH